NCT01278407

Brief Summary

The purpose of this study is to confirm the efficacy of E2020 in patients with dementia with Lewy bodies (DLB).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
142

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Feb 2011

Geographic Reach
1 country

56 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 14, 2011

Completed
3 days until next milestone

First Posted

Study publicly available on registry

January 17, 2011

Completed
15 days until next milestone

Study Start

First participant enrolled

February 1, 2011

Completed
2.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2013

Completed
1 month until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2013

Completed
2.7 years until next milestone

Results Posted

Study results publicly available

November 30, 2015

Completed
Last Updated

June 29, 2023

Status Verified

December 1, 2015

Enrollment Period

2.1 years

First QC Date

January 14, 2011

Results QC Date

October 27, 2015

Last Update Submit

June 16, 2023

Conditions

Keywords

DLBDementia with Lewy bodiesLewy Body DiseaseDementiaE2020DonepezilAricept

Outcome Measures

Primary Outcomes (2)

  • Change From Baseline in Mini-Mental State Examination (MMSE) Score

    The MMSE was used to measure cognitive impairment. The MMSE can evaluate overall cognitive function, and is widely used for the assessment of cognitive impairment in dementia patients. The questionnaire consists of 11 items, and each item aims to evaluate different cognitive domains such as orientation, memory, attention, and construction. The score ranged from 0 to 30, with a higher score indicating better function. A positive change score indicated improvement from baseline. Data are presented as change from baseline in mean MMSE +/- standard deviation.

    Week 12 for Confirmatory Phase

  • Change From Baseline in Neuropsychiatric Inventory (NPI-2) Score

    The NPI was a questionnaire that quantified psychiatric symptoms and behavioral disorders in dementia. A total of 12 items (the original NPI-10 consisting of 10 behavioral domains: delusions, hallucinations, agitation/aggression, dysphoria, anxiety, euphoria, apathy, disinhibition, irritability/lability, and aberrant motor behavior, supplemented by 2 dementia with Lewy bodies (DLB)-relevant domains of sleep, and cognitive fluctuation \[reported as cognitive fluctuation inventory\]) were assessed. The score of each item was calculated as frequency (scale: 1=occasionally to 4=very frequently) x Severity (scale: 1=Mild to 3=Severe). The NPI-2 was calculated as the sum of the scores for hallucinations and cognitive fluctuation, to yield a possible total score of 0 to 24. Lower score=less severity. A negative change score from baseline indicated improvement. Data are presented as change from baseline in mean NPI-2 +/- standard deviation.

    Week 12 for Confirmatory Phase

Study Arms (5)

Placebo - Confirmatory Phase

PLACEBO COMPARATOR

Participants received donepezil matched placebo tablets orally, once daily for 12 weeks in the confirmatory phase.

Drug: Donepezil matched placebo

Donepezil 5 mg - Confirmatory Phase

EXPERIMENTAL

Participants received donepezil tablets orally, once daily for 12 weeks. Treatment began with 3 mg for 2 weeks, and then the dose was increased to 5 mg for 10 weeks in the confirmatory phase.

Drug: Donepezil 5 mg

Donepezil 10 mg - Confirmatory Phase

EXPERIMENTAL

Participants received donepezil tablets orally, once daily for 12 weeks. Treatment began with 3 mg for 2 weeks, and then the dose was increased to 5 mg for 4 weeks. Thereafter, the dose was increased to 10 mg for 6 weeks in the confirmatory phase.

Drug: Donepezil 10 mg

Placebo to Donepezil (5 +10 mg) - Extension Phase

EXPERIMENTAL

Participants previously receiving donepezil matched placebo up to Week 12 in the Confirmatory Phase, continued placebo until Week 16 (at the beginning of the Extension Phase). Participants received 3 mg of donepezil, and the dose was then increased to 5 mg at Week 18 and to 10 mg at Week 24. After Week 24, dose reduction to 5 mg was allowed if continuation at 10 mg caused any safety concerns.

Drug: Donepezil 10 mg

Donepezil (5 +10 mg) - Extension Phase

EXPERIMENTAL

Participants previously receiving donepezil (5 mg or 10 mg) up to Week 12 in the Confirmatory Phase, maintained allocated treatment and dosages until Week 24. In the 5 mg group of the Confirmatory Phase, the dose was increased to 10 mg at Week 24. After Week 24, dose reduction to 5 mg was allowed if continuation at 10 mg caused any safety concerns.

Drug: Donepezil 10 mg

Interventions

Donepezil tablets orally, once daily, uptitrated from 3 to 5 mg

Also known as: E2020
Donepezil 5 mg - Confirmatory Phase

Donepezil tablets orally, once daily, uptitrated from 3 to 5 mg and then the dose was increased to 10 mg

Also known as: E2020
Donepezil (5 +10 mg) - Extension PhaseDonepezil 10 mg - Confirmatory PhasePlacebo to Donepezil (5 +10 mg) - Extension Phase
Placebo - Confirmatory Phase

Eligibility Criteria

Age50 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Patients diagnosed as probable dementia with Lewy bodies (DLB) according to the consensus diagnostic criteria for DLB
  • Patients having caregivers throughout the study who submited written consent to cooperate with this study, who routinely stayed with patients 3 days or more a week (at least 4 hours a day), provided patients' information necessary for this study, assisted treatment compliance, and escorted the patients on required visits to study institution
  • Clinical Dementia Rating (CDR) score ≥ 0.5
  • Mini-Mental State Examination (MMSE) score of 10 to 26

You may not qualify if:

  • Patients diagnosed with Parkinson's disease with dementia (PDD)
  • Patients who received anti-dementia drug therapy at the same institution
  • Patients who received anti-dementia drug therapy within 12 weeks before start of Screening
  • Patients with a complication of serious neuropsychiatric disease(s) such as stroke, brain tumor, schizophrenia, epilepsy, normal pressure hydrocephalus, mental retardation, brain trauma with unconsciousness, or a history of brain surgery causing unrecovered deficiency
  • Patients with severe extrapyramidal disorders (Hoehn and Hahr staging score ≥ IV)
  • Patients whose systolic blood pressure was less than 90 mmHg or pulse rate was less than 50 bpm at screening

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (56)

Unknown Facility

Anjo-shi, Aichi-ken, Japan

Location

Unknown Facility

Nagoya, Aichi-ken, Japan

Location

Unknown Facility

Toyokawa-shi, Aichi-ken, Japan

Location

Unknown Facility

Chiba, Chiba, Japan

Location

Unknown Facility

Fukui-shi, Fukui, Japan

Location

Unknown Facility

Yoshida-gun, Fukui, Japan

Location

Unknown Facility

Fukuoka, Fukuoka, Japan

Location

Unknown Facility

Kitakyushu-shi, Fukuoka, Japan

Location

Unknown Facility

Omuta-shi, Fukuoka, Japan

Location

Unknown Facility

Gifu, Gifu, Japan

Location

Unknown Facility

Mizunami-shi, Gifu, Japan

Location

Unknown Facility

Fujioka-shi, Gunma, Japan

Location

Unknown Facility

Maebashi, Gunma, Japan

Location

Unknown Facility

Kure-shi, Hiroshima, Japan

Location

Unknown Facility

Miyoshi-shi, Hiroshima, Japan

Location

Unknown Facility

Otake-shi, Hiroshima, Japan

Location

Unknown Facility

Obihiro-shi, Hokkaido, Japan

Location

Unknown Facility

Sapporo, Hokkaido, Japan

Location

Unknown Facility

Himeji-shi, Hyōgo, Japan

Location

Unknown Facility

Kobe, Hyōgo, Japan

Location

Unknown Facility

Yabu-shi, Hyōgo, Japan

Location

Unknown Facility

Bando-shi, Ibaraki, Japan

Location

Unknown Facility

Hitachi-shi, Ibaraki, Japan

Location

Unknown Facility

Kahoku, Ishikawa-ken, Japan

Location

Unknown Facility

Morioka, Iwate, Japan

Location

Unknown Facility

Fujisawa-shi, Kanagawa, Japan

Location

Unknown Facility

Kochi, Kochi, Japan

Location

Unknown Facility

Koshi-shi, Kumamoto, Japan

Location

Unknown Facility

Kumamoto, Kumamoto, Japan

Location

Unknown Facility

Kyoto, Kyoto, Japan

Location

Unknown Facility

Uji-shi, Kyoto, Japan

Location

Unknown Facility

Sendai, Miyagi, Japan

Location

Unknown Facility

Higashimorokata-gun, Miyazaki, Japan

Location

Unknown Facility

Ina-shi, Nagano, Japan

Location

Unknown Facility

Kitaazumi-gun, Nagano, Japan

Location

Unknown Facility

Matsumoto-shi, Nagano, Japan

Location

Unknown Facility

Nishisonogi-gun, Nagasaki, Japan

Location

Unknown Facility

Nagaoka-shi, Niigata, Japan

Location

Unknown Facility

Sanjo-shi, Niigata, Japan

Location

Unknown Facility

Tsubame-shi, Niigata, Japan

Location

Unknown Facility

Yufu-shi, Oita Prefecture, Japan

Location

Unknown Facility

Osaka, Osaka, Japan

Location

Unknown Facility

Sakai-shi, Osaka, Japan

Location

Unknown Facility

Sennan-shi, Osaka, Japan

Location

Unknown Facility

Suita-shi, Osaka, Japan

Location

Unknown Facility

Ageo-shi, Saitama, Japan

Location

Unknown Facility

Kasukabe-shi, Saitama, Japan

Location

Unknown Facility

Saitama-shi, Saitama, Japan

Location

Unknown Facility

Fuji-shi, Shizuoka, Japan

Location

Unknown Facility

Hamamatsu, Shizuoka, Japan

Location

Unknown Facility

Shizuoka, Shizuoka, Japan

Location

Unknown Facility

Koto-ku, Tokyo, Japan

Location

Unknown Facility

Ōta-ku, Tokyo, Japan

Location

Unknown Facility

Setagaya-ku, Tokyo, Japan

Location

Unknown Facility

Shinjuku-ku, Tokyo, Japan

Location

Unknown Facility

Suginami-ku, Tokyo, Japan

Location

Related Publications (2)

  • Mori E, Ikeda M, Nagai R, Matsuo K, Nakagawa M, Kosaka K. Long-term donepezil use for dementia with Lewy bodies: results from an open-label extension of Phase III trial. Alzheimers Res Ther. 2015 Feb 3;7(1):5. doi: 10.1186/s13195-014-0081-2. eCollection 2015.

  • Ikeda M, Mori E, Matsuo K, Nakagawa M, Kosaka K. Donepezil for dementia with Lewy bodies: a randomized, placebo-controlled, confirmatory phase III trial. Alzheimers Res Ther. 2015 Feb 3;7(1):4. doi: 10.1186/s13195-014-0083-0. eCollection 2015.

MeSH Terms

Conditions

Lewy Body DiseaseDementia

Interventions

Donepezil

Condition Hierarchy (Ancestors)

Parkinsonian DisordersBasal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesMovement DisordersSynucleinopathiesNeurodegenerative DiseasesNeurocognitive DisordersMental Disorders

Intervention Hierarchy (Ancestors)

IndansIndenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsPiperidinesHeterocyclic Compounds, 1-RingHeterocyclic CompoundsPolycyclic Compounds

Results Point of Contact

Title
Masaki Nakagawa
Organization
Eisai Co., Ltd.

Study Officials

  • Masaki Nakagawa

    Neuroscience Clinical Development Section. JAC PCU

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 14, 2011

First Posted

January 17, 2011

Study Start

February 1, 2011

Primary Completion

March 1, 2013

Study Completion

April 1, 2013

Last Updated

June 29, 2023

Results First Posted

November 30, 2015

Record last verified: 2015-12

Locations