NCT01395524

Brief Summary

The purpose of this study is to evaluate the effect and safety of NKTR-118 treatment of opioid-induced constipation in patients with non-cancer-related pain over a 6-month period.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
302

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Jul 2011

Shorter than P25 for phase_3

Geographic Reach
4 countries

116 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

June 28, 2011

Completed
3 days until next milestone

Study Start

First participant enrolled

July 1, 2011

Completed
14 days until next milestone

First Posted

Study publicly available on registry

July 15, 2011

Completed
1.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2012

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2012

Completed
2.8 years until next milestone

Results Posted

Study results publicly available

June 17, 2015

Completed
Last Updated

February 23, 2017

Status Verified

January 1, 2017

Enrollment Period

1.2 years

First QC Date

June 28, 2011

Results QC Date

October 13, 2014

Last Update Submit

January 9, 2017

Conditions

Keywords

Non-Cancer-Related PainOpioid-Induced Constipation.

Outcome Measures

Primary Outcomes (3)

  • Incidence of Patients Experiencing at Least One Adverse Event (AE)

    The incidence of patients experiencing at least one AE during the randomized treatment and follow-up periods was calculated.

    Baseline (Week 0) to end of the follow-up period (Week 14)

  • Incidence of Patients Experiencing AEs That Resulted in Discontinuation of Investigational Product (IP)

    The incidence of patients experiencing AEs that resulted in discontinuation of IP during the randomized treatment or follow-up periods was calculated.

    Baseline (Week 0) to end of the follow-up period (Week 14)

  • Incidence of Patients Experiencing Severe Adverse Events (SAEs)

    The incidence of patients experiencing SAEs during the randomized treatment and follow-up periods was calculated.

    Baseline (Week 0) to end of the follow-up period (Week 14)

Secondary Outcomes (2)

  • Change From Baseline in Patient Assessment of Constipation Symptoms Questionnaire (PAC-SYM)

    Baseline (prior to treatment) to last on-treatment assessment (up to Week 12)

  • Change From Baseline in Patient Assessment of Constipation Quality of Life (PAC-QOL)

    Baseline (prior to treatment) to last on-treatment assessment (up to Week 12)

Study Arms (3)

NKTR-118 12.5mg

EXPERIMENTAL
Drug: NKTR-118

NKTR-118 25mg

EXPERIMENTAL
Drug: NKTR-118

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

12.5 mg oral tablet once daily

NKTR-118 12.5mg

Oral tablet intake once daily

Placebo

Eligibility Criteria

Age18 Years - 84 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Must have completed the 12-week study D3820C00004 through Visit 8.
  • Provision of written informed consent prior to any study-specific procedures.
  • Men and women who were between the ages of \>18 and \<85 years at the time of the screening visit for study D3820C00004.
  • Continuing to receive a stable maintenance opioid regimen consisting of a total daily dose of 30 mg to 1000 mg of oral morphine, or equianalgesic amount(s) of 1 or more other opioid therapies.
  • Willingness to continue abstinence from all laxatives and other bowel regimens including prune juice and herbal products throughout this additional 12-week treatment period, and to use only bisacodyl as rescue medication if a bowel movement (BM) has not occurred within at least 72 hours of the last recorded BM.

You may not qualify if:

  • Patients receiving opioid regimen for treatment of pain related to cancer.
  • History of cancer within 5 years from the screening visit of study D3820C00004 with the exception of basal cell cancer and squamous cell skin cancer.
  • Medical conditions and treatments associated with diarrhea, intermittent loose stools, or constipation.
  • Other issues related to the gastrointestinal tract that could impose risk to the patient.
  • Pregnancy or lactation.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (116)

Research Site

Birmingham, Alabama, United States

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Calera, Alabama, United States

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Glendale, Arizona, United States

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Mesa, Arizona, United States

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Phoenix, Arizona, United States

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Tucson, Arizona, United States

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Hot Springs, Arkansas, United States

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Malvern, Arkansas, United States

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Anaheim, California, United States

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Beverly Hills, California, United States

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Burbank, California, United States

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Garden Grove, California, United States

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Laguana Hills, California, United States

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Laguna Hills, California, United States

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Long Beach, California, United States

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Los Gatos, California, United States

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Montebello, California, United States

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National City, California, United States

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Norwalk, California, United States

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Paramount, California, United States

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Sacramento, California, United States

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San Diego, California, United States

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Santa Ana, California, United States

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Denver, Colorado, United States

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Boynton Beach, Florida, United States

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Brooksville, Florida, United States

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Crystal River, Florida, United States

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DeLand, Florida, United States

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Fort Myers, Florida, United States

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Hialeah, Florida, United States

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Jacksonville, Florida, United States

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Jupiter, Florida, United States

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Maitland, Florida, United States

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Miami, Florida, United States

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Naples, Florida, United States

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Orlando, Florida, United States

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Ormond Beach, Florida, United States

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Pembroke Pines, Florida, United States

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Plantation, Florida, United States

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Tamarac, Florida, United States

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Tampa, Florida, United States

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Venice, Florida, United States

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West Palm Beach, Florida, United States

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Winter Park, Florida, United States

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Atlanta, Georgia, United States

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Decatur, Georgia, United States

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Boise, Idaho, United States

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Bloomington, Illinois, United States

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Rockford, Illinois, United States

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Avon, Indiana, United States

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Evansville, Indiana, United States

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Indianapolis, Indiana, United States

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West Des Moines, Iowa, United States

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Pikesville, Maryland, United States

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Brockton, Massachusetts, United States

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Kalamazoo, Michigan, United States

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Biloxi, Mississippi, United States

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Saint Joseph, Missouri, United States

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St Louis, Missouri, United States

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Missoula, Montana, United States

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Omaha, Nebraska, United States

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Las Vegas, Nevada, United States

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Trenton, New Jersey, United States

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Albuquerque, New Mexico, United States

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New York, New York, United States

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Charlotte, North Carolina, United States

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Greensboro, North Carolina, United States

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Hickory, North Carolina, United States

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High Point, North Carolina, United States

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Morrisville, North Carolina, United States

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Beavercreek, Ohio, United States

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Cincinnati, Ohio, United States

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Medord, Oregon, United States

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Feasterville, Pennsylvania, United States

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Huntingdon Valley, Pennsylvania, United States

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Levittown, Pennsylvania, United States

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Philadelphia, Pennsylvania, United States

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Yardley, Pennsylvania, United States

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Cumberland, Rhode Island, United States

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Charleston, South Carolina, United States

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Greer, South Carolina, United States

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Orangeburg, South Carolina, United States

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Clarksville, Tennessee, United States

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Austin, Texas, United States

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Dallas, Texas, United States

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Doral, Texas, United States

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Houston, Texas, United States

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North Richland Hills, Texas, United States

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Salt Lake City, Utah, United States

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Spokane, Washington, United States

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Broadmeadow, New South Wales, Australia

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Darlinghurst, New South Wales, Australia

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Port Kembla, New South Wales, Australia

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Westmead, New South Wales, Australia

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Greenslopes, Queensland, Australia

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Adelaide, South Australia, Australia

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Fremantle, Western Australia, Australia

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Nedlands, Western Australia, Australia

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Potsdam, BR, Germany

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Hamburg, Hamburg, Germany

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Dietzenbach, Hesse, Germany

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Hüttenberg, Hesse, Germany

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Wetzlar, Hesse, Germany

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Celle, Lower Saxony, Germany

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Hanover, Lower Saxony, Germany

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Schwerin, Mecklenburg-Vorpommern, Germany

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Essen, North Rhine-Westphalia, Germany

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Mainz, Rhineland-Palatinate, Germany

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Leipzig, Saxony, Germany

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Kiel, Schleswig-Holstein, Germany

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Berlin, Germany

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Dresden, Germany

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Banská Bystrica, Slovakia

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Bratislava, Slovakia

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Košice, Slovakia

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Prešov, Slovakia

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Related Publications (2)

  • Webster L, Tummala R, Diva U, Lappalainen J. A 12-week extension study to assess the safety and tolerability of naloxegol in patients with noncancer pain and opioid-induced constipation. J Opioid Manag. 2016 Nov/Dec;12(6):405-419. doi: 10.5055/jom.2016.0360.

    PMID: 28059433BACKGROUND
  • Lawson R, King F, Marsh K, Altincatal A, Cimen A. Impact of Treatment with Naloxegol for Opioid-Induced Constipation on Patients' Health State Utility. Adv Ther. 2016 Aug;33(8):1331-46. doi: 10.1007/s12325-016-0365-y. Epub 2016 Jun 24.

Related Links

MeSH Terms

Conditions

Opioid-Induced Constipation

Interventions

naloxegol

Condition Hierarchy (Ancestors)

ConstipationSigns and Symptoms, DigestiveSigns and SymptomsPathological Conditions, Signs and SymptomsNarcotic-Related DisordersSubstance-Related DisordersChemically-Induced DisordersMental Disorders

Results Point of Contact

Title
Mark Sostek
Organization
AstraZeneca

Study Officials

  • Mark Sostek

    AstraZeneca

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

June 28, 2011

First Posted

July 15, 2011

Study Start

July 1, 2011

Primary Completion

September 1, 2012

Study Completion

September 1, 2012

Last Updated

February 23, 2017

Results First Posted

June 17, 2015

Record last verified: 2017-01

Locations