NCT00835068

Brief Summary

The primary objective of this observational study is to collect safety data on reformulated BeneFIX as prescribed in routine clinical practice conditions in France. The secondary objectives are to collect data on the clinical course of individuals treated with reformulated BeneFIX and on the ease of reformulated BeneFIX.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
58

participants targeted

Target at P25-P50 for all trials

Timeline
Completed

Started Jan 2009

Longer than P75 for all trials

Geographic Reach
1 country

17 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

January 1, 2009

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

February 2, 2009

Completed
1 day until next milestone

First Posted

Study publicly available on registry

February 3, 2009

Completed
4.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2013

Completed
12 months until next milestone

Results Posted

Study results publicly available

September 17, 2014

Completed
Last Updated

September 17, 2014

Status Verified

September 1, 2014

Enrollment Period

4.8 years

First QC Date

February 2, 2009

Results QC Date

September 11, 2014

Last Update Submit

September 11, 2014

Conditions

Keywords

Hemophilia Bobservationalpost marketing study

Outcome Measures

Primary Outcomes (3)

  • Number of Participants With Treatment-Related Adverse Events (AEs) and Serious Adverse Events (SAEs) Prior to Safety Amendment

    A treatment-related AE was any untoward medical occurrence attributed to study drug in a participant who received study drug. An SAE was an AE resulting in any of the following outcomes or deemed significant for any other reason: death; initial or prolonged inpatient hospitalization; life-threatening experience (immediate risk of dying); persistent or significant disability/incapacity; congenital anomaly. AEs included SAEs as well as non-serious AEs which occurred prior to safety amendment. Prior to safety amendment, only AEs/SAEs deemed related to BeneFIX as per participating physician were collected.

    Baseline up to Year 3.5

  • Number of Participants With Adverse Events (AEs) and Serious Adverse Events (SAEs) by Relationship After Safety Amendment

    AE was any untoward medical occurrence in a participant who received study drug without regard to possibility of causal relationship. An SAE was an AE resulting in any of the following outcomes or deemed significant for any other reason: death; initial or prolonged inpatient hospitalization; life-threatening experience (immediate risk of dying); persistent or significant disability/incapacity; congenital anomaly. A treatment-related AE was any untoward medical occurrence attributed to study drug in a participant who received study drug as per participating physician. AEs included SAEs as well as non-serious AEs which occurred after the safety amendment. After the safety amendment, all AEs/SAEs were collected irrespective of their relationship to BeneFIX.

    Year 3.5 up to 4.75

  • Number of Participants With Events of Special Interest

    Events of special interest included allergic reactions, red blood cell (RBC) agglutination phenomena, lack of efficacy/low recovery, thrombotic events and onset of factor IX (FIX) inhibitor. Participants may be represented in more than 1 category.

    Baseline up to Year 4.75

Secondary Outcomes (7)

  • Number of Bleeding Episodes

    Baseline up to Year 4.75

  • Number of Bleeding Episodes Requiring Treatment by Injection

    Baseline up to Year 4.75

  • Total Consumption of BeneFIX

    Baseline up to Year 4.75

  • Subjective Assessment of Efficacy by Participant

    Baseline up to Year 4.75

  • Dose Per Injection of BeneFIX

    Baseline up to Year 4.75

  • +2 more secondary outcomes

Study Arms (1)

BeneFIX

Other: No intervention

Interventions

As it is a non interventional study, patient receives his usual treatment (BeneFIX) as determined by the physician

BeneFIX

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)
Sampling MethodNon-Probability Sample
Study Population

Hemophilia B patients already receiving or starting treatment with reformulated BeneFIX

You may qualify if:

  • Subjects with Hemophilia B already receiving or starting treatment with reformulated BeneFIX.
  • Subjects who have dated and signed the informed consent form.

You may not qualify if:

  • Ongoing treatment of Hemophilia B by a product other than reformulated BeneFIX.
  • Participation in the European prospective registry of patients with Hemophilia B treated with BeneFIX (Wyeth protocol 3090A-101039).

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (17)

Pfizer Investigational Site

Chamberry, Cedex, 73011, France

Location

Pfizer Investigational Site

Le Chesnay, Cedex, 78157, France

Location

Pfizer Investigational Site

Caen, 14033, France

Location

Pfizer Investigational Site

Clermont-Ferrand, 63003, France

Location

Pfizer Investigational Site

Dijon, 21070, France

Location

Pfizer Investigational Site

leKremlin-Bicetre, 94275, France

Location

Pfizer Investigational Site

Lyon, 69003, France

Location

Pfizer Investigational Site

Marseille, 13385, France

Location

Pfizer Investigational Site

Montmorency, 95160, France

Location

Pfizer Investigational Site

Montpellier, 34 34295, France

Location

Pfizer Investigational Site

Nantes, 44093, France

Location

Pfizer Investigational Site

Paris, 75014, France

Location

Pfizer Investigational Site

Paris, F-75015, France

Location

Pfizer Investigational Site

Rouen, 76031, France

Location

Pfizer Investigational Site

Saint-Priest-en-Jarez, 42277, France

Location

Pfizer Investigational Site

Tours, 37044, France

Location

Pfizer Investigational Site

Vandœuvre-lès-Nancy, 54511, France

Location

Related Links

MeSH Terms

Conditions

Hemophilia B

Condition Hierarchy (Ancestors)

Blood Coagulation Disorders, InheritedBlood Coagulation DisordersHematologic DiseasesHemic and Lymphatic DiseasesCoagulation Protein DisordersHemorrhagic DisordersGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesGenetic Diseases, X-Linked

Results Point of Contact

Title
Pfizer ClinicalTrials.gov Call Center
Organization
Pfizer, Inc.

Study Officials

  • Pfizer CT.gov Call Center

    Pfizer

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
observational
Observational Model
COHORT
Time Perspective
PROSPECTIVE
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 2, 2009

First Posted

February 3, 2009

Study Start

January 1, 2009

Primary Completion

October 1, 2013

Study Completion

October 1, 2013

Last Updated

September 17, 2014

Results First Posted

September 17, 2014

Record last verified: 2014-09

Locations