NCT01420081

Brief Summary

This study will investigate the individual safety and efficacy of two dual PI3K/mTOR inhibitors in patients with recurrent endometrial cancer.

Trial Health

63
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
67

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jan 2012

Typical duration for phase_2

Geographic Reach
8 countries

51 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 17, 2011

Completed
2 days until next milestone

First Posted

Study publicly available on registry

August 19, 2011

Completed
5 months until next milestone

Study Start

First participant enrolled

January 19, 2012

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 30, 2014

Completed
1.1 years until next milestone

Results Posted

Study results publicly available

May 19, 2015

Completed
7 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 25, 2015

Completed
Last Updated

January 8, 2019

Status Verified

December 1, 2018

Enrollment Period

2.3 years

First QC Date

August 17, 2011

Results QC Date

April 30, 2015

Last Update Submit

December 19, 2018

Conditions

Keywords

uterine neoplasmsendometrialuterinecancerPI3KmTORPI3K/mTORrecurrentmetastatic

Outcome Measures

Primary Outcomes (2)

  • Clinical Benefit Response for PF-04691502

    Clinical benefit response was defined as best overall response of complete response (CR), partial response (PR) or stable disease (SD) for at least 16 weeks from Cycle 1 Day 1 (C1D1) to the first time of disease progression. The outcome data table below presents the number of participants with clinical benefit response as "yes" or "no". On 09 Oct 2012, Pfizer decided to stop enrollment into PF-04691502. While tumor assessment for PF-04691502 was included as a listing in the final report, formal efficacy analysis for PF-04691502 was not performed.

    16 weeks from Cycle 1 Day 1

  • Percentage of Participants With Clinical Benefit Response for PF-05212384

    Clinical benefit response was defined as best overall response of complete response (CR), partial response (PR) or stable disease (SD) for at least 16 weeks from Cycle 1 Day 1 (C1D1) to the first time of disease progression. The primary analysis is based on the clinical benefit rate which is calculated as proportion of participants with a clinical benefit response relative to total number of response evaluable participants. Per RECIST v1.1 for target lesions: CR defined as disappearance of all target lesions; PR defined as \>=30% decrease in the sum of the longest diameter of target lesions; SD does not qualify for CR, PR or Progression. All target lesions must be assessed. SD can follow PR only in the rare case that the sum increases by less than 20% from the nadir, but enough that a previously documented 30% decrease no longer holds. A Clopper-Pearson exact 95% CI for the clinical benefit rate is presented in the below table.

    16 weeks from Cycle 1 Day 1

Secondary Outcomes (24)

  • Objective Response for PF-04691502

    Randomization to objective progression, death or last tumor assessment without progression (up to 12 months)

  • Percentage of Participants With Objective Response for PF-05212384

    Randomization to objective progression, death or last tumor assessment without progression (up to 12 months)

  • Progression Free Survival for PF-04691502

    From Cycle 1 Day 1 to objective progressive disease or death due to any cause whichever occurs first (up to 12 months)

  • Progression Free Survival for PF-05212384

    From Cycle 1 Day 1 to objective progressive disease or death due to any cause whichever occurs first (up to 12 months)

  • Percentage of Participants With Progression Free Survival (PFS) at 6 Months for PF-05212384

    6 months

  • +19 more secondary outcomes

Study Arms (3)

B

EXPERIMENTAL

PI3K Basal, IV Compound

Drug: PF-05212384

C

EXPERIMENTAL

PI3K Activated, Oral Compound

Drug: PF-05212384

F

EXPERIMENTAL

Japanese lead in cohort, IV compound

Drug: PF-05212384

Interventions

154mg IV weekly

Also known as: PKI-587
B

Eligibility Criteria

Age18 Years+
Sexfemale(Gender-based eligibility)
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Recurrent endometrial carcinoma
  • Disease progression following one or two lines of prior treatment with platinum containing chemotherapy
  • Tumor tissue available at time of screening for PI3K analysis
  • Adequate performance status
  • Adequate glucose control, bone marrow, kidney, liver, and heart function

You may not qualify if:

  • More than 2 prior cytotoxic chemo regimens for endometrial carcinoma
  • Prior therapy with an agent known to be a PI3K, and or mTOR and or AKT inhibitor
  • Active brain metastases

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (51)

University of Alabama at Birmingham

Birmingham, Alabama, 35233, United States

Location

University of Alabama at Birmingham, IDS Pharmacy

Birmingham, Alabama, 35249, United States

Location

University of Alabama at Birmingham

Birmingham, Alabama, 35249, United States

Location

University of California Medical Center

La Jolla, California, 92037, United States

Location

Moores UC San Diego Cancer Center

La Jolla, California, 92093, United States

Location

University of California Medical Center

San Diego, California, 92103, United States

Location

Mercy Hospital

Miami, Florida, 33133, United States

Location

Mercy Research Institute

Miami, Florida, 33133, United States

Location

University of Chicago Medical Center

Chicago, Illinois, 60637, United States

Location

University of Chicago Medicine Comprehensive Cancer Center at Silver Cross Hospital

New Lenox, Illinois, 60451, United States

Location

University of Kansas

Fairway, Kansas, 66205, United States

Location

University of Kansas Hospital

Kansas City, Kansas, 66160, United States

Location

University of Kansas Cancer Center and Medical Pavilion

Westwood, Kansas, 66205, United States

Location

Mary Bird Perkins Cancer Center at St. Tammany Parish Hospital

Covington, Louisiana, 70433, United States

Location

Women's Cancer Care

Covington, Louisiana, 70433, United States

Location

Women's Cancer Care

Metairie, Louisiana, 70006, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Brigham and Women's Hospital

Boston, Massachusetts, 02115, United States

Location

Dana Farber Cancer Institute

Boston, Massachusetts, 02215, United States

Location

University of Michigan

Ann Arbor, Michigan, 48109, United States

Location

University of New Mexico Cancer Center

Albuquerque, New Mexico, 87106, United States

Location

Peter MacCallum Cancer Centre, Division of Cancer Madicine

East Melbourne, Victoria, 3002, Australia

Location

Foothills Medical Center

Calgary, Alberta, T2N 2T9, Canada

Location

Tom Baker Cancer Centre

Calgary, Alberta, T2N 4N2, Canada

Location

British Columbia Cancer Agency - Vancouver Centre

Vancouver, British Columbia, V5Z 4E6, Canada

Location

Cancer Centre of Southeastern Ontario at Kingston General Hospital

Kingston, Ontario, K7L 5P9, Canada

Location

Princess Margaret Hospital

Toronto, Ontario, M5G 2M9, Canada

Location

Royal Victoria Hospital

Montreal, Quebec, H3A 1A1, Canada

Location

Jewish General Hospital

Montreal, Quebec, H3T 1E2, Canada

Location

St. Mary's Hospital

Montreal, Quebec, H3T 1M5, Canada

Location

Aichi cancer center hospital

Nagoya, Aichi-ken, 464-8681, Japan

Location

Hyogo Cancer Center

Akashi, Hyōgo, 673-8558, Japan

Location

Saitama Medical University International Medical Center

Hidaka, Saitama, 350-1298, Japan

Location

National Cancer Center Hospital

Chuo-Ku, Tokyo, 104-0045, Japan

Location

Regionalny Osrodek Onkologiczny Wojewodzki Szpital Specjalistyczny im. M. Kopernika

Lodz, 93-509, Poland

Location

Zaklad Radiologii

Lodz, 93-513, Poland

Location

Centrum Onkologii Ziemi Lubelskiej im. Św. Jana z Dukli

Lublin, 20-090, Poland

Location

Federal State Healthcare Institution

Lermontov, Stavropol Territory, 357340, Russia

Location

Clinical Oncology Dispensary 1 of Department of Healthcare of the Krasnodar Region

Krasnodar, 350040, Russia

Location

Pyatigorsk Oncology Center

Pyatigorsk, 357502, Russia

Location

Saint Petersburg State Healthcare Institution City Clinical Oncology Dispensary

Saint Petersburg, 198255, Russia

Location

Hospital Universitari Vall d'hebron

Barcelona, 08035, Spain

Location

Centro Oncologico MD Anderson Internacional España

Madrid, 28033, Spain

Location

Hospital Clinico San Carlos

Madrid, 28040, Spain

Location

Hospital Universitario La Paz

Madrid, 28046, Spain

Location

Fundacion Instituto Valenciano de Oncologia - I.V.O.

Valencia, 46009, Spain

Location

Fundacion Instituto Valenciano de Oncologia - I.V.O

Valencia, 46009, Spain

Location

The Royal Marsden NHS Foundation Trust

Sutton, Surrey, SM2 5PT, United Kingdom

Location

Beatson Oncology Centre

Glasgow, G12 0YN, United Kingdom

Location

University College London Hospital NHS Foundation Trust

London, NW1 2PG, United Kingdom

Location

The Royal Marsden NHS Foundation Trust

London, SW3 6JJ, United Kingdom

Location

Related Publications (1)

  • Del Campo JM, Birrer M, Davis C, Fujiwara K, Gollerkeri A, Gore M, Houk B, Lau S, Poveda A, Gonzalez-Martin A, Muller C, Muro K, Pierce K, Suzuki M, Vermette J, Oza A. A randomized phase II non-comparative study of PF-04691502 and gedatolisib (PF-05212384) in patients with recurrent endometrial cancer. Gynecol Oncol. 2016 Jul;142(1):62-69. doi: 10.1016/j.ygyno.2016.04.019. Epub 2016 Apr 24.

Related Links

MeSH Terms

Conditions

Endometrial NeoplasmsUterine NeoplasmsNeoplasmsRecurrenceNeoplasm Metastasis

Interventions

gedatolisib

Condition Hierarchy (Ancestors)

Genital Neoplasms, FemaleUrogenital NeoplasmsNeoplasms by SiteUterine DiseasesGenital Diseases, FemaleFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesGenital DiseasesDisease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsNeoplastic Processes

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer, Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 17, 2011

First Posted

August 19, 2011

Study Start

January 19, 2012

Primary Completion

April 30, 2014

Study Completion

December 25, 2015

Last Updated

January 8, 2019

Results First Posted

May 19, 2015

Record last verified: 2018-12

Data Sharing

IPD Sharing
Will share

Pfizer will provide access to individual de-identified participant data and related study documents (e.g. protocol, Statistical Analysis Plan (SAP), Clinical Study Report (CSR)) upon request from qualified researchers, and subject to certain criteria, conditions, and exceptions. Further details on Pfizer's data sharing criteria and process for requesting access can be found at: https://www.pfizer.com/science/clinical\_trials/trial\_data\_and\_results/data\_requests.

More information

Locations