NCT01202721

Brief Summary

The purpose of this study is to determine whether long-term treatment with a beta-blocker (BB) such as atenolol and/or an angiotensin receptor blocker (ARB) such as telmisartan, given to adult patients with bicuspid aortic valve (BAV) disease (aortopathy) reduces the widening (dilatation) of the aorta from its baseline size.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
85

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Jun 2011

Longer than P75 for phase_3

Geographic Reach
1 country

13 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

September 14, 2010

Completed
2 days until next milestone

First Posted

Study publicly available on registry

September 16, 2010

Completed
9 months until next milestone

Study Start

First participant enrolled

June 1, 2011

Completed
4.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

April 19, 2016

Completed
7 months until next milestone

Study Completion

Last participant's last visit for all outcomes

November 1, 2016

Completed
2.9 years until next milestone

Results Posted

Study results publicly available

September 18, 2019

Completed
Last Updated

September 18, 2019

Status Verified

August 1, 2019

Enrollment Period

4.9 years

First QC Date

September 14, 2010

Results QC Date

February 20, 2019

Last Update Submit

August 12, 2019

Conditions

Keywords

CongenitalAortic ValveBicuspidAortopathybicuspid aortic valve aortopathy

Outcome Measures

Primary Outcomes (1)

  • Change From Baseline in Ascending Aorta Size, as Evaluated by MRI

    The primary analyses include the evaluation of the effects of monotherapy (atenolol vs. placebo, telmisartan vs. placebo) on the change in aortic root size measured at 3 years. Change is measured in centimeters squared (final measurement - baseline measurement). Original outcome measure time frame was scheduled for 5 years, however due to poor study participant and site recruitment study was closed early and final outcome measures taken at approximately 3 years.

    The difference between baseline measures (2012-2013) and Year 3 measure (2015-2016)

Secondary Outcomes (1)

  • Rate of Change in Ascending Aorta Size Evaluated by Transthoracic Echocardiography (TEE)

    The difference between baseline measures (2012-2013) and Year 3 measure (2015-2016)

Study Arms (2)

Atenolol

EXPERIMENTAL

Atenolol or matching placebo 25 mg up-titrated to 100 mg.

Drug: Atenolol

Telmisartan

EXPERIMENTAL

Telmisartan or matching placebo 40 mg up-titrated to 80mg

Drug: Telmisartan

Interventions

Atenolol or matching placebo 25 mg up-titrated to 100 mg

Also known as: Atenolol 25/50/100 mg, or matched placebo
Atenolol

Telmisartan or matching placebo 40 mg up-titrated to 80mg.

Also known as: Micardis 40/80 mg, or matched placebo
Telmisartan

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age =\> 18 years
  • Men and women with BAV and ascending aorta measuring \> 37mm.
  • Written informed consent

You may not qualify if:

  • History of cardiac diseases, such as
  • Symptomatic aortic stenosis or aortic regurgitation referred for surgical intervention or asymptomatic severe aortic stenosis or regurgitation based on current guidelines
  • Uncontrolled heart failure, right ventricular failure due to pulmonary hypertension
  • Cardiogenic shock
  • Systolic blood pressure \< 100 mmHg
  • Ascending aorta measuring ≥ 50mm, requiring prophylactic ascending aorta surgery
  • Unable to provide informed consent
  • Prior surgery on ascending aorta or aortic root (balloon valvuloplasty, aortic valvotomy or post coarctation surgery are acceptable)
  • Women who are pregnant at screening visit
  • Contraindication to MRI (claustrophobia, pacemaker, metallic clip in eye or brain)
  • History of any illness which limits the participants' ability to complete the study
  • Heart rate \<60 bpm
  • Heart block (1st, 2nd and 3rd degree AV block on ECG), or sick sinus syndrome
  • Asthma of sufficient severity to represent a contraindication to BB use in the judgment of the patient's physician
  • History of severe peripheral artery disorders
  • +8 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (13)

Mazankowski Alberta Heart Institute

Edmonton, Alberta, T6G 2B7, Canada

Location

University of British Columbia

Vancouver, British Columbia, V6Z 1Y6, Canada

Location

St. Boniface Hospital

Winnipeg, Manitoba, Canada

Location

Hamilton Health Sciences-General

Hamilton, Ontario, L8L 2X2, Canada

Location

Population Health Research Institute - Coordinating Centre

Hamilton, Ontario, L8L2X2, Canada

Location

London Health Sciences Centre

London, Ontario, N6A 5A5, Canada

Location

St. Michael's Hospital

Toronto, Ontario, M5B 1W8, Canada

Location

Toronto General Hospital/University of Toronto

Toronto, Ontario, Canada

Location

Cité de la Santé de Laval

Laval, Quebec, H7M 3L9, Canada

Location

McGill University Health Centre

Montreal, Quebec, H3A 1A1, Canada

Location

Jewish General Hospital

Montreal, Quebec, H3T 1E2, Canada

Location

Centre Hospitalier Universitaire de Sherbrooke

Sherbrooke, Quebec, J1H 5N4, Canada

Location

Regina General Hospital

Regina, Saskatchewan, S4P 0W5, Canada

Location

MeSH Terms

Conditions

Heart DiseasesBicuspid Aortic Valve Disease

Interventions

AtenololTelmisartan

Condition Hierarchy (Ancestors)

Cardiovascular DiseasesHeart Defects, CongenitalCardiovascular AbnormalitiesAortic Valve DiseaseHeart Valve DiseasesCongenital AbnormalitiesCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Intervention Hierarchy (Ancestors)

PhenoxypropanolaminesPropanolaminesAmino AlcoholsAlcoholsOrganic ChemicalsPropanolsAminesBiphenyl CompoundsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsBenzimidazolesHeterocyclic Compounds, 2-RingHeterocyclic Compounds, Fused-RingHeterocyclic Compounds

Results Point of Contact

Title
Dr. Tara McCready, Program Director
Organization
Population Health Research Institute

Study Officials

  • Judith Therrien, MD

    MdGill University

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
PREVENTION
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 14, 2010

First Posted

September 16, 2010

Study Start

June 1, 2011

Primary Completion

April 19, 2016

Study Completion

November 1, 2016

Last Updated

September 18, 2019

Results First Posted

September 18, 2019

Record last verified: 2019-08

Locations