NCT00813527

Brief Summary

The purpose of this study is to compare changes in cholesterol levels in patients with elevated blood cholesterol with administration of lapaquistat acetate, once daily (QD), and fenofibrate.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
213

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started Feb 2006

Shorter than P25 for phase_2

Geographic Reach
2 countries

36 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

February 1, 2006

Completed
11 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2007

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2007

Completed
2 years until next milestone

First Submitted

Initial submission to the registry

December 19, 2008

Completed
4 days until next milestone

First Posted

Study publicly available on registry

December 23, 2008

Completed
Last Updated

May 24, 2012

Status Verified

May 1, 2012

Enrollment Period

11 months

First QC Date

December 19, 2008

Last Update Submit

May 23, 2012

Conditions

Keywords

Drug TherapyLipid Metabolism DisordersHyperlipidemiasHypercholesterolemiaHypertriglyceridemia

Outcome Measures

Primary Outcomes (1)

  • Percent change from Baseline in direct fasting plasma low-density lipoprotein cholesterol.

    Week 12 or Final Visit.

Secondary Outcomes (11)

  • Change from baseline in calculated low-density lipoprotein cholesterol.

    Week 12 or Final Visit.

  • Change from baseline in non- high-density lipoprotein cholesterol.

    Week 12 or Final Visit.

  • Change from baseline in total cholesterol.

    Week 12 or Final Visit.

  • Change from baseline in apolipoprotein B.

    Week 12 or Final Visit.

  • Change from baseline in triglycerides.

    Week 12 or Final Visit.

  • +6 more secondary outcomes

Study Arms (2)

Lapaquistat Acetate 100 mg QD + Fenofibrate 145 mg QD

EXPERIMENTAL
Drug: Lapaquistat acetate and fenofibrate

Fenofibrate 145 mg QD

ACTIVE COMPARATOR
Drug: Fenofibrate

Interventions

Lapaquistat acetate 100 mg, tablets, orally, once daily and fenofibrate 145 mg, tablets, orally, once daily for up to 12 weeks.

Also known as: Lapaquistat, TAK-475
Lapaquistat Acetate 100 mg QD + Fenofibrate 145 mg QD

Lapaquistat acetate placebo-matching tablets, orally, once daily and fenofibrate 145 mg, tablets, orally, once daily for up to 12 weeks.

Also known as: Tricor, Trilipix
Fenofibrate 145 mg QD

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Women of childbearing potential must not be pregnant as determined by a negative serum human chorionic gonadotropin, not lactating, not planning on becoming pregnant between Screening and 30 days following the last dose of study medication, and agreed to use acceptable forms of contraception during the study.
  • Prior to Randomization, must have a mean low density lipoprotein cholesterol greater than or equal to 100 mg/dL (2.59 mmol/L) for 2 consecutive samples. The difference between the two individual low density lipoprotein cholesterol values not to exceed 15% of the higher value.
  • Prior to Randomization, must have mean triglycerides greater than or equal to 150 and less than or equal to 600 mg/dL (1.70 and 6.78 mmol/L, respectively) for 2 consecutive samples. The upper value for either triglycerides sample must have been less than or equal to 650 mg/dL (7.35 mmol/L).
  • Clinical laboratory evaluations (including clinical chemistry \[fasted for at least 10 hours\], hematology and urinalysis) within the reference range for the testing laboratory unless results deemed not clinically significant or considered within normal limits for this subject by the investigator or the sponsor.
  • Willing and able to continue to comply with a standardized low cholesterol diet.

You may not qualify if:

  • Alanine aminotransferase or aspartate aminotransferase level of greater than 1.5 times the upper limit of normal, active liver disease or jaundice.
  • Serum creatinine greater than 1.5 mg/dL (133 μmol/L).
  • Creatine phosphokinase greater than 3 times the upper limit of normal.
  • Diabetes with a hemoglobin A1c greater than 8 % at Visit 1.
  • Previous history of cancer in remission for less than 5 years prior to the first dose of study medication. Does not include those subjects with basal cell or stage I squamous cell carcinoma of the skin.
  • An endocrine disorder, such as Cushing's syndrome, hyperthyroidism, or inappropriately treated hypothyroidism, affecting lipid metabolism. Subjects with hypothyroidism on appropriate replacement therapy (defined as stable thyroid hormone replacement therapy at least 3 months prior to Visit 1 and thyrotropin levels less than 1.5 times the upper limit of normal) are eligible for enrollment. If thyrotropin is greater than 1.5 times upper limit of normal, a free thyroxine level is to be determined. If the free thyroxine is within normal limits for that subject, the subject may continue in the study.
  • History of myocardial infarction, unstable angina, transient ischemic attacks, cerebrovascular accident, percutaneous coronary intervention, coronary or peripheral arterial surgery (bypass graft surgery) in the 6 months prior to Visit 1.
  • Positive hepatitis B surface antigen, or hepatitis C virus antibody, as determined by medical history and/or subject's verbal report.
  • Positive human immunodeficiency virus status or is taking anti-retroviral medications, as determined by medical history and/or subject's verbal report.
  • Unable or unwilling to discontinue excluded medications or to continue stable doses of "stable dose" medications or required treatment with any excluded medication during the study.
  • Exposure to TAK-475 in other studies or currently is participating in another investigational study or has participated in an investigational study within the past 30 days or, for drugs with a long half-life, within a period of less than 5 times the drug's halflife.
  • Known hypersensitivity or history of adverse reaction to any fibrate.
  • History or presence of clinically significant food allergy that would prevent adherence to the therapeutic lifestyle change (or equivalent) diet.
  • Known homozygous familial hypercholesterolemia or known Type III hyperlipoproteinemia (familial dysbetalipoproteinemia).
  • Active cholecystitis or known cholelithiasis (a fibrate risk factor).
  • +8 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (36)

Unknown Facility

Huntsville, Alabama, United States

Location

Unknown Facility

Sierra Vista, Arizona, United States

Location

Unknown Facility

Beverly Hills, California, United States

Location

Unknown Facility

Long Beach, California, United States

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Unknown Facility

Spring Valley, California, United States

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Unknown Facility

Colorado Springs, Colorado, United States

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Unknown Facility

Golden, Colorado, United States

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Unknown Facility

Waterbury, Connecticut, United States

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Unknown Facility

Jacksonville, Florida, United States

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Unknown Facility

Kissimmee, Florida, United States

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Unknown Facility

Miami, Florida, United States

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Unknown Facility

Ocala, Florida, United States

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Unknown Facility

Pembroke Pines, Florida, United States

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Unknown Facility

Pinellas Park, Florida, United States

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Unknown Facility

West Palm Beach, Florida, United States

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Unknown Facility

Warner Robins, Georgia, United States

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Unknown Facility

Chicago, Illinois, United States

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Unknown Facility

Peoria, Illinois, United States

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Unknown Facility

Indianapolis, Indiana, United States

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Wichita, Kansas, United States

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Edina, Minnesota, United States

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St Louis, Missouri, United States

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Raleigh, North Carolina, United States

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Winston-Salem, North Carolina, United States

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Cincinnati, Ohio, United States

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Columbus, Ohio, United States

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Hillsboro, Oregon, United States

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Beaver, Pennsylvania, United States

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Unknown Facility

Goose Creek, South Carolina, United States

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Nashville, Tennessee, United States

Location

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Norfolk, Virginia, United States

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Richmond, Virginia, United States

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Unknown Facility

Coquitlam, British Columbia, Canada

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Unknown Facility

Victoria, British Columbia, Canada

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Unknown Facility

London, Ontario, Canada

Location

Unknown Facility

Toronto, Ontario, Canada

Location

Related Publications (1)

  • Stein EA, Bays H, O'Brien D, Pedicano J, Piper E, Spezzi A. Lapaquistat acetate: development of a squalene synthase inhibitor for the treatment of hypercholesterolemia. Circulation. 2011 May 10;123(18):1974-85. doi: 10.1161/CIRCULATIONAHA.110.975284. Epub 2011 Apr 25.

MeSH Terms

Conditions

HyperlipidemiasLipid Metabolism DisordersHypercholesterolemiaHypertriglyceridemia

Interventions

1-((1-(3-acetoxy-2,2-dimethylpropyl)-7-chloro-5-(2,3-dimethoxyphenyl)-2-oxo-1,2,3,5-tetrahydro-4,1-benzoxazepin-3-yl)acetyl)piperidine-4-acetic acidFenofibrate

Condition Hierarchy (Ancestors)

DyslipidemiasMetabolic DiseasesNutritional and Metabolic Diseases

Intervention Hierarchy (Ancestors)

Fibric AcidsIsobutyratesButyratesAcids, AcyclicCarboxylic AcidsOrganic ChemicalsPhenyl EthersEthersBenzophenonesBenzene DerivativesHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsPhenolsKetones

Study Officials

  • Senior Medical Director

    Takeda

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 19, 2008

First Posted

December 23, 2008

Study Start

February 1, 2006

Primary Completion

January 1, 2007

Study Completion

January 1, 2007

Last Updated

May 24, 2012

Record last verified: 2012-05

Locations