NCT01134432

Brief Summary

The conventional treatment in warm-antibody dependent autoimmune haemolytic anaemia (AIHA) is high-dose glucocorticoid, but in more than half of the patients, haemolytic activity will recur after end of treatment or during the gradual reduction in dose of the drug. As a result, many patients will finally be splenectomized or be treated with long-term glucocorticoids or other immunosuppressive drugs as azathioprine or cyclophosphamide. Recent studies have shown however, that some patients will respond to treatment with the chimeric anti-CD 20 antibody Rituximab and is some cases, the response is permanent. In most of the studies, Rituximab has been used in refractory disease or at least as second line treatment. In this study, patients with AIHA are randomized to receive either high-dose prednisolone with gradual reduction in dose over 2-3 months alone or in combination with Rituximab 375 mg/m2 once a week for 4 weeks. The efficacy of Rituximab will be evaluated by a comparison of the patients in the two treatment arms. The primary treatment goal is a reduction in the number of patients who obtain long-term complete or partial remission. The secondary treatment goal is a reduction in patients who will be splenectomised or receive other immunosuppressive drugs. Finally a comparison of side effects of the treatments will take place.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
65

participants targeted

Target at below P25 for phase_3

Timeline
Completed

Started Mar 2005

Longer than P75 for phase_3

Geographic Reach
1 country

11 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 1, 2005

Completed
5.2 years until next milestone

First Submitted

Initial submission to the registry

May 28, 2010

Completed
5 days until next milestone

First Posted

Study publicly available on registry

June 2, 2010

Completed
2.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2012

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2012

Completed
Last Updated

September 10, 2013

Status Verified

September 1, 2013

Enrollment Period

7.3 years

First QC Date

May 28, 2010

Last Update Submit

September 9, 2013

Conditions

Keywords

autoimmune hemolytic anemiahemolytic anemiaRituximabTreatment of autoimmune hemolytic anemiawarm antibody dependant autoimmune hemolytic anemia

Outcome Measures

Primary Outcomes (1)

  • Number of patients in each group in complete or partial remission

    End of treatment and follow-up for 12 months

Secondary Outcomes (1)

  • Side effects

    End of treatment plus follow-up for 12 months

Study Arms (2)

Prednisolone + Rituximab

EXPERIMENTAL
Drug: prednisolone + mabthera

Prednisolone

ACTIVE COMPARATOR
Drug: Prednisolone

Interventions

Prednisolone: 1,5 mg/kg for two weeks with gradually reduced dosis over two months. Mabthera: 375 mg/m2 once a week for four weeks

Also known as: mabthera equals Rituximab
Prednisolone + Rituximab

Prednisolone: 1,5 mg/kg for two weeks and then gradually reduced dosis over two months

Prednisolone

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age 18 years or over
  • Clinical and biochemical signs of haemolytic anaemia
  • Positive Coombs test with anti-IgG on its own or with anti-CD3d
  • Adequate contraceptive measures (intrauterine device, contraceptive pill or gestagen deposit) for women of childbearing potential

You may not qualify if:

  • Performance status \> 2
  • Previous treatment with Rituximab
  • Other immune suppressive or anti neoplastic treatment including prednisolone within 3 months
  • Auto immune haemolytic anaemia within 6 months
  • Other serious disease
  • Pregnant women and nursing mothers. Adequate contraceptive measures must be taken for the duration of the study.
  • Contraindication for treatment with Rituximab, i.e. patients that develop hypersensitivity/allergy to the contents of the drug or have antibodies against murine proteins.
  • Active infection which requires antibiotic treatment

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (11)

Aalborg Hospital

Aalborg, DK-9000, Denmark

Location

Rigshospitalet - Copenhagen University Hospital

Copenhagen, DK-2100, Denmark

Location

Esbjerg Sygehus

Esbjerg, DK-6700, Denmark

Location

Haderslev Sygehus

Haderslev, DK-6100, Denmark

Location

Department of Haematology, Herlev Hospital

Herlev, DK-2730, Denmark

Location

Holstebro Sygehus

Holstebro, DK-7500, Denmark

Location

Naestved Sygehus

Næstved, DK-4700, Denmark

Location

Odense University Hospital

Odense, DK-5000, Denmark

Location

Roskilde Hospital

Roskilde, DK-4000, Denmark

Location

Vejle Hospital

Vejle, DK-7100, Denmark

Location

Viborg Sygehus

Viborg, DK-8800, Denmark

Location

MeSH Terms

Conditions

Anemia, Hemolytic, AutoimmuneAnemia, Hemolytic

Interventions

PrednisoloneRituximab

Condition Hierarchy (Ancestors)

AnemiaHematologic DiseasesHemic and Lymphatic DiseasesAutoimmune DiseasesImmune System Diseases

Intervention Hierarchy (Ancestors)

PregnadienetriolsPregnadienesPregnanesSteroidsFused-Ring CompoundsPolycyclic CompoundsAntibodies, Monoclonal, Murine-DerivedAntibodies, MonoclonalAntibodiesImmunoglobulinsImmunoproteinsBlood ProteinsProteinsAmino Acids, Peptides, and ProteinsSerum GlobulinsGlobulins

Study Officials

  • Henrik S Birgens, MD

    Department of Haematology (L121), Copenhagen University Hospital Herlev

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 28, 2010

First Posted

June 2, 2010

Study Start

March 1, 2005

Primary Completion

July 1, 2012

Study Completion

July 1, 2012

Last Updated

September 10, 2013

Record last verified: 2013-09

Locations