NCT01049919

Brief Summary

This trial will evaluate the safety and efficacy of concentrated bone marrow aspirate (cBMA) to prevent or delay major amputation and/or death in subjects with critical limb ischemia (CLI) due to severe peripheral arterial disease (PAD).

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
153

participants targeted

Target at P75+ for not_applicable

Timeline
Completed

Started Jun 2010

Longer than P75 for not_applicable

Geographic Reach
1 country

25 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

January 14, 2010

Completed
1 day until next milestone

First Posted

Study publicly available on registry

January 15, 2010

Completed
5 months until next milestone

Study Start

First participant enrolled

June 1, 2010

Completed
6 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

June 1, 2016

Completed
3.7 years until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2020

Completed
1.3 years until next milestone

Results Posted

Study results publicly available

May 28, 2021

Completed
Last Updated

May 28, 2021

Status Verified

May 1, 2021

Enrollment Period

6 years

First QC Date

January 14, 2010

Results QC Date

January 22, 2021

Last Update Submit

May 5, 2021

Conditions

Keywords

Critical Limb IschemiaPeripheral Arterial DiseasePeripheral Vascular DiseaseCLIPADPVDAngiogenesisStem CellsCell TherapyLimb SalvageAmputationLeg Pain

Outcome Measures

Primary Outcomes (1)

  • Occurrence of Major Amputation or Death

    Occurrence of major amputation (above the ankle joint) or death.

    52 weeks

Secondary Outcomes (2)

  • Visual Analog Scale (VAS) - Pain

    52 weeks

  • Six-Minute Walk Test

    52 weeks

Other Outcomes (1)

  • Occurrence of Major Amputation or Death

    5 years

Study Arms (2)

Concentrated bone marrow aspirate (cBMA)

EXPERIMENTAL

Collection of autologous bone marrow aspirate and point-of-care concentration using the bone marrow concentration device, followed by intramuscular injection of concentrated bone marrow aspirate (cBMA) into the affected limb

Device: Bone marrow concentration device

Placebo control (sham)

SHAM COMPARATOR

Placebo procedure (sham) consists of simulated bone marrow aspiration followed by simulated intramuscular injections into the affected limb

Procedure: Placebo procedure (sham)

Interventions

Concentration of autologous bone marrow aspirate for intramuscular delivery to affected limb

Also known as: Bone marrow concentrate, Bone marrow mononuclear cells, MarrowStim
Concentrated bone marrow aspirate (cBMA)

Sham bone marrow aspiration, sham delivery to affected limb

Placebo control (sham)

Eligibility Criteria

Age21 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Unilateral or bilateral lower extremity ischemia due to advanced peripheral arterial disease
  • Unsuitable for revascularization
  • Minor tissue loss (Rutherford Category 5) or ischemic rest pain (Rutherford Category 4) with ABI ≤ 0.6, or TBI ≤ 0.4, or TcPO2 ≤ 50 mm Hg
  • Competent to give consent
  • No current malignancy or history of previous malignancy within the last five years, with the exception of adequately treated non-melanoma skin cancer (evidence of standard preventative cancer screenings required)

You may not qualify if:

  • Major tissue loss (Rutherford Category 6)
  • Diabetics on oral or insulin therapy with uncontrolled or untreated proliferative retinopathy (evidence of retinal exam required)
  • Poorly controlled diabetes mellitus with HbA1C \> 10% (evidence of HbA1C test required)
  • Uncompensated congestive heart failure (New York Heart Association Class IV) and/or other conditions that preclude general anesthesia
  • Myocardial infarction or stroke within last 90 days
  • Elevated liver function tests (AST or ALT more than twice normal upper limit)
  • Renal disease (creatinine \> 2.5 mg/dl) or chronic hemodialysis
  • White blood cell count \< 3,000/µL or \> 15,000/µL, platelet count \< 100,000/µL, or hematocrit \< 32%
  • Topical growth hormone therapy within last 90 days, or injected growth hormone therapy within last 180 days
  • Disease of central nervous system and/or other conditions that impair cognitive function
  • Two or more episodes of pulmonary embolus with a documented DVT in index leg or history of DVT in index leg without evidence of clot resolution
  • Current infection of index leg
  • Pregnant women (negative urine pregnancy test required)
  • Lower extremity venous disease with pitting edema in index leg
  • Recent history (in the 6 months prior to screening) of bone marrow disease or treatment with any medication or procedure which adversely affects the bone marrow and would prohibit transplantation
  • +6 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (25)

Central Arkansas Veterans Healthcare System

Little Rock, Arkansas, 72205, United States

Location

University of California-Davis Medical Center

Sacramento, California, 95817, United States

Location

University of Miami

Miami, Florida, 33136, United States

Location

Piedmont Hospital

Atlanta, Georgia, 30309, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

Indiana University School of Medicine

Indianapolis, Indiana, 46202, United States

Location

University of Iowa Hospitals and Clinics

Iowa City, Iowa, 52242, United States

Location

University of Louisville

Louisville, Kentucky, 40202, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

UMass Memorial Health Care

Worcester, Massachusetts, 01655, United States

Location

Spectrum Health

Grand Rapids, Michigan, 49503, United States

Location

Saint Luke's Hospital

Kansas City, Missouri, 64111, United States

Location

Nebraska-Western Iowa VA Healthcare System

Omaha, Nebraska, 68105, United States

Location

Holy Name Medical Center

Teaneck, New Jersey, 07666, United States

Location

The Mount Sinai Hospital

New York, New York, 10029, United States

Location

Weill Cornell Medical College / New York-Presbyterian Hospital

New York, New York, 10065, United States

Location

University Hospitals Cleveland Medical Center

Cleveland, Ohio, 44106, United States

Location

The Cleveland Clinic

Cleveland, Ohio, 44195, United States

Location

Remington-Davis

Columbus, Ohio, 43215, United States

Location

Temple University Hospital

Philadelphia, Pennsylvania, 19140, United States

Location

VA Pittsburgh Healthcare System

Pittsburgh, Pennsylvania, 15240, United States

Location

The Methodist Hospital

Houston, Texas, 77030, United States

Location

University of Virginia Hospital

Charlottesville, Virginia, 22908, United States

Location

Providence Sacred Heart Medical Center

Spokane, Washington, 99204, United States

Location

Aurora St. Luke's Medical Center

Milwaukee, Wisconsin, 53215, United States

Location

Related Publications (1)

  • Murphy MP, Lawson JH, Rapp BM, Dalsing MC, Klein J, Wilson MG, Hutchins GD, March KL. Autologous bone marrow mononuclear cell therapy is safe and promotes amputation-free survival in patients with critical limb ischemia. J Vasc Surg. 2011 Jun;53(6):1565-74.e1. doi: 10.1016/j.jvs.2011.01.074. Epub 2011 Apr 22.

    PMID: 21514773BACKGROUND

MeSH Terms

Conditions

Chronic Limb-Threatening IschemiaPeripheral Arterial DiseasePeripheral Vascular Diseases

Interventions

salicylhydroxamic acid

Condition Hierarchy (Ancestors)

AtherosclerosisArteriosclerosisArterial Occlusive DiseasesVascular DiseasesCardiovascular DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsIschemia

Results Point of Contact

Title
Hillary Overholser
Organization
Zimmer Biomet

Study Officials

  • Michael P. Murphy, MD

    Indiana University School of Medicine

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
not applicable
Allocation
RANDOMIZED
Masking
DOUBLE
Who Masked
PARTICIPANT, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 14, 2010

First Posted

January 15, 2010

Study Start

June 1, 2010

Primary Completion

June 1, 2016

Study Completion

February 1, 2020

Last Updated

May 28, 2021

Results First Posted

May 28, 2021

Record last verified: 2021-05

Locations