NCT01522716

Brief Summary

The aim of the study is to evaluate the safety and efficacy of mesenchymal stromal cells as treatment for steroid-refractory chronic graft-versus-host disease.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
11

participants targeted

Target at below P25 for phase_1

Timeline
Completed

Started Aug 2011

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

August 1, 2011

Completed
6 months until next milestone

First Submitted

Initial submission to the registry

January 24, 2012

Completed
8 days until next milestone

First Posted

Study publicly available on registry

February 1, 2012

Completed
4.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2016

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2017

Completed
Last Updated

November 25, 2020

Status Verified

November 1, 2020

Enrollment Period

4.6 years

First QC Date

January 24, 2012

Last Update Submit

November 23, 2020

Conditions

Outcome Measures

Primary Outcomes (1)

  • Change in disease activity according to National Institute of Health criteria

    Patients are evaluated according to NIH criteria at 3, 6 and (if applicable) 9 months after initialising MSC treatment, and the score compared to baseline score.

    Baseline to 9 months

Secondary Outcomes (4)

  • Change in disease activity as measured by histological examination

    Baseline to 9 months

  • Change in self-assessed disease activity and quality of life

    Baseline to 9 months

  • Safety (Adverse events, infections and relapse)

    21 months

  • Freedom from steroids at 1 year after MSC treatment

    1 year after finishing treatment

Study Arms (1)

Mesenchymal stromal cell treatment

EXPERIMENTAL
Biological: Mesenchymal stromal cells

Interventions

Allogenous mesenchymal stromal cells, to be injected intravenously at a dose of 1-2 million/kg at a frequency of once a month (frequency may be changed during the study if deemed appropriate by investigators) for 6-9 months.

Mesenchymal stromal cell treatment

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Chronic graft-versus-host disease, grade moderate or severe despite at least 3 months treatment with calcineurin inhibitors and steroids OR
  • Chronic graft-versus-host disease, grade moderate or severe, where full treatment with calcineurin inhibitors and steroids is impossible due to intolerable side-effects

You may not qualify if:

  • Active malignancy
  • Fulfilling criteria for previously initiated study for treatment of chronic graft-versus-host disease

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Hematology Center, Karolinska University Hospital Huddinge

Stockholm, Sweden

Location

Related Publications (1)

  • Boberg E, von Bahr L, Afram G, Lindstrom C, Ljungman P, Heldring N, Petzelbauer P, Garming Legert K, Kadri N, Le Blanc K. Treatment of chronic GvHD with mesenchymal stromal cells induces durable responses: A phase II study. Stem Cells Transl Med. 2020 Oct;9(10):1190-1202. doi: 10.1002/sctm.20-0099. Epub 2020 Jun 23.

MeSH Terms

Conditions

Graft vs Host Disease

Condition Hierarchy (Ancestors)

Immune System Diseases

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Leg läkare

Study Record Dates

First Submitted

January 24, 2012

First Posted

February 1, 2012

Study Start

August 1, 2011

Primary Completion

March 1, 2016

Study Completion

March 1, 2017

Last Updated

November 25, 2020

Record last verified: 2020-11

Locations