NCT01688024

Brief Summary

The purpose of this study is to determine the effectiveness and safety of mitomycin C in the treatment of primary sclerosing cholangitis (PSC).

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
130

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Sep 2012

Longer than P75 for phase_2

Geographic Reach
1 country

1 active site

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2012

Completed
9 days until next milestone

First Submitted

Initial submission to the registry

September 10, 2012

Completed
9 days until next milestone

First Posted

Study publicly available on registry

September 19, 2012

Completed
5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2017

Completed
2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2019

Completed
Last Updated

September 7, 2016

Status Verified

September 1, 2016

Enrollment Period

5 years

First QC Date

September 10, 2012

Last Update Submit

September 6, 2016

Conditions

Keywords

mitomycin C

Outcome Measures

Primary Outcomes (1)

  • Therapeutic Effect on Disease Prognosis as Determined by the Mayo Natural History Model for Primary Sclerosing Cholangitis

    Two years

Secondary Outcomes (2)

  • Number of Patients with Adverse Events

    Two years

  • Frequency of Endoscopic Interventions Needed to Manage Disease-related Complications

    Two years

Study Arms (2)

Mitomycin C

EXPERIMENTAL

Up to 10 mg administered during each standard of care endoscopic retrograde cholangiography. No more than five mitomycin C applications per every twelve months will be given.

Drug: Mitomycin C

Normal saline

PLACEBO COMPARATOR

Given during each standard of care endoscopic retrograde cholangiography. No more than five normal saline applications per every twelve months will be performed.

Drug: Normal saline

Interventions

Mitomycin C
Normal saline

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Ages 18 or older
  • Previously established diagnosis of primary sclerosing cholangitis

You may not qualify if:

  • American Society of Anesthesiologists class 4 or greater
  • Serum creatinine \>= 1.7 mg/dL, eGFR \<= 30 mL/min, or dialysis dependence
  • Serum hemoglobin \<= 7 g
  • Left ventricular ejection fraction \<= 30%
  • Dyspnea with minimal exertion (or supplemental oxygen dependence)
  • History of bone marrow disease
  • Prior recipient of organ transplantation
  • Ongoing chemotherapy
  • Obstruction of the upper GI tract
  • Pregnant or lactating
  • Inability to provide informed consent

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Johns Hopkins Hospital

Baltimore, Maryland, 21288, United States

RECRUITING

MeSH Terms

Conditions

Cholangitis, Sclerosing

Interventions

MitomycinSaline Solution

Condition Hierarchy (Ancestors)

CholangitisBile Duct DiseasesBiliary Tract DiseasesDigestive System Diseases

Intervention Hierarchy (Ancestors)

MitomycinsIndolequinonesQuinonesOrganic ChemicalsAzirinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsIndolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingCrystalloid SolutionsIsotonic SolutionsSolutionsPharmaceutical Preparations

Study Officials

  • Zhiping Li, M.D.

    Johns Hopkins University

    PRINCIPAL INVESTIGATOR

Central Study Contacts

Po-Hung Chen, M.D.

CONTACT

Tinsay A. Woreta, M.D., M.P.H.

CONTACT

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, CARE PROVIDER
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDIV
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 10, 2012

First Posted

September 19, 2012

Study Start

September 1, 2012

Primary Completion

September 1, 2017

Study Completion

September 1, 2019

Last Updated

September 7, 2016

Record last verified: 2016-09

Locations