NCT01670981

Brief Summary

This study is designed to assess the efficacy, safety and tolerability of ixmyelocel-T compared to placebo (vehicle control) when administered via transendocardial catheter-based injections to patients with end stage heart failure due to IDCM, who have no reasonable revascularization options (either surgical or percutaneous interventional) likely to provide clinical benefit.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
114

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Feb 2013

Longer than P75 for phase_2

Geographic Reach
2 countries

36 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 20, 2012

Completed
3 days until next milestone

First Posted

Study publicly available on registry

August 23, 2012

Completed
6 months until next milestone

Study Start

First participant enrolled

February 20, 2013

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2016

Completed
2.1 years until next milestone

Study Completion

Last participant's last visit for all outcomes

March 7, 2018

Completed
Last Updated

May 27, 2021

Status Verified

May 1, 2021

Enrollment Period

2.9 years

First QC Date

August 20, 2012

Last Update Submit

May 25, 2021

Conditions

Keywords

Ischemic dilated cardiomyopathyHeart failureixCELLixCELL DCMIDCMDCMstem cellsMSCcell therapy

Outcome Measures

Primary Outcomes (1)

  • Average number of clinical events over 12 months post-treatment.

    The primary endpoint will assess the efficacy of ixmyelocel-T compared to placebo (vehicle control) on the average number of events per patient over 12 months post-treatment in each treatment arm (total number events in each arm/total number of patients in each arm). The events include: all-cause deaths, cardiovascular hospitalizations, and unplanned outpatient or emergency department visits to treat acute decompensated heart failure. The clinical events used in this endpoint will be adjudicated by an independent clinical endpoint committee who are blinded to treatment.

    12 Months

Secondary Outcomes (7)

  • The win ratio of the hierarchical occurrence of all-cause deaths/left ventricular assist device (LVAD) implant/heart transplant, cardiovascular hospitalizations, and unplanned outpatient and ED interventions to treat ADHF

    12 Months

  • Change from baseline to 12 months post-treatment in 6-minute walk test.

    12 Months

  • Change from baseline to 12 months post-treatment in left ventricular function as evaluated by echocardiography.

    12 Months

  • Change from baseline to 12 months post-treatment in quality of life.

    12 Months

  • Change from baseline to 12 months post-treatment in NYHA Classification.

    12 Months

  • +2 more secondary outcomes

Study Arms (2)

ixmyelocel-T

EXPERIMENTAL

Ixmyelocel-T delivered by catheter-based intramyocardial injection procedure.

Biological: ixmyelocel-T

Placebo

PLACEBO COMPARATOR

Placebo delivered by catheter-based intramyocardial injection procedure.

Other: Placebo

Interventions

ixmyelocel-TBIOLOGICAL

12-20 transendocardial injections of 0.4 mL of ixmyelocel-T per injection into the left ventricle.

ixmyelocel-T
PlaceboOTHER

12-20 transendocardial injections of 0.4 mL of vehicle control per injection into the left ventricle.

Placebo

Eligibility Criteria

Age30 Years - 86 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Males and non-pregnant, non-lactating females;
  • Age 30 to 86 years of age;
  • Diagnosis of ischemic dilated cardiomyopathy;
  • LVEF ≤ 35% by echocardiogram;
  • Symptomatic heart failure in NYHA functional class III or IV;
  • Subject is not a candidate for reasonable revascularization procedures that will produce clinical improvement;
  • Subject is receiving appropriate clinical standard of care heart failure therapy, as tolerated and as dictated by a subject's current medical condition, for at least 30 days prior to screening;
  • Must have an automatic implantable cardioverter defibrillator (AICD);
  • Worsening heart failure hospitalization or equivalent within 6 months prior to screening, hospitalization equivalent defined as an unplanned outpatient/emergency department visit for treatment of acute decompensated heart failure; or have an N-terminal prohormone B-type natriuretic peptide (NT-proBNP) ≥2000 pg/mL or BNP ≥400 pg/mL within 30 days of screening (including screening); or have a 6-minute walk test (6MWT) distance of ≤400 meters at screening;
  • Life expectancy of at least 12 months in the opinion of the Investigator;
  • LV wall thickness ≥ 7mm (by echocardiogram) at anticipated target injection area;
  • Hemodynamic stability without IV vasopressors or support devices;
  • Given medical history and concurrent medication, subject is an acceptable candidate for bone marrow aspiration and cardiac catheterization and transendocardial injection procedures in the opinion of the Investigator;
  • Willing and able to comply scheduled visits and tolerate study procedures.
  • Voluntarily provide a personally-signed and dated informed consent.

You may not qualify if:

  • Disease-specific:
  • Severe primary valvular heart disease including, but not limited to, aortic valve stenosis and insufficiency;
  • VAD implantation, heart transplantation, cardiomyoplasty, left ventricular reduction surgery, or cardiac shunt implantation;
  • Planned heart failure-related device interventions (e.g., VAD implantation, initial cardiac resynchronization therapy) or planned cardiac procedures (e.g., heart transplant, cardiomyoplasty, valvular repair);
  • Current arrhythmias that would prohibit accurate NOGA® electromechanical mapping and NOGA®-guided injections;
  • LV thrombus (as documented on echocardiography or LV angiography);
  • Myocardial infarction, stroke or transient ischemic attack within 3 months prior to screening;
  • Percutaneous coronary intervention, valvuloplasty, cardiac surgery, and other major cardiac procedure within 30 days prior to screening;
  • In the opinion of the Investigator, the subject's left ventricular wall is unsuitable for transendocardial injections (due to thickness or other reasons).
  • Medical History:
  • Stroke or transient ischemic attack (TIA) within 3 months of screening;
  • Hemoglobin A1c (HbA1c) ≥ 9% at screening;
  • Diabetic subjects with uncontrolled or untreated proliferative retinopathy as determined by dilated eye exam administered by a qualified eye care professional as per American Diabetes Association guidelines;
  • Blood clotting disorder not caused by medication (e.g., thrombophilia);
  • Active malignancy (non-basal cell) requiring surgery, chemotherapy, and/or radiation in the past 12 months;
  • +17 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (36)

Cardiology, P.C. & Center for Therapeutic Angiogenesis

Birmingham, Alabama, 35211, United States

Location

University of Alabama at Birmingham

Birmingham, Alabama, 35294, United States

Location

Mercy Gilbert Medical Center

Gilbert, Arizona, 85297, United States

Location

Mayo Clinic Arizona

Phoenix, Arizona, 85054, United States

Location

Scripps Clinic

La Jolla, California, 92037, United States

Location

UCSD Medical Center

La Jolla, California, 92037, United States

Location

Cedars-Sinai Heart and Lung Institute

Los Angeles, California, 90048, United States

Location

University of California Los Angeles (UCLA)

Los Angeles, California, 90095, United States

Location

St. John's Regional Medical Center

Oxnard, California, 93030, United States

Location

Stanford University

Stanford, California, 94305, United States

Location

Cardiology Research Associates

Daytona Beach, Florida, 32117, United States

Location

University of Florida - Division of Cardiology

Gainesville, Florida, 32610, United States

Location

Mayo Clinic Florida (Jacksonville)

Jacksonville, Florida, 32224, United States

Location

University of Miami - Miller School of Medicine

Miami, Florida, 33136, United States

Location

Emory University Hospital

Atlanta, Georgia, 30322, United States

Location

Georgia Regents University

Augusta, Georgia, 30912, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

Ochsner Clinic Foundation

New Orleans, Louisiana, 70121, United States

Location

Massachusetts General Hospital, Division of Cardiology

Boston, Massachusetts, 02114, United States

Location

Michigan CardioVascular Institute

Saginaw, Michigan, 48602, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

Newark Beth Israel Hospital

Newark, New Jersey, 07112, United States

Location

Columbia University Medical Center

New York, New York, 10032, United States

Location

The Carl and Edyth Linder Center for Research & Education at The Christ Hospital

Cincinnati, Ohio, 45219, United States

Location

University Hospitals - Case Medical Center

Cleveland, Ohio, 44106, United States

Location

Temple University

Philadelphia, Pennsylvania, 19140, United States

Location

UPMC Cardiovascular Institute

Pittsburgh, Pennsylvania, 15213, United States

Location

Veterans Administration Healthcare System

Pittsburgh, Pennsylvania, 15240, United States

Location

Stern Cardiovascular Foundation, Inc.

Germantown, Tennessee, 38138, United States

Location

Soltero Cardiovascular Research Center

Dallas, Texas, 75226, United States

Location

Methodist DeBakey Heart and Vascular Center

Houston, Texas, 77030, United States

Location

University of Utah Health Services Center

Salt Lake City, Utah, 84132, United States

Location

Swedish Medical Center - Cherry Hill Professional Building

Seattle, Washington, 98122, United States

Location

University of Wisconsin-Madison Cardiovascular Medicine

Madison, Wisconsin, 53792, United States

Location

University of Alberta Hospital

Edmonton, Alberta, T6G 287, Canada

Location

Montreal Heart Institute

Montreal, Quebec, H1T 1C8, Canada

Location

Related Publications (1)

  • Patel AN, Henry TD, Quyyumi AA, Schaer GL, Anderson RD, Toma C, East C, Remmers AE, Goodrich J, Desai AS, Recker D, DeMaria A; ixCELL-DCM Investigators. Ixmyelocel-T for patients with ischaemic heart failure: a prospective randomised double-blind trial. Lancet. 2016 Jun 11;387(10036):2412-21. doi: 10.1016/S0140-6736(16)30137-4. Epub 2016 Apr 5.

Related Links

MeSH Terms

Conditions

Heart Failure

Condition Hierarchy (Ancestors)

Heart DiseasesCardiovascular Diseases

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 20, 2012

First Posted

August 23, 2012

Study Start

February 20, 2013

Primary Completion

February 1, 2016

Study Completion

March 7, 2018

Last Updated

May 27, 2021

Record last verified: 2021-05

Locations