NCT01859754

Brief Summary

Study Design: This is a 2 arm non-interventional trial that will compare the occurrence of adverse drug reactions between Octagam 5% and other marketed IVIG infusion treatments.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
623

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started May 2013

Longer than P75 for all trials

Geographic Reach
1 country

27 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

May 9, 2013

Completed
12 days until next milestone

Study Start

First participant enrolled

May 21, 2013

Completed
1 day until next milestone

First Posted

Study publicly available on registry

May 22, 2013

Completed
6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 22, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 22, 2019

Completed
Last Updated

June 10, 2019

Status Verified

June 1, 2019

Enrollment Period

6 years

First QC Date

May 9, 2013

Last Update Submit

June 7, 2019

Conditions

Keywords

Primary Immune Deficiency SyndromePrimary immunodeficiency Disease (PIDD)PID

Outcome Measures

Primary Outcomes (1)

  • Incidence Rate of Thromboembolytic events

    4 months

Study Arms (2)

Octagam 5%

Primary Immune Deficiency Syndrome patients receiving Octagam 5% by infusion who have been treated with a marketed IVIG product for at least 6 months.

Biological: Octagam 5%

Other marketed IVIG product

Primary Immune Deficiency Syndrome patients receiving marketed IVIG product other than Octagam 5% by infusion as treatment for at least 6 months.

Biological: Other marketed IVIG product

Interventions

Octagam 5%BIOLOGICAL

Intravenous immunoglobulin 5%

Octagam 5%

Any intravenous immunoglobulin marketed product approved for the treatment of PID

Other marketed IVIG product

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Patients over 18 years old with Primary Immune Deficiency Syndrome PID receiving marketed IVIG as treatment

You may qualify if:

  • Male and female patients aged 18 years.
  • Patients with confirmed diagnosis of Primary Humoral Immunodeficiency (PI) as stated by the World Health Organization and requiring immunoglobulinreplacement therapy due to hypogammaglobulinemia or agammaglobulinemia.
  • Patients on regular treatment (every 3 to 4 weeks) with low dose IGIV (1 g/kg) for a period of at least 6 months without changing the brand.

You may not qualify if:

  • Patients with a history of TEEs within the previous 24 months.
  • Patients with a regular treatment frequency of more than once every 3 to 4 weeks.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (27)

Octapharma Research Site

Granada Hills, California, 91344, United States

Location

Octapharma Research Site

Irvine, California, 92697, United States

Location

Octapharma Research Site

Los Angeles, California, 90025, United States

Location

Octapharma Research Site

Redlands, California, 92373, United States

Location

Octapharma Research Site

Centennial, Colorado, 80112, United States

Location

Octapharma Research Site

Roswell, Georgia, 30076, United States

Location

Octapharma Research Site

Chicago, Illinois, 60612, United States

Location

Octapharma Research Site

Springfield, Illinois, 62701, United States

Location

Octapharma Research Site

Fort Wayne, Indiana, 46815, United States

Location

Octapharma Research Site

Wichita, Kansas, 67201, United States

Location

Octapharma Research Site

Fort Mitchell, Kentucky, 41017, United States

Location

Octapharma Research Site

Farmington Hills, Michigan, 48334, United States

Location

Octapharma Research Site

Plymouth, Minnesota, 55446, United States

Location

Octapharma Research Site

Plymouth, Minnesota, 55447, United States

Location

Octapharma Research Site

Omaha, Nebraska, 68124, United States

Location

Octapharma Research Site

East Setauket, New York, 11733, United States

Location

Octapharma Research Site

New York, New York, 10012, United States

Location

Octapharma Research Site

New York, New York, 10065, United States

Location

Octapharma Research Site

Columbus, Ohio, 43235, United States

Location

Octapharma Research Site

Mayfield Heights, Ohio, 44124, United States

Location

Octapharma Research Site

Toledo, Ohio, 43617, United States

Location

Octapharma Research Site

Pawtucket, Rhode Island, 02860, United States

Location

Octapharma Research Site

Anderson, South Carolina, 29621, United States

Location

Octapharma Research Site

Nashville, Tennessee, 37203, United States

Location

Octapharma Research Site

Amarillo, Texas, 79124, United States

Location

Octapharma Research Site

Dallas, Texas, 75231, United States

Location

Octapharma Research Site

Irving, Texas, 75014, United States

Location

MeSH Terms

Conditions

Primary Immunodeficiency Diseases

Condition Hierarchy (Ancestors)

Genetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesImmunologic Deficiency SyndromesImmune System Diseases

Study Officials

  • Wolfgang Frenzel

    International Medical Monitor, Octapharma AG

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 9, 2013

First Posted

May 22, 2013

Study Start

May 21, 2013

Primary Completion

May 22, 2019

Study Completion

May 22, 2019

Last Updated

June 10, 2019

Record last verified: 2019-06

Locations