NCT01509677

Brief Summary

The objective of the Biopsy trial is to investigate the effect of roflumilast 500 µg tablets once daily versus placebo on inflammation parameters in bronchial biopsy tissue specimen and additional in sputum and blood serum. Also data on safety status will be obtained. Patients to be included required to have moderate to severe COPD associated with chronic bronchitis. The total duration of this randomized, multicentre, phase III trial is 24 weeks maximum.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
158

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Feb 2012

Typical duration for phase_3

Geographic Reach
5 countries

20 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 21, 2011

Completed
23 days until next milestone

First Posted

Study publicly available on registry

January 13, 2012

Completed
19 days until next milestone

Study Start

First participant enrolled

February 1, 2012

Completed
4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2016

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2016

Completed
3.8 years until next milestone

Results Posted

Study results publicly available

November 29, 2019

Completed
Last Updated

November 29, 2019

Status Verified

November 1, 2019

Enrollment Period

4 years

First QC Date

December 21, 2011

Results QC Date

January 23, 2017

Last Update Submit

November 27, 2019

Conditions

Keywords

RoflumilastChronic Obstructive Pulmonary DiseaseCOPD

Outcome Measures

Primary Outcomes (2)

  • Number of CD8+ Inflammatory Cells in Bronchial Biopsy Tissue.

    16 weeks

  • Change in Number of CD8+ Inflammatory Cells in Bronchial Biopsy Tissue

    Baseline to 16 weeks

Secondary Outcomes (31)

  • CD68+ Count in Biopsied Material (Submucosa)

    16 weeks

  • CD68+ Cell Count in Biopsied Material (Submucosa): Poisson Regression (Ratio)

    16 weeks

  • Change From V2 to V6 in CD68+ Cell Count (Cells/mm^2) in Biopsied Material (Submucosa) (ITT)

    Baseline and 16 weeks

  • CD4+ Cell Counts in Biopsied Material (Submucosa):Poisson Regression Model

    16 weeks

  • CD45+ Cell Counts in Biopsied Material (Submucosa):Poisson Regression Model

    16 weeks

  • +26 more secondary outcomes

Study Arms (2)

Roflumilast

ACTIVE COMPARATOR

500 μg tablet, once daily, oral administration in the morning after breakfast

Drug: Roflumilast

Placebo

PLACEBO COMPARATOR

tablet, once daily, oral administration in the morning after breakfast

Drug: Placebo

Interventions

500 μg tablet, once daily, oral administration in the morning after breakfast

Also known as: Daxas
Roflumilast

tablet, once daily, oral administration in the morning after breakfast

Also known as: Placebo to Roflumilast
Placebo

Eligibility Criteria

Age40 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Giving written informed consent
  • History of COPD (according to GOLD 2009) for at least 12 months prior to baseline visit V0 associated with chronic productive cough for at least three months in each of the two years prior to baseline visit V0 (with other causes of productive cough excluded)
  • Outpatients 40-80 years of age
  • Post-bronchodilator 30% ≤FEV1 ≤80% predicted
  • Post-bronchodilator FEV1/FVC ratio ≤70%
  • Current or former smokers with smoking history ≥20 pack years

You may not qualify if:

  • Criteria affecting the read-out parameters of the trial:
  • Clinical instability, defined as experiencing a COPD exacerbation six months prior to V0
  • An upper/lower respiratory tract infection which has not resolved four weeks prior to V0
  • Diagnosis of asthma and/or other relevant lung disease
  • Known alpha-1-antitrypsin deficiency
  • Suspicion or diagnosis of a bleeding disorders irrespective of its pathophysiological mechanism

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (20)

Unknown Facility

København NV, DK-2400, Denmark

Location

Unknown Facility

København NV, Denmark

Location

Unknown Facility

Freiburg im Breisgau, Germany

Location

Unknown Facility

Großhansdorf, Germany

Location

Unknown Facility

Hanover, Germany

Location

Unknown Facility

Heidelberg, Germany

Location

Unknown Facility

Immenhausen, Germany

Location

Unknown Facility

Kiel, Germany

Location

Unknown Facility

Mainz, Germany

Location

Unknown Facility

Bialystok, Poland

Location

Unknown Facility

Krakow, Poland

Location

Unknown Facility

Lodz, 90-153, Poland

Location

Unknown Facility

Lodz, Poland

Location

Unknown Facility

Lund, Sweden

Location

Unknown Facility

Cottingham, United Kingdom

Location

Unknown Facility

Dafen, United Kingdom

Location

Unknown Facility

Leicester, United Kingdom

Location

Unknown Facility

London, United Kingdom

Location

Unknown Facility

Manchester, United Kingdom

Location

Unknown Facility

Norwich, NR4 7UY, United Kingdom

Location

Related Publications (1)

  • Rabe KF, Watz H, Baraldo S, Pedersen F, Biondini D, Bagul N, Hanauer G, Gohring UM, Purkayastha D, Roman J, Alagappan VKT, Saetta M. Anti-inflammatory effects of roflumilast in chronic obstructive pulmonary disease (ROBERT): a 16-week, randomised, placebo-controlled trial. Lancet Respir Med. 2018 Nov;6(11):827-836. doi: 10.1016/S2213-2600(18)30331-X. Epub 2018 Sep 14.

Related Links

MeSH Terms

Conditions

Pulmonary Disease, Chronic Obstructive

Interventions

Roflumilast

Condition Hierarchy (Ancestors)

Lung Diseases, ObstructiveLung DiseasesRespiratory Tract DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
AstraZeneca Clinical Study Information Center
Organization
AstraZeneca

Study Officials

  • AstraZeneca AstraZeneca

    AstraZeneca

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 21, 2011

First Posted

January 13, 2012

Study Start

February 1, 2012

Primary Completion

February 1, 2016

Study Completion

February 1, 2016

Last Updated

November 29, 2019

Results First Posted

November 29, 2019

Record last verified: 2019-11

Locations