NCT01747915

Brief Summary

The study is designed to evaluate the safety, tolerability and efficacy of two doses of pregabalin as add-on treatment in pediatric and adult subjects with Primary Generalized Tonic-Clonic (PGTC) seizures as compared to placebo. It is hypothesized that both doses of pregabalin will demonstrated superior efficacy when compared to placebo by reducing PGTC seizure frequency and that pregabalin will be safe and well tolerated.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
219

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Apr 2013

Longer than P75 for phase_3

Geographic Reach
26 countries

127 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

November 27, 2012

Completed
15 days until next milestone

First Posted

Study publicly available on registry

December 12, 2012

Completed
4 months until next milestone

Study Start

First participant enrolled

April 3, 2013

Completed
5.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 20, 2019

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 20, 2019

Completed
6 months until next milestone

Results Posted

Study results publicly available

August 28, 2019

Completed
Last Updated

January 20, 2021

Status Verified

August 1, 2019

Enrollment Period

5.9 years

First QC Date

November 27, 2012

Results QC Date

August 8, 2019

Last Update Submit

January 15, 2021

Conditions

Keywords

Primary Generalized Tonic Clonic SeizuresEpilepsySafetyEfficacyTolerabilityPregabalinLyricaAdjunctive treatmentPlacebo ControlledBlinded

Outcome Measures

Primary Outcomes (1)

  • Log-transformed (Log) 28-day Seizure Rate for All Primary Generalized Tonic-Clonic (PGTC) Seizures During 12-Week Double-Blind Treatment Phase

    All PGTC seizures experienced during treatment phase were recorded by the participants or their parents/legal guardian in a daily seizure diary. 28-day seizure rate for all PGTC seizures= (\[number of seizures in the double blind treatment phase\] divided by \[number of days in double blind treatment phase minus {-} number of missing diary days in treatment phase\])\*28. For log-transformation, the quantity 1 was added to the 28-day seizure rate for all participants to account for any possible "0" seizure incidence. This resulted in final calculation as: log transformed (28-day seizure rate +1).

    Day 1 up to Week 12

Secondary Outcomes (1)

  • Percentage of Participants With at Least 50 Percent (%) or Greater Reduction From Baseline in 28-day Primary Generalized Tonic-clonic (PGTC) Seizure Rate During the 12-Week Double-blind Treatment Phase

    Day 1 up to Week 12

Study Arms (3)

Study Drug Level 1

EXPERIMENTAL
Drug: Pregabalin Dose Level 1

Study Drug Level 2

EXPERIMENTAL
Drug: Pregabalin Dose Level 2

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

Pregabalin, either liquid or capsule, dosed twice daily, escalated up to a maximum of 300 mg/day beginning at Randomization to Taper Phase, then tapered down to a maximum dose of 150 mg/day during 1 week Taper Phase to End of Study/Early Termination.

Also known as: Lyrica Dose Level 1
Study Drug Level 1

Pregabalin, either liquid or capsule, dosed twice daily, escalated up to a maximum of 600 mg/day beginning at Randomization to Taper Phase, then tapered down to a maximum of 150 mg/day during 1 week Taper Phase to End of Study/Early Termination.

Also known as: Lyrica Dose Level 2
Study Drug Level 2

Placebo, either liquid or capsule, dosed twice daily beginning at Randomization to End of Study/Early Termination.

Placebo

Eligibility Criteria

Age5 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Seizures classified as Primary Generalized Tonic Clonic Seizures
  • Must have at least 1 PGTC seizure in the 8 weeks prior to screening
  • Must have a minimum of 3 PGTC seizures during the 8-week baseline phase and at least 1 PGTC in each 4-week period of the baseline phase
  • Currently receiving adequate and stable dosage of 1 to 3 anti-epileptic treatments (stable within 28 days of screening)
  • Signed informed consent and assent if a minor
  • Ability to comply with daily seizure and dosing diary requirements and all study procedures

You may not qualify if:

  • A current diagnosis of febrile seizures, or seizures related to an ongoing acute medical illness
  • Focal seizures (simple partial, complex partial, or partial becoming secondarily generalized)
  • Status Epilepticus within 1 year prior to screening
  • Lennox-Gastaut syndrome, infantile spasms, Benign Epilepsy with Centrotemporal Spikes (BECTS) and Dravet syndrome
  • Seizures related to drugs, alcohol, or acute medical illness
  • Any change in anti-epileptic treatment regimen (type of medication or dose; VNS alteration) within 28 days of the screening visit or during the baseline phase
  • Progressive or potentially progressive structural CNS lesion or a progressive encephalopathy.
  • Progressive inborn errors of metabolism.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (127)

Axcess Medical Research

Loxahatchee Groves, Florida, 33470, United States

Location

Pediatric Epilepsy Center of Central Florida

Orlando, Florida, 32819, United States

Location

Pediatric Neurology, PA

Orlando, Florida, 32819, United States

Location

Medsol Clinical Research Center

Port Charlotte, Florida, 33952, United States

Location

Hawaii Pacific Neuroscience

Honolulu, Hawaii, 96817, United States

Location

Alexian Brothers Center for Psychiatric Research

Hoffman Estates, Illinois, 60169, United States

Location

Chinmay K. Patel, D.O.

Hoffman Estates, Illinois, 60169, United States

Location

St. Alexius Medical Center

Hoffman Estates, Illinois, 60169, United States

Location

Ohio Clinical Research Partners, LLC

Canton, Ohio, 44718, United States

Location

Road Runner Research, Ltd

San Antonio, Texas, 78249, United States

Location

Scott & White Memorial Hospital and Clinic

Temple, Texas, 76508, United States

Location

Rainier Clinical Research Center, Inc.

Renton, Washington, 98057, United States

Location

Medizinische Universitaet Innsbruck

Innsbruck, 6020, Austria

Location

AKH Linz

Linz, 4021, Austria

Location

UZ Vitebsk Regional Childrens Clinical Centre

Vitebsk, 210015, Belarus

Location

UZ Vitebsk Regional Childrens Clinical Centre

Vitebsk, 210022, Belarus

Location

University Clinical Center Sarajevo

Sarajevo, Canton Sarajevo, 71000, Bosnia and Herzegovina

Location

University Clinical Center Tuzla

Tuzla, Canton Tuzla, 75000, Bosnia and Herzegovina

Location

University Clinical Hospital Mostar

Mostar, Herzegovinaneretva Canton, 88000, Bosnia and Herzegovina

Location

Public Health Institution Hospital Dr Mladen Stojanovic

Prijedor, Republika Srpska, 79101, Bosnia and Herzegovina

Location

Multiprofile Hospital for Active Treatment Puls AD

Blagoevgrad, 2700, Bulgaria

Location

DCC Sv. Pantaleimon OOD

Pleven, 5800, Bulgaria

Location

Military Medical Academy - Multiprofile Hospital for Active Treatment

Pleven, 5800, Bulgaria

Location

MHAT Central Onco Hospital OOD

Plovdiv, 4000, Bulgaria

Location

Medical Center Teodora

Rousse, 7000, Bulgaria

Location

MHATNP Sveti Naum EAD

Sofia, 1113, Bulgaria

Location

UMHAT Aleksandrovska

Sofia, 1431, Bulgaria

Location

DCC Sveta Anna - Sofia

Sofia, 1784, Bulgaria

Location

The First Affiliated Hospital of Chongqing Medical University

Chongqing, Chongqing Municipality, 400016, China

Location

The First Bethune Hospital of Jilin University

Changchun, Jilin, 130021, China

Location

Shanghai Huashan Hospital, Neurology Department

Shanghai, Shanghai Municipality, 201100, China

Location

University Hospital Center Split, Clinic for Neurology

Split, 21000, Croatia

Location

Aarhus University Hospital

Aarhus C, 8000, Denmark

Location

Odense University Hospital

Odense C, 5000, Denmark

Location

CHU d'Amiens - Picardie

Amiens, 80054, France

Location

CHRU de Rennes - Hôpital Pontchaillou

Rennes, 35033, France

Location

CHU d'Amiens Hopital Pontchaillou

Rennes, 35033, France

Location

Eginition Hospital

Athens, 11528, Greece

Location

Athens Medical Center

Athens, 15125, Greece

Location

General Children's Hospital Penteli

Athens, 15236, Greece

Location

University General Hospital of Thessaloniki "AHEPA"

Thessaloniki, 54636, Greece

Location

Semmelweis Egyetem, I. Sz. Gyermekgyogyaszati Klinika

Budapest, H-1083, Hungary

Location

Csongrad Megyei Egeszsegugyi Ellato Kozpont Hodmezovasarhely-Mako

Hódmezővásárhely, H-6800, Hungary

Location

Pest Megyei Flór Ferenc Kórhaz

Kistarcsa, 2143, Hungary

Location

St. John's Medical College Hospital

Bangalore, Karnataka, 560034, India

Location

Mangala Hospital & Mangala Kidney Foundation

Mangalore, Karnataka, 575003, India

Location

P D Hinduja National Hospital and Medical Research Centre

Mumbai, Maharashtra, 400016, India

Location

Getwell Hospital and Research Institute

Nagpur, Maharashtra, 440012, India

Location

Sahyadri Speciality Hospital

Pune, Maharashtra, 411004, India

Location

KEM Hospital Research Centre

Pune, Maharashtra, 411011, India

Location

Indraprastha Apollo Hospitals

New Delhi, National Capital Territory of Delhi, 110076, India

Location

Saint George Hospital - University Medical Center

Beirut, NAP, Lebanon

Location

Ain Wazein Medical Village

El Chouf, Lebanon

Location

Hospital Raja Permaisuri Bainun

Ipoh, Perak, 30990, Malaysia

Location

Pzu Neuron

Bijelo Polje, 84000, Montenegro

Location

Cebu Doctors' University Hospital

Cebu City, CEBU, 6000, Philippines

Location

Perpetual Succour Hospital

Cebu City, CEBU, 6000, Philippines

Location

Cebu Doctors' University Hospital, Rm Ph 7

Cebu City, 6000, Philippines

Location

Manila Doctors Hospital

Manila, 1000, Philippines

Location

Metropolitan Medical Center

Manila, 1003, Philippines

Location

University of Santo Tomas Hospital

Manila, 1008, Philippines

Location

St. Luke's Medical Center Cathedral Heights Building

Quezon City, Philippines

Location

COPERNICUS Podmiot Leczniczy Spzoo

Gdansk, 80-803, Poland

Location

NZOZ Wielospecjalistyczna Poradnia Lekarska SYNAPSIS

Katowice, 40-123, Poland

Location

NZOZ Novo Med

Katowice, 40-650, Poland

Location

Neuro-Care Gabriela Klodowska

Katowice, 40-749, Poland

Location

NZOZ "HIPOKRATES II" Sp. z o.o.

Krakow, 31-223, Poland

Location

Instytut Medycyny Wsi im. Witolda Chodzki w Lublinie

Lublin, 20-090, Poland

Location

Solumed Centrum Medyczne

Poznan, 60-529, Poland

Location

NZOZ IGNIS dr n. med. Alicja Lobinska

Świdnik, 21-040, Poland

Location

Lecznica Medyczna ''Zycie"

Warsaw, 00-453, Poland

Location

Centrul Medical de Diagnostic si Tratament Ambulator Neomed

Brasov, 500283, Romania

Location

CMI Neurologie, Neurofiziologie (EEG, EMG, PEC) Roceanu Adina Maria

Bucharest, 010042, Romania

Location

Sapiens Medical Center

Bucharest, 030583, Romania

Location

Spitalul Clinic de Urgenta "Prof. Dr. Nicolae Oblu"

Iași, 700309, Romania

Location

Spitalul Clinic de Urgente pentru Copii "Sf. Maria"

Iași, 700309, Romania

Location

Spitalul de Psihiatrie "Dr. Gh. Preda"

Sibiu, 550082, Romania

Location

SPHI Leningrad Regional Psychoneurological Dispensary

Pgt. Roshchino, Leningradskaya Oblast', 188820, Russia

Location

Nizhmedklinika

Nizhny Novgorod, Nizhny Novgorod Oblast, 603159, Russia

Location

Perm State Medical University n. a. acad. E.A. Vagner

Perm, Permskiy KRAY, 614000, Russia

Location

State Budgetary Healthcare Institution of Stavropol region

Pyatigorsk, Stavropol Kray, 357538, Russia

Location

GBOU VPO "Kazan State Medical University" of Roszdrav

Kazan', Tatarstan Republic, 420012, Russia

Location

Republican clinical hospital

Kazan', Tatarstan Republic, 420064, Russia

Location

TSBHI City Hospital No. 5 of Barnaul

Barnaul, 656045, Russia

Location

MAHI of the Order of the Red Banner of Labor City Clinical Hospital No. 1

Chelyabinsk, 454048, Russia

Location

Non-state Healthcare Institution

Moscow, 129128, Russia

Location

LLC City Neurological Center "Sibneiromed"

Novosibirsk, 630091, Russia

Location

Perm State Medical University n. a. acad. E.A. Vagner

Perm, 614990, Russia

Location

SPHI Leningrad Regional Psychoneurological Dispensary

Saint Petersburg, 191040, Russia

Location

FSBI V.M. Bekhterev National Research Medical Center for

Saint Petersburg, 192019, Russia

Location

SBHI of Saint Petersburg Psychoneurological Dispensary #5

Saint Petersburg, 195112, Russia

Location

SBHI of Saint Petersburg Psychoneurological Dispensary #5

Saint Petersburg, 195176, Russia

Location

Regional State Budgetary Institution of Ministry of Health

Smolensk, 214018, Russia

Location

RSBHI Smolensk Regional Clinical Hospital

Smolensk, 214018, Russia

Location

GBOU VPO Smolensk State Medical University

Smolensk, 214019, Russia

Location

SHI "Central Clinical Medical Unit

Ulyanovsk, 432026, Russia

Location

SHI "Central Clinical Medical Unit

Ulyanovsk, 432045, Russia

Location

Institute for Child and Youth Healthcare of Vojvodina

Novi Sad, Vojvodina, 21000, Serbia

Location

Institute for Mental Health

Belgrade, 11000, Serbia

Location

University Children's Hospital

Belgrade, 11000, Serbia

Location

Clinical Center Kragujevac

Kragujevac, 34000, Serbia

Location

Nemocnica s poliklinikou Hlohovec, s.r.o.

Hlohovec, 92001, Slovakia

Location

Neurologicka ambulancia MUDr. Eva Gasparova

Hlohovec, 92001, Slovakia

Location

Keimyung University Dongsan Hospital

Daegu, Korea, 41931, South Korea

Location

Seoul National University Hospital

Seoul, 03080, South Korea

Location

Konkuk University medical center

Seoul, 05030, South Korea

Location

Samsung Medical Center

Seoul, 06351, South Korea

Location

Hospital Universitari de Bellvitge

L'Hospitalet de Llobregat, Barcelona, 08907, Spain

Location

Marmara University Pendik Training and Research Hospital

Istanbul, UST Kaynarca/pendik, 34899, Turkey (Türkiye)

Location

Eskisehir Osmangazi University Medical Faculty Department Of Neurology

Eskişehir, 26480, Turkey (Türkiye)

Location

Dokuz Eylul Ün. Tip Fakültesi İç Hastalıkları

Izmir, 35340, Turkey (Türkiye)

Location

Celal Bayar University School of Medicine, Neurology Department

Manisa, 45010, Turkey (Türkiye)

Location

Komunalna ustanova "Odeska oblasna psykhiatrychna likarnia 2"

S. Oleksandrivka, Komintern. R-N, Odeska OBL., 67513, Ukraine

Location

Komunalnyi zaklad "Dnipropetrovska dytiacha miska klinichna likarnia No. 5"

Dnipro, 49027, Ukraine

Location

Komunalnyi zaklad "Dnipropetrovska oblasna dytiacha klinichna likarnia"

Dnipro, 49100, Ukraine

Location

Ivano-Frankivska oblasna dytiacha klinichna likarnia

Ivano-Frankivsk, 76018, Ukraine

Location

Derzhavna ustanova "Instytut nevrolohii, psykhiatrii ta narkolohii

Kharkiv, 61068, Ukraine

Location

Komunalne nekomertsiine pidpryiemstvo Kharkivskoi oblasnoi rady "Oblasna klinichna psykhiatrychna li

Kharkiv, 61068, Ukraine

Location

Derzhavnyi zaklad "Ukrainskyi medychnyi tsentr reabilitatsii ditei z

Kyiv, 04209, Ukraine

Location

Komunalnyi zaklad Lvivskoi oblasnoi rady "Lvivska oblasna klinichna likarnia"

Lviv, 79010, Ukraine

Location

Komunalne nekomertsiine pidpryiemstvo "Odeskyi oblasnyi

Odesa, 65006, Ukraine

Location

Oblasnyi klinichnyi tsentr neirokhirurhii ta nevrolohii,

Uzhhorod, 88018, Ukraine

Location

Komunalna ustanova "Miska klinichna likarnia #2", nevrolohichne viddilennia

Zaporizhzhia, 69068, Ukraine

Location

The Barberry National Centre for Mental Health

Birmingham, WEST Midlands, B15 2FG, United Kingdom

Location

Barts Health NHS Foundation Trust, The Royal London Hospital

London, E1 2AT, United Kingdom

Location

Salford Royal NHS Foundation Trust

Salford, M6 8HD, United Kingdom

Location

ABMU Local Health Board, Morriston Hospital

Swansea, SA6 6NL, United Kingdom

Location

Related Publications (1)

  • Driscoll J, Almas M, Gregorian G, Kyrychenko A, Makedonska I, Liu J, Patrick J, Scavone JM, Antinew J; 1105 Study Group. Pregabalin as adjunctive therapy in adult and pediatric patients with generalized tonic-clonic seizures: A randomized, placebo-controlled trial. Epilepsia Open. 2021 Jun;6(2):381-393. doi: 10.1002/epi4.12492. Epub 2021 May 16.

Related Links

MeSH Terms

Conditions

SeizuresEpilepsy

Condition Hierarchy (Ancestors)

Neurologic ManifestationsNervous System DiseasesSigns and SymptomsPathological Conditions, Signs and SymptomsBrain DiseasesCentral Nervous System Diseases

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 27, 2012

First Posted

December 12, 2012

Study Start

April 3, 2013

Primary Completion

February 20, 2019

Study Completion

February 20, 2019

Last Updated

January 20, 2021

Results First Posted

August 28, 2019

Record last verified: 2019-08

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations