NCT01397422

Brief Summary

This is a multi-center, randomized, double-blind, placebo-controlled, 4-arm parallel group study to evaluate the tolerability and efficacy of each of three dose levels of ADS-5102 oral capsules, an extended release formulation of amantadine, dosed once daily for the treatment of levodopa-induced dyskinesia (LID) in subjects with Parkinson's disease (PD). The novel pharmacokinetic profile of ADS-5102 is expected to achieve i) higher amantadine plasma concentrations during daytime hours when dyskinesia as well as motor and non-motor symptoms of PD are most problematic, ii) low amantadine plasma concentrations overnight, which may reduce the sleep disturbances and vivid dreams occasionally associated with amantadine, and iii) a reduced initial rate of rise in plasma concentration, which is expected to improve overall tolerability of amantadine.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
83

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Jul 2011

Geographic Reach
1 country

33 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2011

Completed
17 days until next milestone

First Submitted

Initial submission to the registry

July 18, 2011

Completed
1 day until next milestone

First Posted

Study publicly available on registry

July 19, 2011

Completed
1.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2013

Completed
5 months until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2013

Completed
4.1 years until next milestone

Results Posted

Study results publicly available

November 6, 2017

Completed
Last Updated

December 13, 2017

Status Verified

November 1, 2017

Enrollment Period

1.8 years

First QC Date

July 18, 2011

Results QC Date

October 7, 2017

Last Update Submit

November 17, 2017

Conditions

Keywords

Levodopa-induced dyskinesiaParkinsonism

Outcome Measures

Primary Outcomes (1)

  • Change in the Unified Dyskinesia Rating Scale (UDysRS) Total Score From Baseline to Week 8

    The UDysRS is a dyskinesia rating scale from 0-104, and it evaluates involuntary movements associated with PD. A higher score indicates more severe PD. The last observation carried forward (LOCF) method was used for analysis. Participants were summarized according to the actual treatment received.

    Baseline (Day 1) and Week 8

Secondary Outcomes (5)

  • Change in the Fatigue Severity Score (FSS) From Baseline to Week 8

    Baseline (Day 1) and Week 8

  • Change in Total Objective Score (III, IV) of the UDysRS From Baseline to Week 8

    Baseline (Day 1) and Week 8

  • Change in ON Time Without Troublesome Dyskinesia (ON Without Dyskinesia Plus ON With Non-troublesome Dyskinesia) From Baseline to Week 8; Based on a Standardized PD Home Diary

    Baseline (Day 1) and Week 8

  • Change in Unified Parkinson's Disease Rating Scale (MDS-UPDRS) Combined Scores (Parts I, II, III) From Baseline to Week 8

    Baseline (Day 1) and Week 8

  • Clinician's Global Impression of Change (CGI-C) in Overall PD Symptoms From Baseline to Week 8

    Baseline (Day 1) and Week 8

Study Arms (4)

Treatment A

PLACEBO COMPARATOR
Drug: ADS-5102 (extended release amantadine HCl)

Treatment B

ACTIVE COMPARATOR

Low dose ADS-5102 (amantadine extended release)

Drug: ADS-5102 (extended release amantadine HCl)

Treatment C

ACTIVE COMPARATOR

A mid-dose ADS-5102 (amantadine extended release)

Drug: ADS-5102 (extended release amantadine HCl)

Treatment D

ACTIVE COMPARATOR

High dose ADS-5102 (amantadine extended release)

Drug: ADS-5102 (extended release amantadine HCl)

Interventions

Oral capsules to be administered once daily at bedtime, for 8 weeks

Treatment ATreatment BTreatment CTreatment D

Eligibility Criteria

Age30 Years - 85 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Signed a current IRB/IEC-approved informed consent form
  • Parkinson's disease, per UK Parkinson's Disease Society (UKPDS) Brain Bank Clinical Diagnostic Criteria
  • On a stable regimen of antiparkinson's medications , including any levodopa preparation administered not less than three times daily, and willing to continue the same doses and regimens during study participation
  • Experiencing troublesome dyskinesia following levodopa dosing (peak dose dyskinesia)
  • Able to understand and complete a standardized PD home diary, following training

You may not qualify if:

  • History of neurosurgical intervention related to Parkinson's disease (e.g. deep brain stimulation)
  • History of seizures or stroke/TIA within 2 years of screening
  • History of cancer within 5 years of screening, except adequately treated non-melanomatous skin cancers, localized bladder cancer, non-metastatic prostate cancer or in situ cervical cancer
  • Estimated GFR \< 50 mL/min/1.73m2
  • Presence of cognitive impairment, as evidenced by a Mini-Mental Status Examination (MMSE) score of less than 24 during screening
  • If female, is pregnant or lactating, or has a positive pregnancy test result pre-dose
  • If a sexually active female, is not surgically sterile or at least 2 years post-menopausal, or does not agree to utilize an effective method of contraception from screening through at least 4 weeks after the completion of study treatment
  • Treatment with an investigational drug or device within 30 days prior to screening
  • Treatment with an investigational biologic within 6 months prior to screening

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (33)

Unknown Facility

Sun City, Arizona, United States

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Fountain Valley, California, United States

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Long Beach, California, United States

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Los Angeles, California, United States

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Oxnard, California, United States

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Pasadena, California, United States

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Reseda, California, United States

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Sunnyvale, California, United States

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Ventura, California, United States

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Fairfield, Connecticut, United States

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Boca Raton, Florida, United States

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Bradenton, Florida, United States

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Port Charlotte, Florida, United States

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Tampa, Florida, United States

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Atlanta, Georgia, United States

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Augusta, Georgia, United States

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Chicago, Illinois, United States

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Winfield, Illinois, United States

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Des Moines, Iowa, United States

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Kansas City, Kansas, United States

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Boston, Massachusetts, United States

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West Bloomfield, Michigan, United States

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Toms River, New Jersey, United States

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New York, New York, United States

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Durham, North Carolina, United States

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Raleigh, North Carolina, United States

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Toledo, Ohio, United States

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Tulsa, Oklahoma, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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Richmond, Virginia, United States

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Kirkland, Washington, United States

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Milwaukee, Wisconsin, United States

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MeSH Terms

Conditions

DyskinesiasParkinson DiseaseParkinsonian Disorders

Condition Hierarchy (Ancestors)

Movement DisordersCentral Nervous System DiseasesNervous System DiseasesNeurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and SymptomsBasal Ganglia DiseasesBrain DiseasesSynucleinopathiesNeurodegenerative Diseases

Results Point of Contact

Title
Head, Regulatory Affairs
Organization
Adamas Pharmaceuticals, Inc.

Study Officials

  • Clinical Trials Director

    Adamas Pharmaceuticals, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

July 18, 2011

First Posted

July 19, 2011

Study Start

July 1, 2011

Primary Completion

May 1, 2013

Study Completion

October 1, 2013

Last Updated

December 13, 2017

Results First Posted

November 6, 2017

Record last verified: 2017-11

Locations