NCT01349270

Brief Summary

Treatment of Chronic Inflammatory Demyelinating Polyneuropathy (CIDP) is a challenge because disease may generate important disability in patients including young adults. Randomized trials showed that corticosteroids, plasma exchanges and intravenous immunoglobulin (IVIg) can reduce impairment on a short term period but the treatment of a chronic disease doesn't agree with it. Corticosteroids and IVIg are the first line CIDP treatments. No study permits to demonstrate the superiority of one treatment to the other. Long term adverse effects of corticosteroids and IVIg cost are the respective limitation of their use. The investigators scheduled to recruit 40 CIDP patients in 23 French centres to receive either 0,8mg/kg/day of prednisone progressively tapered over 6 months or a monthly 2g/kg cure of IVIg during 6 months. Patients will be followed during 6 months after the treatment.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
40

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Jun 2004

Longer than P75 for phase_3

Geographic Reach
1 country

11 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

June 1, 2004

Completed
6.9 years until next milestone

First Submitted

Initial submission to the registry

May 5, 2011

Completed
1 day until next milestone

First Posted

Study publicly available on registry

May 6, 2011

Completed
2.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2013

Completed
Last Updated

September 26, 2014

Status Verified

September 1, 2014

Enrollment Period

9.5 years

First QC Date

May 5, 2011

Last Update Submit

September 25, 2014

Conditions

Keywords

chronic inflammatory demyelinating polyneuropathyimmunoglobulinprednisone

Outcome Measures

Primary Outcomes (1)

  • Main outcome

    Rate of patients with a decreased INCAT score of at least 1 point after 3 months of treatment, * Responders: ≥ 1 point improvement in the INCAT score at 3 months in comparison to baseline, * Non responders: unchanged INCAT score at 3 months in comparison to baseline or patients for whom the primary endpoint can't be assessed because of the occurrence of an adverse event requiring treatment stop.

    3 months

Secondary Outcomes (1)

  • Secondary outcome

    3 months

Study Arms (2)

immunoglobulin

EXPERIMENTAL

patient who received monthly 2g/kg cure of intravenous Immunoglobulin during 6 months

Drug: Immunoglobulin perfusion

prednisone

ACTIVE COMPARATOR

patient who received 0,8mg/kg/day of prednisone progressively tapered over 6 months

Drug: Prednisone

Interventions

patient who received monthly 2g/kg intravenous cure of immunoglobulin

immunoglobulin

patient who received 0,8mg/kg/day of prednisone progressively tapered over 6 months

prednisone

Eligibility Criteria

Age18 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Man or woman between 18 and 80, Weight ≤ 100 kg,
  • CIDP diagnosis:
  • stable or deteriorated state (no spontaneous improvement),
  • with the following features:
  • motor or sensory and motor deficits, and reduced or abolished tendon reflexes,
  • progressive or relapsing evolution,
  • global symmetric disability in more than one limb,
  • disease course installation over at least 2 months,
  • cerebrospinal fluid with ≤10/µL white blood cells and \> 0.5 g/L protein rate (non compulsory examination),
  • electrophysiological or histological signs of demyelinization,
  • INCAT disability score ≥ 2 in arms or ≥ 1 in legs

You may not qualify if:

  • Severe electrophysiological axonal damage,
  • Pure motor syndrome,
  • Spontaneous improvement,
  • Associated systemic disease that could be the cause of neuropathy,
  • Severe cardiac insufficiency,
  • Cardiac arrhythmia,
  • Severe cardiopulmonary pathology,
  • Inflammatory syndrome,
  • Severe physical disease which can interfere with the trial,
  • Patient in a strict salt-free diet,
  • A clinically significant abnormal biological result,
  • Positive serology in one of the following tests: HIV1, HIV2, A-B-C hepatitis, Hbs antigen, Lyme disease,
  • IgA complete deficiency,
  • History of anaphylactic reaction during previous IVIg infusion,
  • Hypogammaglobulinemia (IgG \< 3g/L),
  • +6 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (11)

CHU Clermont-Ferrand

Clermont-Ferrand, France, 63000, France

Location

Chu Dijon

Dijon, 21000, France

Location

CHU Grenoble

Grenoble, 38000, France

Location

Hôpital Neurologique de Lyon

Lyon, 69000, France

Location

Chu Marseille

Marseille, 13000, France

Location

Chu Nancy

Nancy, 54000, France

Location

Chu Nantes

Nantes, 44000, France

Location

CHU Nice

Nice, 06000, France

Location

Chu Saint-Etienne

Saint-Etienne, 42100, France

Location

Chu Strasbourg

Strasbourg, 67000, France

Location

Centre hospitalier de Valence

Valence, 26000, France

Location

Related Publications (1)

  • Bus SR, de Haan RJ, Vermeulen M, van Schaik IN, Eftimov F. Intravenous immunoglobulin for chronic inflammatory demyelinating polyradiculoneuropathy. Cochrane Database Syst Rev. 2024 Feb 14;2(2):CD001797. doi: 10.1002/14651858.CD001797.pub4.

MeSH Terms

Conditions

Polyradiculoneuropathy, Chronic Inflammatory Demyelinating

Interventions

Prednisone

Condition Hierarchy (Ancestors)

PolyradiculoneuropathyAutoimmune Diseases of the Nervous SystemNervous System DiseasesDemyelinating DiseasesPolyneuropathiesPeripheral Nervous System DiseasesNeuromuscular DiseasesAutoimmune DiseasesImmune System DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and Symptoms

Intervention Hierarchy (Ancestors)

PregnadienediolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic Compounds

Study Officials

  • Jean-Philippe CAMDESSANCHE, Dr

    CHU de SAINT-ETIENNE

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 5, 2011

First Posted

May 6, 2011

Study Start

June 1, 2004

Primary Completion

December 1, 2013

Study Completion

December 1, 2013

Last Updated

September 26, 2014

Record last verified: 2014-09

Locations