NCT01857362

Brief Summary

The purpose of this study is to evaluate the bioequivalence between Orfadin 20 mg and 10 mg capsules in healthy volunteers.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
12

participants targeted

Target at below P25 for phase_1 healthy

Timeline
Completed

Started May 2013

Shorter than P25 for phase_1 healthy

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 1, 2013

Completed
15 days until next milestone

First Submitted

Initial submission to the registry

May 16, 2013

Completed
4 days until next milestone

First Posted

Study publicly available on registry

May 20, 2013

Completed
12 days until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2013

Completed
1.4 years until next milestone

Results Posted

Study results publicly available

October 27, 2014

Completed
Last Updated

October 12, 2021

Status Verified

September 1, 2021

Enrollment Period

1 month

First QC Date

May 16, 2013

Results QC Date

June 9, 2014

Last Update Submit

September 20, 2021

Conditions

Keywords

OrfadinNitisinoneBioequivalence

Outcome Measures

Primary Outcomes (2)

  • The Area Under the Serum Concentration vs. Time Profile During 72 Hours After Dose (AUC72h).

    Day 1 predose and at 15, 30, 45 minutes and 1, 1.5, 2, 2.5, 3, 3.5, 4, 6, 8, 10, 12, 24, 36, 48 and 72 hours postdose

  • The Maximum Serum Concentration (Cmax).

    Day 1 predose and at 15, 30, 45 minutes and 1, 1.5, 2, 2.5, 3, 3.5, 4, 6, 8, 10, 12, 24, 36, 48 and 72 hours postdose

Study Arms (2)

Nitisinone 2 x 10 mg

ACTIVE COMPARATOR

Two nitisinone 10 mg capsules by mouth as a single dose

Drug: Nitisinone 10 mg

Nitisinone 1 x 20 mg capsule

EXPERIMENTAL

One nitisinone 20 mg capsule by mouth as a single dose

Drug: Nitisinone 20 mg

Interventions

Nitisinone 20 mg capsules

Nitisinone 1 x 20 mg capsule

Nitisinone 10 mg capsules

Nitisinone 2 x 10 mg

Eligibility Criteria

Age18 Years - 55 Years
Sexall
Healthy VolunteersYes
Age GroupsAdult (18-64)

You may qualify if:

  • Healthy male and female volunteers between 18-55 years of age, inclusive.
  • BMI between 18,5-30,0 kg/m2, inclusive.

You may not qualify if:

  • Subjects with current keratopathy, or other abnormalities found by slit-lamp examination.
  • Subjects who are heavy smokers or consume more than 5 cups of coffee per day.
  • Subjects with history of drug and/or alcohol abuse or a positive drug screen or alcohol breath test.
  • Subjects with positive screens for hepatitis B surface antigen, hepatitis C antibodies and human immunodeficiency virus (HIV) 1-2 antibodies.
  • Subjects who donate more than 50 mL of blood within 60 days prior to drug administration or donate more than 1,5 liters of blood in the 10 months prior to first drug administration.
  • Female subjects that are pregnant or breastfeeding.
  • Female subjects of childbearing potential and all male subjects must be willing to use effective forms of contraception.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Pharmaceutical Research Associates Group B.V (PRA)

Zuidlaren, 9471 GP, Netherlands

Location

MeSH Terms

Interventions

nitisinone

Results Point of Contact

Title
Dr Erik Brouwer, Medical Director
Organization
Swedish Orphan Biovitrum

Study Officials

  • Erik Brouwer, MD

    Swedish Orphan Biovitrum

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 1
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
CROSSOVER
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 16, 2013

First Posted

May 20, 2013

Study Start

May 1, 2013

Primary Completion

June 1, 2013

Study Completion

June 1, 2013

Last Updated

October 12, 2021

Results First Posted

October 27, 2014

Record last verified: 2021-09

Locations