NCT01535508

Brief Summary

Primary: to investigate tolerability of interventional high dose Vitamin D3 supplementation, titrated to reach serum levels near the high end of the reference range (30-100 ng/ml), in vitamin D deficient pediatric Autism Spectrum Disorder (ASD) patients. The study will determine if initial safety and effect estimates predict that a double blind randomized control trial (RCT) with a larger set of patients will be worthwhile in the localization of this treatment aimed at improving the symptoms of ASDs. Exploratory: to determine efficacy of high dose D3 replacement for improvement in the core symptoms of autism, including sociability, eye contact, anger outbursts, stimming behavior, and sleep, as determined by parental and clinical evaluation scales.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
10

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Feb 2012

Typical duration for phase_2

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

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Study Timeline

Key milestones and dates

Study Start

First participant enrolled

February 1, 2012

Completed
13 days until next milestone

First Submitted

Initial submission to the registry

February 14, 2012

Completed
3 days until next milestone

First Posted

Study publicly available on registry

February 17, 2012

Completed
3.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2015

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2015

Completed
Last Updated

October 9, 2019

Status Verified

October 1, 2019

Enrollment Period

3.6 years

First QC Date

February 14, 2012

Last Update Submit

October 8, 2019

Conditions

Outcome Measures

Primary Outcomes (1)

  • Clinical Global Impression Scale - Improvement (CGI-I)

    Assessment of global changes in severity of autistic symptoms. CGI-I scores formulated by the clinician based on parent interview of changes in the child's behavior and from direct clinical observation, where scores of 0 = no improvement,1 = minimally improved, 2 = much improved, and 3 = very much improved.

    Baseline and 12 weeks from Baseline

Study Arms (1)

Liquid Vitamin D

EXPERIMENTAL
Drug: Liquid Vitamin D

Interventions

300 IU/Kg/day not to exceed 10,000 IU/day.

Also known as: Ddrops
Liquid Vitamin D

Eligibility Criteria

Age3 Years - 8 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Diagnosis of Autism from DSM-IV TR and ADOS
  • Moderate but less than severe on CGI-Severity scale
  • IQ \> 40
  • ZRT 25(OH)D blood spot test \< 30 ng/ml
  • Age 3-8 years old

You may not qualify if:

  • Developmental delays prior to 12 months of age
  • history of head trauma
  • seizure in the past year
  • bleeding disorder
  • history of kidney or liver disease
  • clinically significant low white blood cell count
  • PDD-NOS, Rett's syndrome, Childhood Disintegrative Disorder or Fragile X syndrome
  • current supplementation with Vitamin D, Vitamin A or cod-liver oil

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

University of California, San Francisco

San Francisco, California, 94143, United States

Location

MeSH Terms

Conditions

Autistic DisorderVitamin D Deficiency

Condition Hierarchy (Ancestors)

Autism Spectrum DisorderChild Development Disorders, PervasiveNeurodevelopmental DisordersMental DisordersAvitaminosisDeficiency DiseasesMalnutritionNutrition DisordersNutritional and Metabolic Diseases

Study Officials

  • Robert L Hendren, DO

    University of California, San Francisco

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 14, 2012

First Posted

February 17, 2012

Study Start

February 1, 2012

Primary Completion

September 1, 2015

Study Completion

December 1, 2015

Last Updated

October 9, 2019

Record last verified: 2019-10

Locations