NCT01808911

Brief Summary

CREHA project is a study comparing steroid combined with cyclophosphamide versus steroid combined with rituximab in patients with acquired haemophilia. The study will test the hypothesis that steroid combined with cyclophosphamide is more effective than steroid plus rituximab for FVIII inhibitor eradication in acquired haemophilia.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
110

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started May 2012

Longer than P75 for phase_3

Geographic Reach
1 country

34 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 1, 2012

Completed
6 months until next milestone

First Submitted

Initial submission to the registry

October 16, 2012

Completed
5 months until next milestone

First Posted

Study publicly available on registry

March 11, 2013

Completed
7.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 14, 2021

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 14, 2021

Completed
Last Updated

March 24, 2026

Status Verified

March 1, 2026

Enrollment Period

8.7 years

First QC Date

October 16, 2012

Last Update Submit

March 19, 2026

Conditions

Keywords

Acquired haemophiliaComparative and randomized studyCyclophosphamideRituximab

Outcome Measures

Primary Outcomes (3)

  • Primary objective

    Demonstrate the inferiority of steroid combined with rituximab as compared to the recommended immunosuppressive approach (steroid combined with cysclophosphamide for 21 to 42 days) as the first-line immunosuppressive therapy for FVIII inhibitor eradication in acquired haemophilia

    During 18 months

  • Primary efficacy outcome

    The primary efficacy outcome is the proportion of patients achieving complete remission defined as titer FVII inhibitor lower than 0.4 Bethesda unit and factor VIII level \> 50%

    During 18 months

  • Primary safety outcomes

    The primary safety outcomes will be the occurrence of major bleeding and infection related immunosuppressive treatment adverse events.

    During 18 months

Secondary Outcomes (2)

  • Secondary objective

    6 months, 12 months and 18 months

  • Other key safety outcome

    During 18 months

Study Arms (2)

Bras A

ACTIVE COMPARATOR

Steroid 1mg/kg/d and Cyclophosphamide 2mg/kg/d

Drug: Steroid + cyclophosphamide

Bras B

EXPERIMENTAL

Steroid 1mg/kg/d and Rituximab 375 mg/m2 every week during four weeks

Drug: Steroid + rituximab

Interventions

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • men or women
  • women post-menpausal or with ongoing contraception
  • years old or more
  • diagnosis of acquired hemophilia
  • patient must be insured
  • patient has provided written informed consent prior to enrolment
  • patient compliant

You may not qualify if:

  • constitutional hemophilia
  • chemotherapy
  • ongoing treatment with prednisone \> 20mg further more 1 month
  • ongoing treatment with prednisone \>0.7 mg/d further more 10 days
  • thrombocytopenia
  • leukopenia
  • chronic disease

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (34)

University Hospital Amiens

Amiens, 80054, France

Location

Hospital of Béziers

Béziers, 34525, France

Location

Hospital Jean Verdier

Bondy, 93140, France

Location

Hospital Ambroise Paré

Boulogne-Billancourt, 92104, France

Location

University Hospital of Brest - Hospital La cavale Blanche

Brest, 29609, France

Location

University Hospital Côte de Nacre

Caen, 14033, France

Location

University Hospital G. Montpied

Clermont-Ferrand, 63003, France

Location

Hospital Henri Mondor

Créteil, 94010, France

Location

University Hospital of Dijon - Hospital Général

Dijon, 21033, France

Location

University Hospital Bocage

Dijon, 21079, France

Location

University Hospital Michallon

Grenoble, 38043, France

Location

Hospital Kremlin-Bicêtre

Le Kremlin-Bicêtre, 94270, France

Location

University Regional Hospital of Lille

Lille, 59037, France

Location

university Hospital of Limoges

Limoges, 87042, France

Location

AP-HM, University Hospital La Conception

Marseille, 13385, France

Location

University Hospital Saint-Eloi

Montpellier, 34295, France

Location

Regional Center of Haemophilia Treatment (CRTH) de Lorraine

Nancy, France

Location

University Hospital of Nantes, Hospital Hôtel-Dieu

Nantes, 44093, France

Location

Hospital Archet 1

Nice, 06202, France

Location

Hospital Bichat

Paris, 75018, France

Location

Hospital Saint-Louis

Paris, 75475, France

Location

Hospital Pitié-Salpêtrière

Paris, 75651, France

Location

Hospital Cochin

Paris, 75679, France

Location

Europen Hospital of Georges Pompidou (HEGP)

Paris, 75908, France

Location

University Hospital of Bordeaux - Hospital Haut-Lévêque

Pessac, 33604, France

Location

Hospital Lyon Sud

Pierre-Bénite, 69495, France

Location

University Hospital of Poitiers

Poitiers, 86021, France

Location

Hospital Sud / Hospital Pontchaillou

Rennes, 35000, France

Location

University Hospital of Rouen

Rouen, 76031, France

Location

Hospital Nord

Saint-Etienne, 42055, France

Location

University Regional Hospital Hautepierre

Strasbourg, 67098, France

Location

Hospital Purpan

Toulouse, 31059, France

Location

Hospital Rangueil

Toulouse, 31059, France

Location

Hopsital Bretonneau

Tours, 37044, France

Location

Related Publications (1)

  • Levesque H, Viallard JF, Houivet E, Bonnotte B, Voisin S, Le Cam-Duchez V, Maillot F, Lambert M, Liozon E, Hervier B, Fain O, Guillet B, Schmidt J, Luca LE, Ebbo M, Ferreira-Maldent N, Babuty A, Sailler L, Duffau P, Barbay V, Audia S, Benichou J, Graveleau J, Benhamou Y; CREHA Study investigators on behalf the scientific committee of the "Societe Nationale Francaise de Medecine Interne" (SNFMI - French National Society of Internal Medicine). Cyclophosphamide vs rituximab for eradicating inhibitors in acquired hemophilia A: A randomized trial in 108 patients. Thromb Res. 2024 May;237:79-87. doi: 10.1016/j.thromres.2024.03.012. Epub 2024 Mar 15.

MeSH Terms

Interventions

SteroidsCyclophosphamideRituximab

Intervention Hierarchy (Ancestors)

Fused-Ring CompoundsPolycyclic CompoundsPhosphoramide MustardsNitrogen Mustard CompoundsMustard CompoundsHydrocarbons, HalogenatedHydrocarbonsOrganic ChemicalsPhosphoramidesOrganophosphorus CompoundsAntibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 16, 2012

First Posted

March 11, 2013

Study Start

May 1, 2012

Primary Completion

January 14, 2021

Study Completion

January 14, 2021

Last Updated

March 24, 2026

Record last verified: 2026-03

Locations