NCT01101906

Brief Summary

This is a randomized, placebo-controlled, double-blind phase 2 study of OSI-906 or placebo at a continuous 150 mg twice daily (BID) dose.

Trial Health

68
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
23

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Jan 2011

Shorter than P25 for phase_2

Geographic Reach
10 countries

41 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

April 8, 2010

Completed
4 days until next milestone

First Posted

Study publicly available on registry

April 12, 2010

Completed
9 months until next milestone

Study Start

First participant enrolled

January 10, 2011

Completed
10 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

November 4, 2011

Completed
2 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 28, 2011

Completed
Last Updated

November 20, 2024

Status Verified

November 1, 2024

Enrollment Period

10 months

First QC Date

April 8, 2010

Last Update Submit

November 18, 2024

Conditions

Keywords

HCCOSI-906Hepatocellular Carcinoma

Outcome Measures

Primary Outcomes (1)

  • Time to progression (TTP)

    Time from randomization to radiological disease progression based on Response Evaluation Criteria in Solid Tumors (RECIST) version 1.1

    20 months

Secondary Outcomes (10)

  • Overall Survival (OS)

    23 months

  • Progression Free Survival (PFS)

    23 months

  • Time to Progression (including clinical progression) (TTPc)

    23 months

  • Disease Control Rate (DCR)

    23 months

  • Overall Response Rate

    23 months

  • +5 more secondary outcomes

Study Arms (2)

Arm A: OSI-906

EXPERIMENTAL

150 mg BID

Drug: OSI-906

Arm B: Placebo

PLACEBO COMPARATOR

Placebo BID

Drug: Placebo

Interventions

OSI-906 administered orally

Arm A: OSI-906

Matching placebo administered orally

Arm B: Placebo

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Histologically confirmed diagnosis of advanced HCC. Clinical diagnosis by American Association for the Study of Liver Diseases (AASLD) criteria in cirrhotic patients is acceptable. For patients without cirrhosis histological confirmation is mandatory
  • Patients must have received prior systemic treatment for advanced HCC with sorafenib and had confirmed disease progression or had discontinued sorafenib due to a drug related toxicity
  • Patient has received their last dose of sorafenib at least 14 days prior to randomization
  • Patient has recovered from sorafenib or investigational agent related toxicity to ≤ grade 2
  • Measurable disease according to RECIST (version 1.1)
  • Eastern Cooperative Oncology Group (ECOG) Performance Status (PS) 0 - 1
  • Child-Pugh Status A or B(7)
  • Barcelona Clinic Liver Cancer (BCLC) stage B/C
  • Previous local therapy (eg, surgery, radiation therapy, hepatic arterial therapy, chemoembolization, radiofrequency ablation, percutaneous ethanol injection, or cryoablation) is permitted if ≥ 21 days before randomization
  • Fasting glucose ≤ 150 mg/dL (8.3 mmol/L). Concurrent use of non-insulinotropic oral antihyperglycemic therapy is permitted if the dose has been stable for ≥ 4 weeks at the time of randomization
  • Following laboratory parameters (determined by laboratory):
  • Platelets ≥ 60 x 10\^9/L
  • Hemoglobin ≥ 8.5 g/dL
  • Absolute neutraphil count (ANC) ≥ 1.5 x 10\^9/L
  • Potassium within normal limits (supplementation may be used)
  • +14 more criteria

You may not qualify if:

  • Child-Pugh B (8 - 9) or C
  • Patients who are candidates for potentially curative intervention (ie, surgical resection or transplantation)
  • Type 1 diabetes mellitus or Type 2 diabetes mellitus currently requiring insulinotropic or insulin therapy
  • Prior insulin-like growth factor - 1 receptor (IGF-1R) therapy
  • Patients requiring interferon
  • Patients with uncontrolled symptomatic ascites
  • Prior investigational agent within 21 days prior to randomization
  • History of poorly controlled gastrointestinal disorders that could affect the absorption of study drug (eg, Crohn's disease, ulcerative colitis, etc)
  • History of organ allograft including liver transplant
  • Malignancy other than HCC within the past 3 years:
  • Exceptions: resected basal cell or squamous cell carcinoma of the skin, cured in situ cervical carcinoma, cured ductal carcinoma in situ of the breast, and/or cured superficial bladder cancer
  • History (within last 6 months) of significant cardiovascular disease unless the disease is well-controlled. Significant cardiac disease includes second/third degree heart block; clinically significant ischemic heart disease; superior vena cava (SVC) syndrome; poorly controlled hypertension; congestive heart failure of New York Heart Association (NYHA) Class II or worse (slight limitation of physical activity; comfortable at rest, but ordinary physical activity results in fatigue, palpitation, or dyspnea)
  • History of arrhythmia (multifocal premature ventricular contractions \[PVCs\], bigeminy, trigeminy, ventricular tachycardia, or uncontrolled atrial fibrillation) that is symptomatic or requires treatment (≥ grade 3), left bundle branch block (LBBB), or asymptomatic sustained ventricular tachycardia are not allowed. Patients with atrial fibrillation controlled by medication are not excluded
  • QTcF interval at screening ≥ 450 msec
  • Use of drugs that have a known risk of causing Torsades de Pointes (TdP) ('Torsades List' on www.azcert.org/medical-pros/drug-lists/by category.cfm)are prohibited within 14 days prior to randomization
  • +8 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (41)

University of California - Los Angeles

Los Angeles, California, 90095, United States

Location

Tulane University Health Services Center

New Orleans, Louisiana, 70112, United States

Location

Oregon Health & Science University

Portland, Oregon, 97239, United States

Location

Virginia Mason Medical Center

Seattle, Washington, 98101, United States

Location

Seattle Cancer Care Alliance University of Washington

Seattle, Washington, 98109, United States

Location

Medical College of Wisconsin

Milwaukee, Wisconsin, 52336, United States

Location

Cliniques Universitaires Saint-Luc

Brussells, 1200, Belgium

Location

Universitair Ziekenhuis Gent

Ghent, 9000, Belgium

Location

Hopital Jean Verdier - Dervice d'Hepato-Gastroenterologie

Bondy, 93143, France

Location

Hôpital Henri Mondor

Créteil, 94010, France

Location

Hopital de la Timone

Marseille, 13385, France

Location

Hopital l'Archet 2

Nice, 6202, France

Location

Hôpital Saint-Antoine

Paris, 75012, France

Location

Hôpital de Tenon

Paris, 75020, France

Location

Centre Rene Gauducheau

Saint-Herblain, 44805, France

Location

Universitatsklinikum Essen

Essen, 45122, Germany

Location

Universitätsklinikum Halle

Halle, 06097, Germany

Location

Universitatsklinikum des Saarlandes

Homburg, 66421, Germany

Location

Universitätsklinikum Magdeburg A.ö.R.

Magdeburg, 39120, Germany

Location

Queen Mary Hospital

Hong Kong, Hong Kong

Location

Fondazione Ca' Granda Ospedale Maggiore Policlinico, Divisione di Gastroenterologia I

Milan, 20122, Italy

Location

Ospedale Fatebenefratelli, Dipartimento Medicina Interna

Napoli, 80123, Italy

Location

IRCCS Istituto Nazionale per lo studio e la cura dei tumori Fondazione G. Pascale-SSD Epatobiliare

Napoli, 80131, Italy

Location

Istituto Mediterraneo per i Trapianti e Terapie ad Alta Specializzazione ISMETT-Dipartimento di Epatologia e Gastroenterologia

Palermo, 90127, Italy

Location

Singapore General Hospital

Singapore, 169608, Singapore

Location

Johns Hopkins Singapore International Medical Centre

Singapore, 308433, Singapore

Location

Pusan National University Hospital

Busan, 602-739, South Korea

Location

Kyungpook National University Hospital

Daegu, 700-721, South Korea

Location

National Cancer Center

Goyang-si, 410-769, South Korea

Location

Seoul National University Hospital

Seoul, 110-774, South Korea

Location

Severance Hospital

Seoul, 120-752, South Korea

Location

Samsung Medical Center

Seoul, 135-710, South Korea

Location

Hospital Clinico Universitario de Santiago de Compostela

Santiago de Compostela, Coruna, 15706, Spain

Location

Hospital Clinic Provincial

Barcelona, 08036, Spain

Location

Hospital Puerta de Hierro Majadahonda

Madrid, 28220, Spain

Location

Clinica Universitaria de Navarra

Pamplona, 31008, Spain

Location

Changhua Christian Hospital

Changhua, 500, Taiwan

Location

Kaohsiung Medical University Chung-Ho Memorial Hospital

Kaohsiung City, 807, Taiwan

Location

Taichung Veterans General Hospital

Taichung, 40705, Taiwan

Location

China Medical University Hospital

Taichung, Taiwan

Location

Chang Gung Medical Foundation LinKou Branch

Taoyuan District, 333, Taiwan

Location

Related Links

MeSH Terms

Conditions

Carcinoma, Hepatocellular

Interventions

3-(8-amino-1-(2-phenylquinolin-7-yl)imidazo(1,5-a)pyrazin-3-yl)-1-methylcyclobutanol

Condition Hierarchy (Ancestors)

AdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic TypeNeoplasmsLiver NeoplasmsDigestive System NeoplasmsNeoplasms by SiteDigestive System DiseasesLiver Diseases

Study Officials

  • Medical Director

    Astellas Pharma Global Development

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 8, 2010

First Posted

April 12, 2010

Study Start

January 10, 2011

Primary Completion

November 4, 2011

Study Completion

December 28, 2011

Last Updated

November 20, 2024

Record last verified: 2024-11

Data Sharing

IPD Sharing
Will not share

Access to anonymized individual participant level data will not be provided for this trial. Further details on Astellas' data sharing policy can be found at https://www.clinicaltrials.astellas.com/transparency/.

Locations