NCT01075113

Brief Summary

This phase I trial is studying the side effects and best dose of vorinostat when given together with sorafenib tosylate in treating patients with advanced liver cancer. Sorafenib tosylate and vorinostat may stop the growth of tumor cells by blocking some of the enzymes needed for cell growth or by blocking blood flow to the tumor.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
16

participants targeted

Target at below P25 for phase_1

Timeline
Completed

Started Aug 2010

Longer than P75 for phase_1

Geographic Reach
1 country

2 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

February 19, 2010

Completed
5 days until next milestone

First Posted

Study publicly available on registry

February 24, 2010

Completed
6 months until next milestone

Study Start

First participant enrolled

August 10, 2010

Completed
6.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 2, 2017

Completed
2.5 years until next milestone

Study Completion

Last participant's last visit for all outcomes

July 18, 2019

Completed
Last Updated

August 20, 2019

Status Verified

August 1, 2019

Enrollment Period

6.5 years

First QC Date

February 19, 2010

Last Update Submit

August 16, 2019

Conditions

Keywords

adult primary hepatocellular carcinomaadvanced adult primary liver cancerrecurrent adult primary liver cancer

Outcome Measures

Primary Outcomes (1)

  • Determine the appropriate Doses for the combination of sorafenib tosylate and vorinostat appropriate for phase II study in hepatocellular carcinoma (HCC).

    Identify the maximum tolerated dose of the combination regimen of vorinostat and sorafenib to study further for efficacy of treatment for hepatocellular carcinoma

    4 weeks

Secondary Outcomes (2)

  • Adverse events will be characterized in terms of nature, severity, attribution, onset and resolution according to the National Cancer Institute (NCI) Common Terminology Criteria for Adverse Events (CTCAE) v4.0.

    Up to 30 days post-treatment

  • Anti-tumor effects of the combination of sorafenib tosylate and vorinostat

    Up to 6 years

Study Arms (2)

Arm A

EXPERIMENTAL

Sorafenib + Vorinostat. Patients receive sorafenib tosylate PO BID continuously and vorinostat PO QD, for 5 days each week. Courses repeat every 4 weeks in the absence of disease progression or unacceptable toxicity. Cohort A has only one dose level: sorafenib 400 mg orally twice a day with vorinostat 300 mg orally. Cohort A was modified to include 2 dose levels: Dose level A1 (sorafenib 400 mg orally twice a day and vorinostat 200 mg orally once a day) and dose level A-1 (sorafenib 400 mg orally twice a day with vorinostat 100 mg orally once a day). The starting dose upon reopening after approval of this version will be dose level A-1a. Dose level A1 will only be used if dose level A-1a is not tolerable.

Drug: sorafenib tosylateDrug: vorinostat

Arm B CLOSED

EXPERIMENTAL

Reduced Dose 200mg Sorafenib + Vorinostat. Patients receive sorafenib tosylate PO BID continuously and vorinostat PO QD, for 5 days each week. Courses repeat every 4 weeks in the absence of disease progression or unacceptable toxicity. Cohort B has 2 dose levels starting at the second dose level (sorafenib 200 mg orally twice a day with vorinostat 400 mg orally). Cohort B has been closed. Cohort B was intended to evaluate the possibility of dose intensification of vorinostat when patients were unable to tolerate standard dose sorafenib, and required dose-reduced sorafenib. The patients accrued to date in Cohort B were unable to tolerate therapy, and it has been determined that dose intensification of vorinostat is not possible, despite reducing the dose of sorafenib.

Drug: sorafenib tosylateDrug: vorinostat

Interventions

Given orally

Also known as: BAY 43-9006, BAY 43-9006 Tosylate Salt, BAY 54-9085, Nexavar, SFN
Arm AArm B CLOSED

Given orally

Also known as: L-001079038, SAHA, suberoylanilide hydroxamic acid, Zolinza
Arm AArm B CLOSED

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of HCC by biopsy-proven pathologic diagnosis or by clinical criteria as defined below:
  • \* Clinical criteria to be met if patient has a history of cirrhosis or chronic hepatitis B infection:
  • Imaging abnormalities \> 1 cm in size with classic enhancement by magnetic resonance imaging (MRI) or triple-phase computed tomography (CT) scan
  • Alpha-fetoprotein (AFP) of any value
  • Performance status Eastern Cooperative Oncology Group (ECOG) =\< 1
  • If cirrhosis, Child-Pugh classification A or B
  • Total bilirubin =\< 3.0 mg/dL
  • Creatinine =\< 1.5 x upper limit of normal for the laboratory
  • International normalized ratio (INR) =\< 1.7 (if not due to anticoagulants)
  • Absolute neutrophil count (ANC) \>= 1,500/mm\^3
  • Platelets \>= 80,000/mm\^3
  • Hemoglobin (Hgb) \>= 8.5 g/dL (transfusion or erythropoietin-like substances not permitted prior to baseline evaluation)
  • Any prior therapies such as surgery, chemoembolization, radiofrequency ablation, and alcohol injection are allowed as long as toxicity from such prior therapy is =\< grade 1
  • Prior sorafenib is allowed as long as toxicity from ongoing is ≤ grade 2 and prior intolerance of 400 mg sorafenib PO daily is felt amenable, by the principal investigator, to supportive care measures or dose modifications.
  • Measurable or evaluable disease by Response Evaluation Criteria in Solid Tumors (RECIST) criteria version (v) 1.1 mRECIST or elevated AFP
  • +3 more criteria

You may not qualify if:

  • Candidate for curative therapy including surgical resection or orthotopic liver transplantation
  • Known central nervous system metastasis
  • Any investigational agent within 4 weeks of first dose of study treatment
  • Known intolerance of vorinostat
  • Unable to swallow medication
  • Unable to swallow medication; suspected malabsorption
  • Active alcohol abuse
  • Contraindication to antiangiogenic agents, including:
  • Pulmonary hemorrhage/bleeding event \>= grade 2 within 4 weeks of first dose of study drug
  • Any other hemorrhage/bleeding event \>= grade 3 within 4 weeks of first dose of study treatment
  • Serious non-healing wound, ulcer, or bone fracture
  • Major cardiac dysfunction, such as uncontrolled angina, congestive heart failure with New York Heart Association (NYHA) class III or higher, known left ventricular ejection fraction less than 40%
  • Systolic blood pressure \> 160 mmHg or diastolic pressure \> 90 mmHg despite optimal medical management
  • Significant lung disease (oxygen \[O2\] saturation less than 88% in room air)
  • Serious uncontrolled infection; known human immunodeficiency virus (HIV)-seropositivity requiring retroviral therapy, or diagnosis of acquired immune deficiency syndrome (AIDS); diagnosis of chronic hepatitis B or C allowed
  • +1 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (2)

Hunter Holmes McGuire VA Medical Center

Richmond, Virginia, 23249, United States

Location

Virginia Commonwealth University/Massey Cancer Center

Richmond, Virginia, 23298, United States

Location

Related Publications (1)

  • Gordon SW, McGuire WP 3rd, Shafer DA, Sterling RK, Lee HM, Matherly SC, Roberts JD, Bose P, Tombes MB, Shrader EE, Ryan AA, Kmieciak M, Nguyen T, Deng X, Bandyopadhyay D, Dent P, Poklepovic AS. Phase I Study of Sorafenib and Vorinostat in Advanced Hepatocellular Carcinoma. Am J Clin Oncol. 2019 Aug;42(8):649-654. doi: 10.1097/COC.0000000000000567.

MeSH Terms

Conditions

Liver NeoplasmsCarcinoma, Hepatocellular

Interventions

SorafenibVorinostat

Condition Hierarchy (Ancestors)

Digestive System NeoplasmsNeoplasms by SiteNeoplasmsDigestive System DiseasesLiver DiseasesAdenocarcinomaCarcinomaNeoplasms, Glandular and EpithelialNeoplasms by Histologic Type

Intervention Hierarchy (Ancestors)

Phenylurea CompoundsUreaAmidesOrganic ChemicalsBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsNiacinamideNicotinic AcidsAcids, HeterocyclicHeterocyclic CompoundsPyridinesHeterocyclic Compounds, 1-RingAnilidesAniline CompoundsAminesHydroxamic AcidsHydroxylaminesHydroxy AcidsCarboxylic Acids

Study Officials

  • Andrew S. Poklepovic, MD

    Massey Cancer Center

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 19, 2010

First Posted

February 24, 2010

Study Start

August 10, 2010

Primary Completion

February 2, 2017

Study Completion

July 18, 2019

Last Updated

August 20, 2019

Record last verified: 2019-08

Locations