NCT01529840

Brief Summary

This trial is conducted in Europe. The aim of this trial is to evaluate the effect of somatropin (Norditropin®) on final height in children with Noonan syndrome having being treated for up to 10 years with somatropin (Norditropin®) for the attainment of an optimal final height in the original trial S/GHD/004/NOO.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
24

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Jun 1990

Longer than P75 for phase_3

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 1990

Completed
15.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2005

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2005

Completed
6.3 years until next milestone

First Submitted

Initial submission to the registry

January 2, 2012

Completed
1 month until next milestone

First Posted

Study publicly available on registry

February 9, 2012

Completed
Last Updated

January 18, 2017

Status Verified

January 1, 2017

Enrollment Period

15.3 years

First QC Date

January 2, 2012

Last Update Submit

January 17, 2017

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change in height SDS (Standard Deviation Score) from start of treatment to final height (referenced to normal population)

Secondary Outcomes (7)

  • Final height SDS

  • Change in height SDS from start of treatment to final height (referenced to Noonan population)

  • Height velocity

  • Change in height velocity

  • Sitting height

  • +2 more secondary outcomes

Study Arms (2)

Low dose 33 mcg/kg/day

EXPERIMENTAL
Drug: somatropin

High dose 66 mcg/kg/day

EXPERIMENTAL
Drug: somatropin

Interventions

Retrospective data collection based on data obtained from a prospective, open-label, randomised, parallel-group trial (S/GHD/004/NOO) combined with a present follow-up visit

Low dose 33 mcg/kg/day

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participation in the original S/GHD/004/NOO trial or following the protocol for S/GHD/004/NOO without being randomised in the trial

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Novo Nordisk Investigational Site

Gothenburg, 416 85, Sweden

Location

Related Publications (1)

  • Osio D, Dahlgren J, Wikland KA, Westphal O. Improved final height with long-term growth hormone treatment in Noonan syndrome. Acta Paediatr. 2005 Sep;94(9):1232-7. doi: 10.1111/j.1651-2227.2005.tb02081.x.

Related Links

MeSH Terms

Conditions

Genetic Diseases, InbornNoonan Syndrome

Interventions

Human Growth Hormone

Condition Hierarchy (Ancestors)

Congenital, Hereditary, and Neonatal Diseases and AbnormalitiesCraniofacial AbnormalitiesMusculoskeletal AbnormalitiesMusculoskeletal DiseasesHeart Defects, CongenitalCardiovascular AbnormalitiesCardiovascular DiseasesHeart DiseasesCongenital AbnormalitiesConnective Tissue DiseasesSkin and Connective Tissue Diseases

Intervention Hierarchy (Ancestors)

Growth HormonePituitary Hormones, AnteriorPituitary HormonesPeptide HormonesHormonesHormones, Hormone Substitutes, and Hormone AntagonistsPeptidesAmino Acids, Peptides, and Proteins

Study Officials

  • Global Clinical Registry (GCR, 1452)

    Novo Nordisk A/S

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 2, 2012

First Posted

February 9, 2012

Study Start

June 1, 1990

Primary Completion

September 1, 2005

Study Completion

September 1, 2005

Last Updated

January 18, 2017

Record last verified: 2017-01

Locations