NCT01500681

Brief Summary

Neuromyelitis optica (NMO) is an inflammatory disease of the central nervous system that is associated with autoantibodies to aquaporin-4. Treatment options for prevention of clinical relapses of NMO include immunosuppressive medications. Plasma exchange (PLEX) is commonly used as a rescue therapy for NMO relapses but ongoing, regular PLEX procedures (maintenance PLEX) is sometimes used to prevent relapses. This observational registry will record feasibility, tolerability, safety, and preliminary efficacy data regarding maintenance PLEX for NMO.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
9

participants targeted

Target at below P25 for all trials

Timeline
Completed

Started Jun 2012

Typical duration for all trials

Geographic Reach
1 country

2 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

December 23, 2011

Completed
5 days until next milestone

First Posted

Study publicly available on registry

December 28, 2011

Completed
5 months until next milestone

Study Start

First participant enrolled

June 1, 2012

Completed
3.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 9, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 9, 2015

Completed
Last Updated

December 27, 2021

Status Verified

December 1, 2021

Enrollment Period

3.1 years

First QC Date

December 23, 2011

Last Update Submit

December 7, 2021

Conditions

Outcome Measures

Primary Outcomes (3)

  • Number of participants who complete planned maintenance PLEX regimen

    One year

  • Number of participants with adverse events

    One year

  • Annualized clinical relapse rate

    One year

Secondary Outcomes (1)

  • Median Expanded Disability Status Score (EDSS)

    One year

Study Arms (1)

Maintenance PLEX

Procedure: Plasma exchange (PLEX)

Interventions

Regular maintenance PLEX courses, typically 3 procedures monthly

Maintenance PLEX

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Neuromyelitis optica/CNS demyelinating disease specialty clinics

You may qualify if:

  • Neuromyelitis optica
  • Neuromyelitis optica spectrum disorder
  • Recurrent idiopathic longitudinally extensive myelitis
  • Age 18 years or greater

You may not qualify if:

  • Any condition that in the opinion of the investigator could increase a participant's risk by participating in the observational study or confound the outcome of the study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Mayo Clinic

Scottsdale, Arizona, 85259, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

Related Links

MeSH Terms

Conditions

Neuromyelitis Optica

Interventions

Plasma Exchange

Condition Hierarchy (Ancestors)

Myelitis, TransverseDemyelinating Autoimmune Diseases, CNSAutoimmune Diseases of the Nervous SystemNervous System DiseasesOptic NeuritisOptic Nerve DiseasesCranial Nerve DiseasesDemyelinating DiseasesEye DiseasesAutoimmune DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

Blood TransfusionBiological TherapyTherapeuticsPlasmapheresisBlood Component RemovalSorption DetoxificationExtracorporeal CirculationSurgical Procedures, Operative

Study Officials

  • Dean M Wingerchuk, MD

    Mayo Clinic

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Principal Investigator

Study Record Dates

First Submitted

December 23, 2011

First Posted

December 28, 2011

Study Start

June 1, 2012

Primary Completion

July 9, 2015

Study Completion

July 9, 2015

Last Updated

December 27, 2021

Record last verified: 2021-12

Locations