NCT01283594

Brief Summary

The purpose of this research study is to test the effect of SYN115 compared to placebo (a "sugar pill" that looks like SYN115 but does not include active drug) on movement during the "on" and "off" states as well as other symptoms that some patients with Parkinson's disease experience. This study will also look at whether or not patients with Parkinson's disease experience "side-effects" with SYN115.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
420

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Mar 2011

Geographic Reach
6 countries

61 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 24, 2011

Completed
2 days until next milestone

First Posted

Study publicly available on registry

January 26, 2011

Completed
1 month until next milestone

Study Start

First participant enrolled

March 1, 2011

Completed
1.6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2012

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2012

Completed
Last Updated

January 17, 2019

Status Verified

May 1, 2014

Enrollment Period

1.6 years

First QC Date

January 24, 2011

Last Update Submit

January 14, 2019

Conditions

Outcome Measures

Primary Outcomes (1)

  • Assess efficacy of different doses of SYN115 for reducing the mean total hours of awake time per day spent in the off state

    12 weeks

Secondary Outcomes (6)

  • To assess the effect of SYN115 on dyskinesia

    12 weeks

  • To assess the effect of SYN115 on UPDRS scores

    12 weeks

  • To assess investigator and patient impressions of PD severity and change

    12 weeks

  • To assess the effect of SYN115 on non motor symptoms of PD

    12 weeks

  • To assess the safety and tolerability of SYN115

    12 weeks

  • +1 more secondary outcomes

Study Arms (5)

Tozadenant (SYN115) 60 mg BID

EXPERIMENTAL

Tozadenant tablets, white-coated, modified-oval tablets manufactured in 60 mg dosage strengths.

Drug: Tozadenant (SYN115) 60 mg BIDDrug: Levodopa (L-dopa)

Tozadenant (SYN115) 120 mg BID

EXPERIMENTAL

Tozadenant tablets, white-coated, modified-oval tablets manufactured in 60 mg dosage strengths.

Drug: Levodopa (L-dopa)Drug: Tozadenant (SYN115) 120 mg BID

Tozadenant (SYN115) 180 mg BID

EXPERIMENTAL

Tozadenant tablets, white-coated, modified-oval tablets manufactured in 60 mg dosage strengths.

Drug: Levodopa (L-dopa)Drug: Tozadenant (SYN115) 180 mg BID

Tozadenant (SYN115) 240 mg BID

EXPERIMENTAL

Tozadenant tablets, white-coated, modified-oval tablets manufactured in 60 mg dosage strengths.

Drug: Levodopa (L-dopa)Drug: Tozadenant (SYN115) 240 mg BID

Sugar Pill

PLACEBO COMPARATOR

White-coated, modified-oval placebo tablets.

Drug: PlaceboDrug: Levodopa (L-dopa)

Interventions

Tozadenant tablets, white-coated, modified-oval tablets manufactured in 60 mg dosage strengths. Total daily doses include 60 mg BID.

Tozadenant (SYN115) 60 mg BID

White-coated, modified-oval placebo tablets.

Sugar Pill

One intravenous infusion of L-dopa to reach approximately 600 ng/ ml plasma concentration.

Also known as: L-dopa
Sugar PillTozadenant (SYN115) 120 mg BIDTozadenant (SYN115) 180 mg BIDTozadenant (SYN115) 240 mg BIDTozadenant (SYN115) 60 mg BID

Tozadenant tablets, white-coated, modified-oval tablets manufactured in 60 mg dosage strengths. Total daily doses include 120 mg BID.

Tozadenant (SYN115) 120 mg BID

Tozadenant tablets, white-coated, modified-oval tablets manufactured in 60 mg dosage strengths. Total daily doses include 180 mg BID.

Tozadenant (SYN115) 180 mg BID

Tozadenant tablets, white-coated, modified-oval tablets manufactured in 60 mg dosage strengths. Total daily doses include 240 mg BID.

Tozadenant (SYN115) 240 mg BID

Eligibility Criteria

Age30 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Meet Parkinson's Disease (PD) diagnosis consistent with UK PD diagnostic criteria
  • Meet Hoehn and Yahr PD stage
  • Good response to levodopa
  • Stable regimen of anti-parkinson medications
  • Are able to complete a Parkinson's disease diary
  • If of childbearing potential(male and female), use an acceptable method of birth control
  • Able and willing to sign an IRB/IEC approved informed consent
  • Able and willing to understand study requirements, follow study instructions, attend all visits and undergo all planned tests.

You may not qualify if:

  • Secondary or atypical Parkinson's
  • Neurosurgical intervention for Parkinson's disease
  • Treatment with apomorphine
  • Treatment with anti-psychotic drugs
  • Other abnormal findings on physical or neuro exam or history that in the opinion of the investigator would make subject unsuitable for the study or prejudice safety and efficacy evaluation
  • MMSE less than 26
  • Subjects with untreated or uncontrolled current episode of major depression
  • Receipt of any anti-psychotic drugs greater than 1 month in the past 5 years or any exposure in past year (except for quetiapine at doses \<100mg per day)
  • Women pregnant or lactating
  • History of hepatitis, cholangitis
  • Untreated or uncontrolled hypothyroidism or hyperthyroidism
  • Drops in blood pressure requiring medication to maintain blood pressure
  • Any clinically significant out of range laboratory evaluations
  • Known sensitivity to the study medication or its components
  • Suicide ideation or type 4 or type 5 on the Columbia suicide severity rating scale
  • +2 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (61)

Unknown Facility

Birmingham, Alabama, 35005, United States

Location

Unknown Facility

La Jolla, California, 92037, United States

Location

Unknown Facility

Loma Linda, California, 92318, United States

Location

Unknown Facility

Los Angeles, California, 90001, United States

Location

Unknown Facility

Oxnard, California, 93030, United States

Location

Unknown Facility

San Francisco, California, 94016, United States

Location

Unknown Facility

Denver, Colorado, 80014, United States

Location

Unknown Facility

Manchester, Connecticut, 06040, United States

Location

Unknown Facility

New Haven, Connecticut, 06501, United States

Location

Unknown Facility

Boca Raton, Florida, 33427, United States

Location

Unknown Facility

Gainesville, Florida, 32601, United States

Location

Unknown Facility

Miami, Florida, 33101, United States

Location

Unknown Facility

Tampa, Florida, 33601, United States

Location

Unknown Facility

Weston, Florida, 33326, United States

Location

Unknown Facility

Atlanta, Georgia, 30301, United States

Location

Unknown Facility

Augusta, Georgia, 30901, United States

Location

Unknown Facility

Boise, Idaho, 83701, United States

Location

Unknown Facility

Springfield, Illinois, 62629, United States

Location

Unknown Facility

Indianapolis, Indiana, 46077, United States

Location

Unknown Facility

Des Moines, Iowa, 50047, United States

Location

Unknown Facility

Kansas City, Kansas, 66012, United States

Location

Unknown Facility

Lexington, Kentucky, 40502, United States

Location

Unknown Facility

Baltimore, Maryland, 21201, United States

Location

Unknown Facility

West Bloomfield, Michigan, 48302, United States

Location

Unknown Facility

Minneapolis, Minnesota, 55111, United States

Location

Unknown Facility

Commack, New York, 11725, United States

Location

Unknown Facility

New York, New York, 10001, United States

Location

Unknown Facility

Durham, North Carolina, 27517, United States

Location

Unknown Facility

Cincinnati, Ohio, 41073, United States

Location

Unknown Facility

Cleveland, Ohio, 44101, United States

Location

Unknown Facility

Columbus, Ohio, 43004, United States

Location

Unknown Facility

Toledo, Ohio, 43460, United States

Location

Unknown Facility

Tulsa, Oklahoma, 74008, United States

Location

Unknown Facility

Allentown, Pennsylvania, 18001, United States

Location

Unknown Facility

Philadelphia, Pennsylvania, 19019, United States

Location

Unknown Facility

Charleston, South Carolina, 29401, United States

Location

Unknown Facility

Dallas, Texas, 75001, United States

Location

Unknown Facility

Houston, Texas, 77001, United States

Location

Unknown Facility

Roanoke, Virginia, 24001, United States

Location

Unknown Facility

Milwaukee, Wisconsin, 53201, United States

Location

Unknown Facility

Buenos Aires, Argentina

Location

Unknown Facility

Santa Fe, Argentina

Location

Unknown Facility

Edmonton, Alberta, Canada

Location

Unknown Facility

Halifax, Nova Scotia, Canada

Location

Unknown Facility

Ottawa, Ontario, Canada

Location

Unknown Facility

Montreal, Quebec, Canada

Location

Unknown Facility

Québec, Quebec, Canada

Location

Unknown Facility

Santiago, Chile

Location

Unknown Facility

Valdivia, Chile

Location

Unknown Facility

Brasov, Romania

Location

Unknown Facility

Bucharest, Romania

Location

Unknown Facility

Constanța, Romania

Location

Unknown Facility

Târgu Mureş, Romania

Location

Unknown Facility

Timișoara, Romania

Location

Unknown Facility

Dnipropetrovsk, Ukraine

Location

Unknown Facility

Donetsk, Ukraine

Location

Unknown Facility

Kiev, Ukraine

Location

Unknown Facility

Lviv, Ukraine

Location

Unknown Facility

Poltava, Ukraine

Location

Unknown Facility

Vinnytsia, Ukraine

Location

Unknown Facility

Zaporizhzhya, Ukraine

Location

Related Publications (1)

  • Hauser RA, Olanow CW, Kieburtz KD, Pourcher E, Docu-Axelerad A, Lew M, Kozyolkin O, Neale A, Resburg C, Meya U, Kenney C, Bandak S. Tozadenant (SYN115) in patients with Parkinson's disease who have motor fluctuations on levodopa: a phase 2b, double-blind, randomised trial. Lancet Neurol. 2014 Aug;13(8):767-76. doi: 10.1016/S1474-4422(14)70148-6. Epub 2014 Jul 6.

MeSH Terms

Conditions

Parkinson Disease

Interventions

tozadenantBID protein, humanLevodopa

Condition Hierarchy (Ancestors)

Parkinsonian DisordersBasal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesMovement DisordersSynucleinopathiesNeurodegenerative Diseases

Intervention Hierarchy (Ancestors)

DihydroxyphenylalanineCatecholaminesAminesOrganic ChemicalsCatecholsPhenolsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsPhenylalanineAmino Acids, AromaticAmino Acids, CyclicAmino AcidsAmino Acids, Peptides, and ProteinsTyrosine

Study Officials

  • Steve Bandak, MD

    Biotie Therapies Inc.

    STUDY CHAIR
  • Ann Neale, RN

    Biotie Therapies Inc.

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 24, 2011

First Posted

January 26, 2011

Study Start

March 1, 2011

Primary Completion

October 1, 2012

Study Completion

October 1, 2012

Last Updated

January 17, 2019

Record last verified: 2014-05

Locations