NCT01825811

Brief Summary

The purpose of this study is to determine whether TissueGene-C, allogeneic human chondrocytes expressing Transforming Growth Factor(TGF)-b1, mixed with fibrin-glue is effective and safe in patients with degenerative arthritis.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
18

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Oct 2012

Geographic Reach
1 country

6 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 1, 2012

Completed
6 months until next milestone

First Submitted

Initial submission to the registry

April 3, 2013

Completed
5 days until next milestone

First Posted

Study publicly available on registry

April 8, 2013

Completed
12 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2014

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

June 1, 2014

Completed
Last Updated

January 22, 2015

Status Verified

January 1, 2015

Enrollment Period

1.5 years

First QC Date

April 3, 2013

Last Update Submit

January 20, 2015

Conditions

Keywords

Cell mediated gene therapyOsteoarthritisFibrin-glueDegenerative Arthritis

Outcome Measures

Primary Outcomes (1)

  • Changes in IKDC Subjective Knee Evaluation

    Symptoms, sports activities, and function of the knee will be measured by the International Knee Documentation Committee (IKDC)

    Week 0 and 48

Secondary Outcomes (8)

  • Changes in WOMAC scores

    Week 0, 24 and 48

  • Changes in KOOS scores

    Week 0, 24 and 48

  • Changes in 100 mm-VAS

    Week 0, 24 and 48

  • Comparative Evaluation of Knee Magnetic Resonance Images (MRIs)

    Week 0, 24 and 48

  • Changes in ICRS Cartilage Repair Assessment

    week 0 and 48

  • +3 more secondary outcomes

Study Arms (2)

TissueGene-C (Low dose)

EXPERIMENTAL

TissueGene-C (1.0 x 10\^6 cells per cm\^2 of the cartilage defect) combined with fibrin-glue

Biological: TissueGene-C (Low dose)

Experimental: TissueGene-C (High dose)

EXPERIMENTAL

TissueGene-C (3.0 x 10\^6 cells per cm\^2 of the cartilage defect) combined with fibrin-glue

Biological: TissueGene-C (High dose)

Interventions

TissueGene-C at 1.0 x 10\^6 cells mixed with fibrin-glue

TissueGene-C (Low dose)

TissueGene-C at 3.0 x 10\^6 cells mixed with fibrin-glue

Experimental: TissueGene-C (High dose)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Female or male aged 18 years or more
  • Diagnosed with degenerative arthritis of the knee
  • With an IKDC score of 60 or lower at the screening visit
  • With a BMI of higher than18.5 and lower than 30
  • With an International Cartilage Repair Society(ICRS) Grade IV cartilage damage in the major lesions, as confirmed through an MRI scan
  • With major lesions concentrated in one section of the knee, and with the major lesions considered the main cause of the clinical symptoms
  • With major lesions defect size 2 cm2 \~ 10cm2
  • With no alleviation of the symptoms even after at least three months of non-surgical treatment
  • Healthy, with no major findings from the physical examination, hematology, serum chemistry, and urine tests, and no significant medical history
  • Agreed to use an effective contraceptive method during the study period
  • Voluntarily agreed to participate in this study, and signed the informed consent form

You may not qualify if:

  • Showed clinically significant hematology, serum chemistry, and urine test results at the screening visit
  • Mechanical axis (HKA) is greater than 5°
  • Patients receiving injections to the treated knee within 2 months prior to study entry
  • Patients who are pregnant or currently breast-feeding children
  • With another joint disease (e.g., inflammatory arthritis, infectious arthritis)
  • With an infectious disease, including HIV or hepatitis
  • With any of the following clinically significant diseases:
  • heart disease \[e.g., myocardial infarction, arrhythmia, other serious heart diseases,
  • kidney disease (e.g., chronic renal failure, glomerulonephritis)
  • liver disease (e.g., liver cirrhosis, fatty liver, acute or chronic liver disease)
  • endocrine disease (e.g., hyperthyroidism, hypothyroidism, thyroiditis, diabetes insipidus, Cushing's disease)
  • insulin-dependent diabetes mellitus
  • medical history of past or current malignant tumor
  • In particular, the tumors that TissueGene-C may aggravate can be screened using the following tests:
  • Leukemia (White Blood Cell level in the hematology)
  • +3 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (6)

Kyungpook National University Hospital

Daegu, 700-721, South Korea

Location

Inha University Hospital

Incheon, 400-711, South Korea

Location

Seoul National University Hospital

Seoul, 110-744, South Korea

Location

Samsung Medical Center

Seoul, 135-710, South Korea

Location

Asan Medical Center

Seoul, 138-736, South Korea

Location

Ewha Womans University Mokdong Hospital

Seoul, 158-710, South Korea

Location

MeSH Terms

Conditions

Osteoarthritis

Condition Hierarchy (Ancestors)

ArthritisJoint DiseasesMusculoskeletal DiseasesRheumatic Diseases

Study Officials

  • Myung Chul Lee, MD, PhD

    Seoul National University Hospital

    PRINCIPAL INVESTIGATOR
  • Chul Won Ha, MD, PhD

    Samsung Medical Center

    PRINCIPAL INVESTIGATOR
  • Seong Il Bin, MD, PhD

    Asan Medical Center

    PRINCIPAL INVESTIGATOR
  • Myung Gu Kim, MD, PhD

    Inha University Hospital

    PRINCIPAL INVESTIGATOR
  • Jae Doo Yoo, MD, PhD

    Ewha Womans University Mokdong Hospital

    PRINCIPAL INVESTIGATOR
  • Hee Su Kyung, MD, PhD

    Kyungpook National University Hospital

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
SINGLE
Who Masked
PARTICIPANT
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 3, 2013

First Posted

April 8, 2013

Study Start

October 1, 2012

Primary Completion

April 1, 2014

Study Completion

June 1, 2014

Last Updated

January 22, 2015

Record last verified: 2015-01

Locations