NCT01291901

Brief Summary

The purpose of this study is to examine the impact of intradermal delivery of NP2 on pain scores and pain medication usage in subjects with intractable pain due to malignant disease. A second purpose is to confirm safety and secondary efficacy measurements.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
33

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Jan 2011

Typical duration for phase_2

Geographic Reach
1 country

18 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2011

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

February 4, 2011

Completed
5 days until next milestone

First Posted

Study publicly available on registry

February 9, 2011

Completed
1.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2012

Completed
1.3 years until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2013

Completed
Last Updated

August 8, 2014

Status Verified

July 1, 2014

Enrollment Period

1.5 years

First QC Date

February 4, 2011

Last Update Submit

July 28, 2014

Conditions

Keywords

paincancermalignancyintractablegene therapyenkephalinopioid

Outcome Measures

Primary Outcomes (1)

  • Pain Measured by the Numerical Rating Scale (NRS)

    • Change from baseline of the average daily NRS pain score (scale of 0 to 10 ) of Placebo compared to Active NP2 cohorts.

    Days -5 to -1 predosing and days 3 to 14 postdosing

Secondary Outcomes (4)

  • Opioid Pain Medication Usage Morphine Equivalent Units (MEU)

    Days -5 to -1 predosing and 3 to 14 postdosing

  • Quality of Life ECOG

    Baseline and Week 1, 2 and 4

  • Quality of Life SF-12

    Baseline and Week 1, 2 and 4

  • Pain SF-MPQ

    Baseline and Week 1, 2 and 4

Study Arms (2)

Active NP2

EXPERIMENTAL

Single intradermal dose of active NP2. An open label study extension will offer up to two additional doses of active NP2 between weeks 4-10 following the previous dose.

Biological: NP2

Placebo

PLACEBO COMPARATOR

Single intradermal dose of placebo (vehicle). An open label study extension will offer up to two additional doses of active NP2 between weeks 4-10 following the previous dose.

Biological: Placebo

Interventions

NP2BIOLOGICAL

NP2 is a replication defective HSV-1 based gene transfer vector engineered to express human preproenkephalin. The drug will be injected intradermally corresponding to the distribution of the malignancy-related pain. The total amount to be injected will be a dose volume of 1.0 ml delivered in a single session on Study Day 0.

Active NP2
PlaceboBIOLOGICAL

The placebo (vehicle) will be injected intradermally corresponding to the distribution of the malignancy-related pain. The total amount to be injected will be a dose volume of 1.0 ml delivered in a single session on Study Day 0.

Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically confirmed malignant disease.
  • Intractable pain related to malignancy.
  • Females must be postmenopausal or practicing birth control.
  • Able to provide appropriate written consent.

You may not qualify if:

  • Positive pregnancy test prior to receiving study treatment.
  • Serious uncontrolled medical condition other than malignancy (e.g. congestive heart failure, coagulopathy, uncontrolled diabetes).
  • Evidence of active Hepatitis B, Hepatitis C, or HIV infection.
  • Evidence of viral, bacterial, or fungal infection in the planned treatment area.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (18)

HOPE Research Institute

Phoenix, Arizona, 85050, United States

Location

Arizona Clinical Research Center

Tucson, Arizona, 85715, United States

Location

Compassionate Cancer Care Medical Group, Inc.

Corona, California, 92879, United States

Location

Cancer Care Associates

Fresno, California, 93720, United States

Location

TriWest Research Associates

La Mesa, California, 91942, United States

Location

White Memorial Medical Center

Los Angeles, California, 90033, United States

Location

Hematology Oncology Associates

Oakland, California, 94609, United States

Location

Advanced Pharma CR

Miami, Florida, 33175, United States

Location

Better Health Clinical Research Inc

Newnan, Georgia, 30265, United States

Location

Christie Clinic

Champaign, Illinois, 61820, United States

Location

Global Scientific Innovations

Evansville, Indiana, 47714, United States

Location

Montana Cancer Institute Foundation

Missoula, Montana, 59802, United States

Location

Center for Clinical Research

Winston-Salem, North Carolina, 27103, United States

Location

Signal Point Clinical research Center

Middletown, Ohio, 45042, United States

Location

Pain Research of Oregon

Eugene, Oregon, 97401, United States

Location

Hematology Oncology Associatesof Rhode Island

Cranston, Rhode Island, 02920, United States

Location

Medical Therapy and Research

San Antonio, Texas, 78217, United States

Location

Medical Oncology Associates

Spokane, Washington, 99208, United States

Location

MeSH Terms

Conditions

Pain, IntractableNeoplasmsPain

Condition Hierarchy (Ancestors)

Neurologic ManifestationsSigns and SymptomsPathological Conditions, Signs and Symptoms

Study Officials

  • Darren Wolfe, Ph.D.

    Diamyd Inc

    STUDY DIRECTOR
  • David Fink, M.D.

    University of Michigan

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 4, 2011

First Posted

February 9, 2011

Study Start

January 1, 2011

Primary Completion

July 1, 2012

Study Completion

November 1, 2013

Last Updated

August 8, 2014

Record last verified: 2014-07

Locations