NCT01495403

Brief Summary

This is a pilot study to see if hydroxychloroquine (HCQ) if safe and effective to use with patients having cramps due to their cirrhotic liver disease.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
3

participants targeted

Target at below P25 for early_phase_1

Timeline
Completed

Started Dec 2011

Typical duration for early_phase_1

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

December 1, 2011

Completed
15 days until next milestone

First Submitted

Initial submission to the registry

December 16, 2011

Completed
4 days until next milestone

First Posted

Study publicly available on registry

December 20, 2011

Completed
3.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2015

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2015

Completed
Last Updated

May 3, 2023

Status Verified

May 1, 2023

Enrollment Period

3.3 years

First QC Date

December 16, 2011

Last Update Submit

May 2, 2023

Conditions

Keywords

liver cirrhosismuscle cramps

Outcome Measures

Primary Outcomes (1)

  • frequency and severity of muscle cramps in cirrhotic patients reporting the symptom, based on the modified muscle cramps questionnaire (mMCQ)

    Patients will be given the mMCQ and SF-12 to complete. These instruments will be scored according to established algorithms. Data analysis will include descriptive statistics (frequency, duration and severity of muscle cramps) and correlation between overall quality of life and the mMCQ summary score.

    1 month after completion of questionnaire

Secondary Outcomes (1)

  • safety and efficacy of HCQ for severe cramping using mMCQ, SF-12, and AE inventory.

    28 days after first dose

Study Arms (1)

hydroxychloroquine

EXPERIMENTAL
Drug: Hydroxychloroquine

Interventions

daily dosing

Also known as: Plaquenil
hydroxychloroquine

Eligibility Criteria

Age21 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • previous diagnosis of cirrhosis
  • adult (\>21 years)
  • able to complete a written questionnaire in English
  • stable and ambulatory
  • MELD score \< 25, Platelet count \>25,000

You may not qualify if:

  • people allergic to hydroxychloroquine, 4-aminoquinolone derivatives or any component of the formulation
  • previous diagnosis of retinal or visual field changes attributable to 4-aminoquinolone
  • previous diagnosis of porphyria
  • previous diagnosis of psoriasis
  • fulminant hepatic failure
  • pregnant women

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

MeSH Terms

Conditions

Liver CirrhosisMuscle Cramp

Interventions

Hydroxychloroquine

Condition Hierarchy (Ancestors)

Liver DiseasesDigestive System DiseasesFibrosisPathologic ProcessesPathological Conditions, Signs and SymptomsMuscular DiseasesMusculoskeletal DiseasesNeuromuscular ManifestationsNeurologic ManifestationsNervous System DiseasesSigns and Symptoms

Intervention Hierarchy (Ancestors)

ChloroquineAminoquinolinesQuinolinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds

Study Officials

  • Patrick Kamath, MD

    Mayo Clinic

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
early phase 1
Allocation
NA
Masking
NONE
Purpose
SUPPORTIVE CARE
Intervention Model
SINGLE GROUP
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
PI

Study Record Dates

First Submitted

December 16, 2011

First Posted

December 20, 2011

Study Start

December 1, 2011

Primary Completion

April 1, 2015

Study Completion

April 1, 2015

Last Updated

May 3, 2023

Record last verified: 2023-05

Locations