NCT01639898

Brief Summary

POEMS syndrome is a rare form of B cell dyscrasia combining a proliferation usually of plasma cells, a polyneuropathy, osteocondensing bone lesions and multiple other clinical signs. Lenalidomide appears to be particularly efficient in this pathology. The investigators propose a phase II multicentre protocol, based on the use of lenalidomide combined with dexamethasone in patients presenting a POEMS syndrome, either de novo or resistant or in relapse. Patients who can be treated by local radiation or intensive treatment with stem cell support will undergo 2 cycles of the lenalidomide-dexamethasone (Len-Dex) combination before radiation or intensive treatment (Group 1), the other patients will undergo 9 cycles of the Len-Dex combination (Group 2). A biological study is coupled with this clinical protocol in order to define the best biological markers predicting clinical responses, to better understand the POEMS pathophysiological mechanisms and to set up a bank of samples which can be used to study this rare pathology.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
51

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Jul 2012

Longer than P75 for phase_2

Geographic Reach
1 country

11 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2012

Completed
4 days until next milestone

First Submitted

Initial submission to the registry

July 5, 2012

Completed
8 days until next milestone

First Posted

Study publicly available on registry

July 13, 2012

Completed
5.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2018

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2018

Completed
Last Updated

July 5, 2019

Status Verified

July 1, 2019

Enrollment Period

5.9 years

First QC Date

July 5, 2012

Last Update Submit

July 2, 2019

Conditions

Keywords

POEMSVEGFFree lightlenalidomidedexamethasone

Outcome Measures

Primary Outcomes (2)

  • Biological outcome

    Decrease of monoclonal protein and serum VEGF level

    Two months for group 1

  • Biological outcome

    Decrease of monoclonal protein and serum VEGF level

    2, 4 or 6 month for group 2

Secondary Outcomes (1)

  • Clinical response

    2 months

Study Arms (2)

Group 1 ("2-cycles" trial)

EXPERIMENTAL

The "2-cycles" trial will be available to patients who can be treated by radiation or intensive treatment (75 % of cases occurring in front line); they will then undergo 2 cycles of the lenalidomide-dexamethasone combination before radiation or intensive treatment (Group 1).

Drug: Lenalidomide and dexamethasone

Group 2 ( "9 cylces" Trial)

EXPERIMENTAL

The "9-cycles" trial will be available to all other front-line patients (25 % of front-line patients) or patients in relapse or resistant, they will undergo 9 cycles of the lenalidomide-dexamethasone combination followed by maintenance therapy with lenalidomide alone for one year (Group 2).

Drug: Lenalidomide and dexamethasone

Interventions

2 cycles of the lenalidomide-dexamethasone (Len-Dex) combination before radiation or intensive treatment

Group 1 ("2-cycles" trial)

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients suffering from POEMS syndrome (Mayo Clinic criteria)
  • Patients with a localised disease who can be treated with radiation and those with a disseminated disease and who can be treated intensively will be included in Group 1, all other patients will be included in Group 2.
  • Patients aged of 18 or more
  • Patients who do not show uncontrolled thrombosis
  • Patients who have been duly informed and who have signed a consent form.
  • Patients must respect all the lenalidomide Pregnancy Prevention Program (PPP) requirements described in appendix of the protocol.
  • Patients registered with the French National Health System.

You may not qualify if:

  • Women who are pregnant, or suspected to be pregnant or breastfeeding
  • Pathology not linked with POEMS, contraindicating one of the studied drugs
  • Patients suffering from a deficiency which does not allow them full understanding of the trial requirements and which could compromise proper consent from the patient and/or observance of the protocol and continuous participation in the trial.
  • Prior history of malignancy other than POEMS syndrome or active other cancer or other serious illness.
  • Any contraindication to Revlimid® or to one of its excipient.
  • Patient with clearance creatinine \< 30mL/min.
  • Hepatic insufficiency
  • Patient with Absolute Neutrophil count (ANC) \< 1,0 x 109/L
  • Patient with platelet count \< 75 x 109/L
  • Use of any other experimental drug or therapy within 28 days of baseline
  • Known hypersensitivity to thalidomide
  • Instable, clinically significant ECG findings
  • Known positive for HIV, or active infectious hepatitis, type A, B or C
  • Patients under protection of a legal order.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (11)

CHU d'Angers

Angers, 49933, France

Location

CHU de Caen

Caen, 14000, France

Location

CHU de Lille

Lille, 59037, France

Location

CHU de Limoges

Limoges, 87042, France

Location

Hospices Civil de Lyon

Lyon, 69000, France

Location

Centre Léon Bérard

Lyon, 69373, France

Location

CHU de Nantes

Nantes, 44093, France

Location

Hôpital Saint-Louis

Paris, 75010, France

Location

Pitié Salpétrière

Paris, 75013, France

Location

Hôpital Necker

Paris, 75743, France

Location

CHU de Toulouse

Toulouse, 31059, France

Location

MeSH Terms

Conditions

POEMS Syndrome

Interventions

LenalidomideDexamethasone

Condition Hierarchy (Ancestors)

PolyneuropathiesPeripheral Nervous System DiseasesNeuromuscular DiseasesNervous System DiseasesParaproteinemiasBlood Protein DisordersHematologic DiseasesHemic and Lymphatic DiseasesAbnormalities, MultipleCongenital AbnormalitiesCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesImmunoproliferative DisordersImmune System Diseases

Intervention Hierarchy (Ancestors)

PhthalimidesPhthalic AcidsAcids, CarbocyclicCarboxylic AcidsOrganic ChemicalsPiperidonesPiperidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsIsoindolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingPregnadienetriolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsSteroids, Fluorinated

Study Officials

  • Arnaud JACCARD, MD

    CHU Limoges

    STUDY CHAIR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 5, 2012

First Posted

July 13, 2012

Study Start

July 1, 2012

Primary Completion

June 1, 2018

Study Completion

July 1, 2018

Last Updated

July 5, 2019

Record last verified: 2019-07

Locations