NCT01799941

Brief Summary

The objectives of the study are to evaluate the safety, tolerability, and effectiveness of NUEDEXTA capsules containing 20 mg DM (Dextromethorphan)/10 mg Q (Quinidine) for treatment of Pseudobulbar Affect (PBA) in patients with prevalent conditions such as dementia, stroke, and traumatic brain injury (TBI)over a 12 week period.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
367

participants targeted

Target at P75+ for phase_4

Timeline
Completed

Started Feb 2013

Typical duration for phase_4

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

February 1, 2013

Completed
24 days until next milestone

First Submitted

Initial submission to the registry

February 25, 2013

Completed
2 days until next milestone

First Posted

Study publicly available on registry

February 27, 2013

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2015

Completed
1.9 years until next milestone

Results Posted

Study results publicly available

March 15, 2017

Completed
Last Updated

March 15, 2017

Status Verified

January 1, 2017

Enrollment Period

2.2 years

First QC Date

February 25, 2013

Results QC Date

May 5, 2016

Last Update Submit

January 26, 2017

Conditions

Outcome Measures

Primary Outcomes (1)

  • Mean Change From Baseline in Center for Neurologic Study-Lability Scale (CNS-LS) Score at Day 90

    The CNS-LS was a seven-item, self-administered questionnaire, completed by the participant or participant's caregiver that provided a quantitative measure of the perceived frequency and severity of Pseudobulbar Affect (PBA) episodes. It consisted of two subscales measuring labile laughter (four items) and labile crying (three items). Each item was rated on a scale from 1 (applies never) to 5 (applies most of the time). The total score was calculated as the sum of the item values that resulted in a score ranging from 7 (no symptoms) to 35 (maximum symptom severity and frequency). A single continuous variable was created for the reported time point. The change in CNS-LS was calculated as the score from the Day 90 assessment minus the Baseline CNS-LS measure. A negative change represented a decrease in CNS-LS score over time following the baseline assessment indicating a perceived decrease in frequency and severity of PBA episodes.

    Day 90 (Final visit)

Secondary Outcomes (11)

  • Mean Change From Baseline in Center for Neurologic Study-Lability Scale (CNS-LS) Score at Day 30

    Day 30

  • Mean Pseudobulbar Affect (PBA) Episode Count Per Week by Visit

    Baseline (Day 1), Day 30 (Visit 1), and Day 90 (Final visit)

  • Percentage of Participants With PBA Remission

    Day 30 (Visit 1) and Day 90 (Final visit)

  • Percentage Change From Baseline in PBA Episode Count Per Week

    Day 30 (Visit 1) and Day 90 (Final visit)

  • Percentage of Participants With ≥ 50% Reduction in PBA Episode Count Per Week

    Day 30 (Visit 1) and Day 90 (Final visit)

  • +6 more secondary outcomes

Study Arms (1)

Nuedexta (DM 20 mg/Q 10 mg)

OTHER

Single Arm, Open Label Dosing with Nuedexta (DM 20 mg/Q 10 mg)

Drug: Nuedexta (DM 20 mg/Q 10 mg)

Interventions

Single Arm, Open-Label Dosing with Nuedexta (DM 20 mg/Q 10 mg)

Also known as: Nuedexta
Nuedexta (DM 20 mg/Q 10 mg)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Center for Neurologic Study-Lability Scale (CNS-LS)score of 13 or greater
  • Clinical diagnosis of Pseudobulbar Affect (PBA)
  • Documentation of Neurologic disease or brain injury

You may not qualify if:

  • Unstable neurologic disease
  • Severe dementia
  • Stroke within 3 months
  • Penetrating TBI
  • Contraindications to Nuedexta
  • Severe Depressive Disorder

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Unknown Facility

Pensacola, Florida, 32503, United States

Location

Related Publications (3)

  • Hammond FM, Sauve W, Ledon F, Davis C, Formella AE. Safety, Tolerability, and Effectiveness of Dextromethorphan/Quinidine for Pseudobulbar Affect Among Study Participants With Traumatic Brain Injury: Results From the PRISM-II Open Label Study. PM R. 2018 Oct;10(10):993-1003. doi: 10.1016/j.pmrj.2018.02.010. Epub 2018 Feb 23.

  • Hammond FM, Alexander DN, Cutler AJ, D'Amico S, Doody RS, Sauve W, Zorowitz RD, Davis CS, Shin P, Ledon F, Yonan C, Formella AE, Siffert J. PRISM II: an open-label study to assess effectiveness of dextromethorphan/quinidine for pseudobulbar affect in patients with dementia, stroke or traumatic brain injury. BMC Neurol. 2016 Jun 9;16:89. doi: 10.1186/s12883-016-0609-0.

  • Doody RS, D'Amico S, Cutler AJ, Davis CS, Shin P, Ledon F, Yonan C, Siffert J. An open-label study to assess safety, tolerability, and effectiveness of dextromethorphan/quinidine for pseudobulbar affect in dementia: PRISM II results. CNS Spectr. 2016 Dec;21(6):450-459. doi: 10.1017/S1092852915000620. Epub 2015 Oct 16.

MeSH Terms

Conditions

StrokeDementiaBrain Injuries, Traumatic

Interventions

dextromethorphan - quinidine combination

Condition Hierarchy (Ancestors)

Cerebrovascular DisordersBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesVascular DiseasesCardiovascular DiseasesNeurocognitive DisordersMental DisordersBrain InjuriesCraniocerebral TraumaTrauma, Nervous SystemWounds and Injuries

Results Point of Contact

Title
Nadine Knowles; Executive Director, Research & Development Operations
Organization
Avanir Pharmaceuticals

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 4
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 25, 2013

First Posted

February 27, 2013

Study Start

February 1, 2013

Primary Completion

May 1, 2015

Study Completion

May 1, 2015

Last Updated

March 15, 2017

Results First Posted

March 15, 2017

Record last verified: 2017-01

Locations