NCT01584440

Brief Summary

The objectives of the study are to evaluate the safety, tolerability and efficacy of AVP-923 compared to placebo, for the treatment of symptoms of agitation in participants with Alzheimer's Disease (AD).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
220

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Aug 2012

Geographic Reach
1 country

44 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 23, 2012

Completed
2 days until next milestone

First Posted

Study publicly available on registry

April 25, 2012

Completed
4 months until next milestone

Study Start

First participant enrolled

August 13, 2012

Completed
2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 30, 2014

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 30, 2014

Completed
7.3 years until next milestone

Results Posted

Study results publicly available

November 26, 2021

Completed
Last Updated

November 26, 2021

Status Verified

October 1, 2021

Enrollment Period

2 years

First QC Date

April 23, 2012

Results QC Date

October 29, 2021

Last Update Submit

October 29, 2021

Conditions

Keywords

AVP-923-20AVP-923-30AVP-923DextromethorphanQuinidineNeuropsychiatric InventoryAggressionEfficacySafety

Outcome Measures

Primary Outcomes (1)

  • Change in the Neuropsychiatric Inventory (NPI) Agitation/Aggression Domain Score From Day 1 (Stage 1 Baseline) to Day 36 (Stage 2 Baseline) and From Day 36 to Day 70

    The NPI is a retrospective interview covering 12 neuropsychiatric symptom domains and is used to evaluate psychopathology, neuropsychiatric manifestations, and caregiver distress. The Agitation/Aggression domain was designed to collect information on the behavioral aspects of agitation/aggression in participants with probable Alzheimer's Disease (AD) and clinically meaningful agitation secondary to AD. Each NPI domain is rated by the caregiver for symptom frequency and severity. Symptom frequency is rated as: 1, occasionally; 2, often; 3, frequently; 4, very frequently. Symptom severity is rated as: 1, mild; 2, moderate; 3, marked. The total domain score is calculated as the frequency score multiplied by the severity score and thus ranges from 1 to 12. A higher score represents worsening symptoms. Change from Baseline is calculated as the post-Baseline score minus the Baseline score. Data are reported for only those participants contributing data to the analysis.

    Day 1 (Stage 1 Baseline); Day 36 (Stage 2 Baseline); Day 70

Secondary Outcomes (21)

  • Number of Participants With the Indicated Type of Adverse Event

    up to Week 10

  • Change in the Total NPI Score From Day 1 (Stage 1 Baseline) to Day 36 (Stage 2 Baseline) and From Day 36 to Day 70

    Day 1 (Stage 1 Baseline); Day 36 (Stage 2 Baseline); Day 70

  • Change in the Individual NPI Domain Scores From Day 1 (Stage 1 Baseline) to Day 36 (Stage 2 Baseline) and From Day 36 to Day 70

    Day 1 (Stage 1 Baseline); Day 36 (Stage 2 Baseline); Day 70

  • Change in the Sum of the Agitation/Aggression, Irritability/Lability, Disinhibition, and Aberrant Motor Behavior NPI Domain (NPI4D) Score From Day 1 (Stage 1 Baseline) to Day 36 (Stage 2 Baseline) and From Day 36 to Day 70

    Day 1 (Stage 1 Baseline); Day 36 (Stage 2 Baseline); Day 70

  • Change in the Sum of the Agitation/Aggression, Irritability/Lability, Anxiety, and Aberrant Motor Behavior NPI Domain (NPI4A) Score From Day 1 (Stage 1 Baseline) to Day 36 (Stage 2 Baseline) and From Day 36 to Day 70

    Day 1 (Stage 1 Baseline); Day 36 (Stage 2 Baseline); Day 70

  • +16 more secondary outcomes

Study Arms (3)

Placebo

PLACEBO COMPARATOR

Participants will receive placebo during Stage 1 and Stage 2 of the study.

Drug: Placebo

AVP-923

EXPERIMENTAL

Participants will receive AVP-923-20 and AVP-923-30 in a sequential manner during Stage 1 and Stage 2 of the study.

Drug: AVP-923-20Drug: AVP-923-30

Placebo then AVP-923

EXPERIMENTAL

Participants will receive placebo in Stage 1 followed by AVP-923 in Stage 2.

Drug: AVP-923-20Drug: PlaceboDrug: AVP-923-30

Interventions

AVP-923-20: 20 mg of dextromethorphan and 10 mg of quinidine

Also known as: Nuedexta
AVP-923Placebo then AVP-923

Placebo capsule

PlaceboPlacebo then AVP-923

AVP-923-30: 30 mg of dextromethorphan and 10 mg of quinidine

AVP-923Placebo then AVP-923

Eligibility Criteria

Age50 Years - 90 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of probable Alzheimer's disease (AD).
  • The participant has clinically significant symptoms of agitation secondary to AD, that interfere with daily routine and for which a prescription medication is deemed indicated, in the opinion of the investigator.
  • Either out-patients or residents of an assisted-living facility or a skilled nursing home.
  • CGI-S score is ≥ 4 (moderately ill) at screening and baseline.
  • Mini Mental State Examination (MMSE) score at screening between 8 and 28 (inclusive).
  • Caregiver who is able and willing to comply with all required study procedures, ensuring that the participant attends all study visits and takes the study medication as instructed. In order to qualify as a caregiver for this study, the individual should spend time with the participant for a minimum of 4 hours on 4 separate days per week.

You may not qualify if:

  • Participant has other type of dementia (e.g., vascular dementia, frontotemporal dementia, Parkinson's disease, substance-induced dementia).
  • Participant with co-existent clinically significant or unstable systemic diseases that could confound the interpretation of the safety results of the study (e.g. malignancy, poorly controlled diabetes, poorly controlled hypertension, unstable pulmonary, renal or hepatic disease, unstable ischemic cardiac disease, dilated cardiomyopathy, certain cardiac conduction abnormalities including QTc prolongation, or unstable valvular heart disease).
  • Participant with myasthenia gravis.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (44)

Unknown Facility

Phoenix, Arizona, 85006, United States

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Unknown Facility

Sun City, Arizona, 85351, United States

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Unknown Facility

Fresno, California, 93720, United States

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Unknown Facility

Fullerton, California, 92835, United States

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Unknown Facility

Los Angeles, California, 90073, United States

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Unknown Facility

Los Angeles, California, 90095, United States

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Unknown Facility

San Diego, California, 92103, United States

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Unknown Facility

San Francisco, California, 94109, United States

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Unknown Facility

Sherman Oaks, California, 91403, United States

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Unknown Facility

Temecula, California, 92591, United States

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Unknown Facility

Boynton Beach, Florida, 33426, United States

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Unknown Facility

Deerfield Beach, Florida, 33064, United States

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Unknown Facility

Hialeah, Florida, 33012, United States

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Unknown Facility

Miami, Florida, 33122, United States

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Unknown Facility

Miami, Florida, 33137, United States

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Unknown Facility

Miami, Florida, 33173, United States

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Unknown Facility

Ocala, Florida, 34471, United States

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Unknown Facility

Orlando, Florida, 32806, United States

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Unknown Facility

Sunrise, Florida, 33351, United States

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Unknown Facility

Tampa, Florida, 33609, United States

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Unknown Facility

West Palm Beach, Florida, 33407, United States

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Unknown Facility

West Palm Beach, Florida, 33409, United States

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Unknown Facility

Weston, Florida, 33331, United States

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Unknown Facility

Elk Grove Village, Illinois, 60007, United States

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Unknown Facility

Las Vegas, Nevada, 89106, United States

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Unknown Facility

Las Vegas, Nevada, 89147, United States

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Summit, New Jersey, 07902, United States

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Toms River, New Jersey, 08757, United States

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Unknown Facility

Orangeburg, New York, 10962, United States

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Unknown Facility

Rochester, New York, 14620, United States

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Unknown Facility

White Plains, New York, 10605, United States

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Unknown Facility

Centerville, Ohio, 45459, United States

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Unknown Facility

Cincinnati, Ohio, 45227, United States

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Unknown Facility

Cleveland, Ohio, 44195, United States

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Unknown Facility

Columbus, Ohio, 43221, United States

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Unknown Facility

Lakewood, Ohio, 44107, United States

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Unknown Facility

Allentown, Pennsylvania, 18104, United States

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Unknown Facility

Reading, Pennsylvania, 19604, United States

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Unknown Facility

Charleston, South Carolina, 29401, United States

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Unknown Facility

Houston, Texas, 77030, United States

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Unknown Facility

San Antonio, Texas, 78238, United States

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Unknown Facility

Salt Lake City, Utah, 84106, United States

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Unknown Facility

Bennington, Vermont, 05201, United States

Location

Unknown Facility

Spokane, Washington, 99204, United States

Location

Related Publications (1)

  • Cummings JL, Lyketsos CG, Peskind ER, Porsteinsson AP, Mintzer JE, Scharre DW, De La Gandara JE, Agronin M, Davis CS, Nguyen U, Shin P, Tariot PN, Siffert J. Effect of Dextromethorphan-Quinidine on Agitation in Patients With Alzheimer Disease Dementia: A Randomized Clinical Trial. JAMA. 2015 Sep 22-29;314(12):1242-54. doi: 10.1001/jama.2015.10214.

    PMID: 26393847BACKGROUND

MeSH Terms

Conditions

Psychomotor AgitationAlzheimer DiseaseAggression

Interventions

dextromethorphan - quinidine combination

Condition Hierarchy (Ancestors)

DyskinesiasNeurologic ManifestationsNervous System DiseasesPsychomotor DisordersNeurobehavioral ManifestationsSigns and SymptomsPathological Conditions, Signs and SymptomsAberrant Motor Behavior in DementiaBehavioral SymptomsBehaviorDementiaBrain DiseasesCentral Nervous System DiseasesTauopathiesNeurodegenerative DiseasesNeurocognitive DisordersMental DisordersSocial Behavior

Results Point of Contact

Title
Avanir Medical Information
Organization
Avanir Pharmaceuticals, Inc.

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 23, 2012

First Posted

April 25, 2012

Study Start

August 13, 2012

Primary Completion

July 30, 2014

Study Completion

July 30, 2014

Last Updated

November 26, 2021

Results First Posted

November 26, 2021

Record last verified: 2021-10

Locations