NCT01052194

Brief Summary

This study is designed to evaluate safety and assess initial efficacy of VX-509, a JAK3 inhibitor, for treatment of subjects with active RA. This study will assess the clinical response of 4 doses of VX-509 compared to placebo when administered for 12 weeks to patients with active RA. The study will also evaluate the safety and tolerability of VX-509 compared to placebo when administered for 12 weeks to subjects with active RA.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
206

participants targeted

Target at P50-P75 for phase_2 rheumatoid-arthritis

Timeline
Completed

Started Feb 2010

Geographic Reach
10 countries

48 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 18, 2010

Completed
2 days until next milestone

First Posted

Study publicly available on registry

January 20, 2010

Completed
12 days until next milestone

Study Start

First participant enrolled

February 1, 2010

Completed
1.4 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2011

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2011

Completed
Last Updated

December 13, 2012

Status Verified

December 1, 2012

Enrollment Period

1.4 years

First QC Date

January 18, 2010

Last Update Submit

December 12, 2012

Conditions

Keywords

Rheumatoid Arthritis

Outcome Measures

Primary Outcomes (2)

  • Proportion of subjects who achieve an ACR20 response

    Week 12

  • Change from baseline in DAS28

    Week 12

Secondary Outcomes (5)

  • Proportion of subjects who achieve an ACR50,70 response

    Week 12

  • Proportion of subjects who achieve moderate or good EULAR response

    Week 12

  • Magnitude of improvement in the components of the ACR response criteria

    Week 12

  • Pharmacokinetics of VX-509

    Week 6

  • Pharmacodynamics (PD) of biomarker responses

    Week 6

Study Arms (5)

25 mg b.i.d. VX-509

EXPERIMENTAL
Drug: VX-509

50 mg b.i.d. VX-509

EXPERIMENTAL
Drug: VX-509

100 mg b.i.d. VX-509

EXPERIMENTAL
Drug: VX-509

150 mg b.i.d. VX-509

EXPERIMENTAL
Drug: VX-509

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

tablet, placebo b.i.d. for 12 weeks

Placebo
VX-509DRUG

tablets, 25mg b.i.d. for 12 weeks

25 mg b.i.d. VX-509

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • All subjects must have been diagnosed with RA as defined by the ACR revised criteria with disease duration of at least 6 months from confirmed diagnosis
  • Subjects must have a swollen joint count of ≥6 out of 28 joints and tender joint count of ≥6 out of 28 joints. Joints that have had prior surgery are to be excluded from the joint count.
  • Baseline CRP level must be 1.5 times greater than the upper limit of normal at Screening.
  • Subjects must have failed at least 1 nonbiologic DMARD for any reason.
  • Subjects may have previously failed no more than 1 biologic DMARD and discontinued treatment for reasons other than inadequate response. Subjects must not have been treated with Rituximab previously.
  • Subjects must be willing to comply with contraception requirements.

You may not qualify if:

  • Subjects with inflammatory rheumatological disorders other than RA.
  • History or evidence of a clinically significant disorder other than RA (including but not limited to cardiopulmonary, oncologic, renal, metabolic, hematologic or psychiatric disorders), condition or disease that, in the opinion of the investigator and medical monitor, would pose a risk to subject safety or interfere with the study evaluation, procedures, or completion.
  • Subjects with clinically important abnormalities in screening physical examination or in screening laboratory test results (including the presence of either hepatitis B surface antigen, hepatitis C virus antibody, or HIV types 1 -- Subjects with elevation in alanine aminotransferase or aspartate aminotransferase above the upper limit of normal.
  • History of hematologic disorders including neutropenia and thrombocytopenia.
  • Subjects with an acute or chronic active infection requiring systemic antimicrobial treatment, or subjects who are at high risk of developing an infection due to a compromised immune system. Antifungals for onychomycosis or low-dose antibiotics for rosacea, that are not inhibitors or inducers of CYP3A, will be allowed.
  • Subjects who require concomitant use of any inhibitors or inducers of cytochrome P450 (CYP) 3A.
  • Subjects who have been treated with intra-articular injections of corticosteroids within 28 days prior to Day 1.
  • Subjects who have planned major surgery (e.g., joint replacement) or any procedures during the study.
  • Have received any live, attenuated vaccinations within 1 month prior to study drug administration.
  • History of drug or alcohol abuse or excessive alcohol as determined by the investigator, during the last 12 months before the screening visit.
  • History of TB infection of any kind (pulmonary or extrapulmonary, active or latent), regardless of history of anti-TB treatment.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (48)

Unknown Facility

Birmingham, Alabama, 35216, United States

Location

Unknown Facility

Huntsville, Alabama, 35801, United States

Location

Unknown Facility

Peoria, Arizona, 85381, United States

Location

Unknown Facility

La Mesa, California, 97942, United States

Location

Unknown Facility

Trumbull, Connecticut, 06611, United States

Location

Unknown Facility

Tampa, Florida, 33612, United States

Location

Unknown Facility

Tampa, Florida, 33614, United States

Location

Unknown Facility

Venice, Florida, 34292, United States

Location

Unknown Facility

Decatur, Georgia, 30033, United States

Location

Unknown Facility

Worcester, Massachusetts, 01610, United States

Location

Unknown Facility

St Louis, Missouri, 63141, United States

Location

Unknown Facility

Charlotte, North Carolina, 28210, United States

Location

Unknown Facility

Oklahoma City, Oklahoma, 73104, United States

Location

Unknown Facility

Duncansville, Pennsylvania, 16635, United States

Location

Unknown Facility

Charleston, South Carolina, 29406, United States

Location

Unknown Facility

Dallas, Texas, 75235, United States

Location

Unknown Facility

Spokane, Washington, 99204, United States

Location

Unknown Facility

Clarksburg, West Virginia, 26301, United States

Location

Unknown Facility

Antwerp, Belgium

Location

Unknown Facility

Karlovac, Croatia

Location

Unknown Facility

Opatija, Croatia

Location

Unknown Facility

Zagreb, Croatia

Location

Unknown Facility

Erfurt, Germany

Location

Unknown Facility

Frankfurt, Germany

Location

Unknown Facility

Hamburg, Germany

Location

Unknown Facility

Hildesheim, Germany

Location

Unknown Facility

Nauheim, Germany

Location

Unknown Facility

Zerbst, Germany

Location

Unknown Facility

Balatonfüred, Hungary

Location

Unknown Facility

Budapest, Hungary

Location

Unknown Facility

Debrecen, Hungary

Location

Unknown Facility

Veszprém, Hungary

Location

Unknown Facility

Elblag, Poland

Location

Unknown Facility

Limanow, Poland

Location

Unknown Facility

Lublin, Poland

Location

Unknown Facility

Wroclaw, Poland

Location

Unknown Facility

San Juan, Puerto Rico

Location

Unknown Facility

Baia Mare, Romania

Location

Unknown Facility

Brăila, Romania

Location

Unknown Facility

Bucharest, Romania

Location

Unknown Facility

Galati, Romania

Location

Unknown Facility

Kemerovo, Russia

Location

Unknown Facility

Novosibirsk, Russia

Location

Unknown Facility

Ryazan, Russia

Location

Unknown Facility

Vladimir, Russia

Location

Unknown Facility

Voronezh, Russia

Location

Unknown Facility

Belgrade, Serbia

Location

Unknown Facility

Niška Banja, Serbia

Location

MeSH Terms

Conditions

Arthritis, Rheumatoid

Interventions

2-((2-(1H-pyrrolo(2,3-b)pyridin-3-yl)pyrimidin-4-yl)amino)-2-methyl-N-(2,2,2-trifluoroethyl)butanamide

Condition Hierarchy (Ancestors)

ArthritisJoint DiseasesMusculoskeletal DiseasesRheumatic DiseasesConnective Tissue DiseasesSkin and Connective Tissue DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • Medical Monitor

    Vertex Pharmaceuticals Incorporated

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 18, 2010

First Posted

January 20, 2010

Study Start

February 1, 2010

Primary Completion

July 1, 2011

Study Completion

July 1, 2011

Last Updated

December 13, 2012

Record last verified: 2012-12

Locations