NCT01655862

Brief Summary

This is an observational study to assess health-related quality of life in patients with cervical dystonia (dystonie) treated with OnabotulinumtoxinA per routine clinical practice.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
62

participants targeted

Target at P25-P50 for all trials

Timeline
Completed

Started Jul 2012

Longer than P75 for all trials

Geographic Reach
1 country

8 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2012

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

July 31, 2012

Completed
2 days until next milestone

First Posted

Study publicly available on registry

August 2, 2012

Completed
4.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2017

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2017

Completed
Last Updated

March 30, 2017

Status Verified

March 1, 2017

Enrollment Period

4.6 years

First QC Date

July 31, 2012

Last Update Submit

March 28, 2017

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change from Baseline in Cervical Dystonia Impact Profile Questionnaire (CDIP-58) Score

    Baseline, 96 Weeks

Secondary Outcomes (4)

  • Patient's Global Impression of Change (PGIC) Using a 7-Point Scale

    Baseline, 96 Weeks

  • Work Productivity Assessment Using a 10-Item Questionnaire

    96 Weeks

  • Change from Baseline in Hospital Anxiety and Depression Scale (HAD) Score

    Baseline, 96 Weeks

  • Reasons for Withdrawal of Treatment

    96 Weeks

Study Arms (1)

OnabotulinumtoxinA

OnabotulinumtoxinA injections at doses and frequencies as determined by the physician in accordance with clinical practice.

Biological: OnabotulinumtoxinA

Interventions

OnabotulinumtoxinA injections at doses and frequencies as determined by the physician in accordance with clinical practice.

Also known as: botulinum toxin Type A, BOTOX®
OnabotulinumtoxinA

Eligibility Criteria

Age16 Years+
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Patients with Cervical Dystonia (Dystonie)

You may qualify if:

  • Diagnosis of cervical dystonia (dystonie) and able to receive botulinum toxin Type A as deemed medically necessary by the physician

You may not qualify if:

  • Participation in a clinical trial for any botulinum toxin indication
  • Planning elective surgery during the observational study period
  • Treatment with any botulinum toxin product for cervical dystonia (dystonie)
  • Treatment with any botulinum toxin product for a non-cervical dystonia (dystonie) condition within 2 months of study start

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (8)

Clinique Neuro-Rive Sud

Greenfield Park, Quebec, J4V 2J2, Canada

Location

Hôpital Maisonneuve-Rosemont

Montreal, Quebec, H1T 2M4, Canada

Location

Chum-Notre-Dame

Montreal, Quebec, H2L 4M1, Canada

Location

Queen Elizabeth Health Centre: Medical Specialist Clinic

Montreal, Quebec, H4A 3L5, Canada

Location

CHU de Québec, Hôpital de l'Enfant-Jésus

Québec, Quebec, G1J 1Z4, Canada

Location

Centre Medical Le Mesnil

Québec, Quebec, G2K 0H1, Canada

Location

Polyclinique Medicale des Ponts

Saint Romuald, Quebec, G6W 8H1, Canada

Location

CHU - Sherbrooke

Sherbrooke, Quebec, J1H 5N4, Canada

Location

MeSH Terms

Conditions

Torticollis

Interventions

Botulinum Toxins, Type A

Condition Hierarchy (Ancestors)

DystoniaDyskinesiasNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

Botulinum ToxinsMetalloendopeptidasesEndopeptidasesPeptide HydrolasesHydrolasesEnzymesEnzymes and CoenzymesMetalloproteasesBacterial ProteinsProteinsAmino Acids, Peptides, and ProteinsBacterial ToxinsToxins, BiologicalBiological Factors

Study Officials

  • Goran Davidovic

    Allergan

    STUDY DIRECTOR

Study Design

Study Type
observational
Observational Model
CASE ONLY
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 31, 2012

First Posted

August 2, 2012

Study Start

July 1, 2012

Primary Completion

February 1, 2017

Study Completion

February 1, 2017

Last Updated

March 30, 2017

Record last verified: 2017-03

Locations