NCT01386255

Brief Summary

Despite the use of proton pump inhibitors and available prokinetics, medical therapy is ineffective in an important number of children with cerbreal palsy (CP) and gastroesophageal reflux disease (GERD), and failure of medical therapy is associated with a substantial morbidity. Many patients, particularly children with CP and GERD, continue to experience complications despite aggressive therapy because antisecretory medications do not address the primary reflux mechanism (TLESR). Furthermore, in patients with CP, surgical options are fraught with serious complications and long-term morbidity. Because the available treatment options for children with CP and intractable GERD are limited, new therapies are urgently needed. Baclofen, which has been shown in animals and humans to decrease TLESRs, may be a good alternative for the treatment of children with CP with intractable GERD.

Trial Health

30
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Timeline
Completed

Started Apr 2009

Typical duration for phase_4

Geographic Reach
1 country

1 active site

Status
withdrawn

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 1, 2009

Completed
2.2 years until next milestone

First Submitted

Initial submission to the registry

June 29, 2011

Completed
2 days until next milestone

First Posted

Study publicly available on registry

July 1, 2011

Completed
9 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 1, 2012

Completed
29 days until next milestone

Study Completion

Last participant's last visit for all outcomes

April 30, 2012

Completed
Last Updated

August 29, 2017

Status Verified

August 1, 2017

Enrollment Period

3 years

First QC Date

June 29, 2011

Last Update Submit

August 26, 2017

Conditions

Keywords

GERD

Outcome Measures

Primary Outcomes (1)

  • Symptom control

    Symptom frequency during the 2 weeks of placebo and baclofen administration.

    3 weeks

Secondary Outcomes (2)

  • GERD control

    3 weeks

  • side effects of baclofen

    3 weeks

Study Arms (2)

baclofen

ACTIVE COMPARATOR

Baclofen suspension

Drug: Baclofen

placebo

PLACEBO COMPARATOR

Identical palcebo suspension

Drug: placebo

Interventions

The final baclofen dose will be 0.7 mg/kg (to a maximum of 40 mg/day) divided in three doses.

Also known as: Lioresal
baclofen

placebo. No other names

placebo

Eligibility Criteria

Age3 Years - 18 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • years old
  • Diagnosis of Cerebral Palsy
  • Symptoms of GERD for at least 3 months
  • At least 8 weeks on BID therapy with a PPI at a therapeutic dose at time of enrollment
  • Normal upper gastrointestinal barium contrast study (UGI)
  • Have a g-tube that is used for more than 75% of calories and a stable feeding schedule for at least 2 weeks
  • If seizures are present, they need to be controlled and on stable medications for 4 weeks

You may not qualify if:

  • Underlying electrolyte disturbance
  • History of Nissen fundoplication
  • Renal insufficiency
  • Currently receiving baclofen
  • Baclofen allergy
  • Uncontrolled seizure disorder
  • Lack of informed consent

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Children's Hospital Boston

Boston, Massachusetts, 02115, United States

Location

MeSH Terms

Conditions

Cerebral PalsyGastroesophageal Reflux

Interventions

Baclofen

Condition Hierarchy (Ancestors)

Brain Damage, ChronicBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesEsophageal Motility DisordersDeglutition DisordersEsophageal DiseasesGastrointestinal DiseasesDigestive System Diseases

Intervention Hierarchy (Ancestors)

gamma-Aminobutyric AcidAminobutyratesButyratesAcids, AcyclicCarboxylic AcidsOrganic Chemicals

Study Officials

  • Samuel Nurko, MD

    Boston Children's Hospital

    PRINCIPAL INVESTIGATOR
0

Study Design

Study Type
interventional
Phase
phase 4
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Attending Physician; Director, Center for Motility and Functional Gastrointestinal Disorders

Study Record Dates

First Submitted

June 29, 2011

First Posted

July 1, 2011

Study Start

April 1, 2009

Primary Completion

April 1, 2012

Study Completion

April 30, 2012

Last Updated

August 29, 2017

Record last verified: 2017-08

Locations