NCT01244347

Brief Summary

In 1991 the Medical Research Council Vitamin Study Group and in 1992 the Hungarian randomised clinical trial have shown conclusively that the risk of neural tube defects can be reduced substantially by taking folic acid during the peri-conceptional period. At present there is enough evidence to support the hypothesis that folic acid supplementation can reduce the risk of all congenital malformations or of a specific and selected group of them, namely: neural tube defects, oral clefts, cardiac defects, urinary tract anomalies except hypospadias, limb reduction defects, omphalocele, anal atresia and trisomy 21. The hypothesis that a higher intake of folic acid is related to an higher risk reduction of neural tube defects and of other congenital malformations is the main rationale for the present study. The present study is a randomized, double-blind, controlled trial evaluating whether supplementation with folic acid at high dose (4 mg/day) reduces the overall risk of major congenital malformations in the population more than the standard recommended dose (0.4 mg/day). At the enrolment visit all the eligible women will be interviewed to assess sociodemographic, life style and health status. After randomization, women will be interviewed every 4 months to evaluate pregnancy status. Women who have a pregnancy diagnosis during the study period will be interviewed by telephone at the expected 16, 24 and 40 weeks of gestation to evaluate the pregnancy outcome. The health status of live births will be evaluated at the child's age of 1 month, 3 months and 1 year. The primary aim of this project is conducting a study to assess the effect of folic acid periconceptional supplementation of 4 mg/day compared to the 0.4 mg/day standard dose on reducing the occurrence of all congenital malformations. Secondary aims of this study include comparing severity of CMs in offspring of trial mothers, rates of "selected congenital malformations", rates of twinning, miscarriages, recurrent abortions, small-for-gestational age, preeclampsia and abruptio placentae. The sample size is not easy to be computed because lacking robust estimate of the size effect of the treatment. Three hypotheses of a size effect of 45%, 26% and 13% were considered. A sample size of outcomes (and women) respectively of 2,006 (5,015), 8,510 (21,275) and 30,126 (75,315) is needed. Since the sample size needed to evaluate different scenarios is large, the present study is also the pilot study to promote an international prospective meta-analysis.

Trial Health

43
At Risk

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Trial has exceeded expected completion date
Enrollment
5,000

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jul 2009

Longer than P75 for phase_3

Geographic Reach
1 country

34 active sites

Status
unknown

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

July 1, 2009

Completed
1.3 years until next milestone

First Submitted

Initial submission to the registry

October 11, 2010

Completed
1 month until next milestone

First Posted

Study publicly available on registry

November 19, 2010

Completed
4.8 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2015

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

September 1, 2016

Completed
Last Updated

January 14, 2015

Status Verified

January 1, 2015

Enrollment Period

6.2 years

First QC Date

October 11, 2010

Last Update Submit

January 13, 2015

Conditions

Keywords

folic acidmalformationsprevention

Outcome Measures

Primary Outcomes (1)

  • number of congenital malformations

    The time frame was computed as an average of 32 weeks before conception, plus an average of 28 weeks to all possible outcomes, plus 52 weeks of baby observation.

    112 weeks

Secondary Outcomes (7)

  • rate of selected congenital malformations

    112 weeks

  • Miscarriages and recurrent abortions

    47 weeks

  • pre-eclampsia

    60 weeks

  • abruptio placentae

    34 weeks

  • intrauterine growth restriction

    31 weeks

  • +2 more secondary outcomes

Study Arms (2)

folic acid 4 mg

EXPERIMENTAL
Drug: folic acid

folic acid 0.4 mg

ACTIVE COMPARATOR
Drug: folic acid

Interventions

folic acid 4 mg

Eligibility Criteria

Age18 Years - 44 Years
Sexfemale
Healthy VolunteersNo
Age GroupsAdult (18-64)

You may qualify if:

  • age between 18 and 44 years
  • women who intend to become pregnant (not excluded women

You may not qualify if:

  • pregnant women
  • women planning to move to an area where the study is not ongoing
  • women who do not understand and speak Italian
  • women who do not have a phone
  • women affected by epilepsy, even not assuming anticonvulsivant drugs
  • women affected by diabetes
  • women who previously had a tumour or a disease relevant for the study (Crohn disease, rheumatoid arthritis, ulcerative colitis)
  • women who recently assumed antifolates, like methotrexate
  • women who currently abuse or previously abused alcohol
  • obese women
  • vegetarian women
  • women who had a previous pregnancy with neural tube defect (NTD) or any other congenital structural defect
  • women or partners with NTD, or one of their relatives with an NTD
  • women with positive family history for breast or colorectal cancer
  • women with positive family or personal history of hereditary syndrome like adenomatous polyposis, or hereditary nonpolyposis colorectal cancer
  • +4 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (34)

Ospedale di Adria

Adria, Rovigo, 45011, Italy

Location

Ospedale San Luca

Trecenta, Rovigo, 45027, Italy

Location

Ospedale di Conegliano

Conegliano, Treviso, 31015, Italy

Location

Family Health Centre

Montebelluna, Treviso, 31044, Italy

Location

Family Health Practice

Oderzo, Treviso, 31046, Italy

Location

Family Health Practice

Villorba, Treviso, 31020, Italy

Location

Ospedale Sant'Antonio Abate

Gallarate, Varese, 21013, Italy

Location

Family Health Practice

Camponogara, Venezia, 30010, Italy

Location

Family Health Centre

Martellago, Venezia, 30030, Italy

Location

Family Health Practice

Mira, Venezia, 30034, Italy

Location

Family Health Centre

Noale, Venezia, 30033, Italy

Location

Family Health Centre

San Pietro di Stra, Venezia, 30031, Italy

Location

Family Health Centre

Vogonovo, Venezia, 30030, Italy

Location

Ospedale di Bussolengo

Bussolengo, Verona, 37012, Italy

Location

Ospedale di Legnago

Legnago, Verona, 37045, Italy

Location

Ospedale di San Bonifacio

San Bonifacio, Verona, 37047, Italy

Location

Family Health Centre

Bassano, Vicenza, 36061, Italy

Location

Ospedale San Bassiano

Bassano, Vicenza, 36061, Italy

Location

General Practice

Dueville, Vicenza, 36031, Italy

Location

General Practice

Malo, Vicenza, 36034, Italy

Location

General Practice

Schio, Vicenza, 36014, Italy

Location

General Practice

Sovizzo, Vicenza, 36050, Italy

Location

Ospedale Boldrini

Thiene, Vicenza, 36016, Italy

Location

Ospedale di Valdagno

Valdagno, Vicenza, 36078, Italy

Location

Ospedale di Vicenza

Vicenza, VI, 36100, Italy

Location

Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico

Milan, 20100, Italy

Location

Azienda Ospedaliera di Padova

Padua, 35100, Italy

Location

Family Health Centre

Padua, 35132, Italy

Location

Family Health Centre

Verona, 37122, Italy

Location

General Practice

Verona, 37126, Italy

Location

Ospedale Civile Maggiore

Verona, 37126, Italy

Location

General Practice

Verona, 37129, Italy

Location

Family Health Centre

Verona, 37131, Italy

Location

Policlinico G.B. Rossi

Verona, 37134, Italy

Location

Related Publications (8)

  • Badovinac RL, Werler MM, Williams PL, Kelsey KT, Hayes C. Folic acid-containing supplement consumption during pregnancy and risk for oral clefts: a meta-analysis. Birth Defects Res A Clin Mol Teratol. 2007 Jan;79(1):8-15. doi: 10.1002/bdra.20315.

    PMID: 17133404BACKGROUND
  • Berry RJ, Li Z, Erickson JD, Li S, Moore CA, Wang H, Mulinare J, Zhao P, Wong LY, Gindler J, Hong SX, Correa A. Prevention of neural-tube defects with folic acid in China. China-U.S. Collaborative Project for Neural Tube Defect Prevention. N Engl J Med. 1999 Nov 11;341(20):1485-90. doi: 10.1056/NEJM199911113412001.

    PMID: 10559448BACKGROUND
  • Botto LD, Olney RS, Erickson JD. Vitamin supplements and the risk for congenital anomalies other than neural tube defects. Am J Med Genet C Semin Med Genet. 2004 Feb 15;125C(1):12-21. doi: 10.1002/ajmg.c.30004.

    PMID: 14755429BACKGROUND
  • Catov JM, Bodnar LM, Ness RB, Markovic N, Roberts JM. Association of periconceptional multivitamin use and risk of preterm or small-for-gestational-age births. Am J Epidemiol. 2007 Aug 1;166(3):296-303. doi: 10.1093/aje/kwm071. Epub 2007 May 11.

    PMID: 17496313BACKGROUND
  • Czeizel AE, Dudas I. Prevention of the first occurrence of neural-tube defects by periconceptional vitamin supplementation. N Engl J Med. 1992 Dec 24;327(26):1832-5. doi: 10.1056/NEJM199212243272602.

    PMID: 1307234BACKGROUND
  • Ingrid Goh Y, Bollano E, Einarson TR, Koren G. Prenatal multivitamin supplementation and rates of congenital anomalies: a meta-analysis. J Obstet Gynaecol Can. 2006 Aug;28(8):680-689. doi: 10.1016/S1701-2163(16)32227-7.

    PMID: 17022907BACKGROUND
  • Prevention of neural tube defects: results of the Medical Research Council Vitamin Study. MRC Vitamin Study Research Group. Lancet. 1991 Jul 20;338(8760):131-7.

    PMID: 1677062BACKGROUND
  • Bortolus R, Blom F, Filippini F, van Poppel MN, Leoncini E, de Smit DJ, Benetollo PP, Cornel MC, de Walle HE, Mastroiacovo P; Italian and Dutch folic acid trial study groups. Prevention of congenital malformations and other adverse pregnancy outcomes with 4.0 mg of folic acid: community-based randomized clinical trial in Italy and the Netherlands. BMC Pregnancy Childbirth. 2014 May 13;14:166. doi: 10.1186/1471-2393-14-166.

Related Links

MeSH Terms

Conditions

Congenital Abnormalities

Interventions

Folic Acid

Condition Hierarchy (Ancestors)

Congenital, Hereditary, and Neonatal Diseases and Abnormalities

Intervention Hierarchy (Ancestors)

PterinsPteridinesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds

Study Officials

  • Renata Bortolus, MD

    Azienda Ospedaliera Universitaria Integrata Verona

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
PREVENTION
Intervention Model
PARALLEL
Sponsor Type
OTHER

Study Record Dates

First Submitted

October 11, 2010

First Posted

November 19, 2010

Study Start

July 1, 2009

Primary Completion

September 1, 2015

Study Completion

September 1, 2016

Last Updated

January 14, 2015

Record last verified: 2015-01

Locations