NCT00788827

Brief Summary

This is a phase I study to assess the safety and tolerability of infusing expanded stem cells into the pancreas of patients with type I diabetes and a successful renal transplant. The stem cells used in this study occur naturally in the body and are collected from each recipient by a procedure called leukapheresis. The cells are then expanded and differentiated into insulin-like cells in a sterile suite before being injected into the body or tail of the pancreas of the recipient.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
7

participants targeted

Target at below P25 for phase_1

Timeline
Completed

Started Nov 2008

Longer than P75 for phase_1

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

November 1, 2008

Completed
9 days until next milestone

First Submitted

Initial submission to the registry

November 10, 2008

Completed
1 day until next milestone

First Posted

Study publicly available on registry

November 11, 2008

Completed
4.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2013

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2013

Completed
6.6 years until next milestone

Results Posted

Study results publicly available

November 18, 2019

Completed
Last Updated

November 18, 2019

Status Verified

October 1, 2019

Enrollment Period

4.5 years

First QC Date

November 10, 2008

Results QC Date

July 26, 2019

Last Update Submit

October 28, 2019

Conditions

Keywords

diabetes type Idiabetes type 2renal transplantstem cellssuccessful renal transplant

Outcome Measures

Primary Outcomes (1)

  • Number of Participants Who Experienced Adverse Events

    Safety will be evaluated in terms of adverse events graded according to CTCTAE toxicity criteria and laboratory test results. All adverse events will also be graded for relationship to treatment and as expected and unexpected.

    14 days

Secondary Outcomes (4)

  • Hba1C Data of Pre and Post Stem Cell Infusion

    12 weeks

  • Insulin Level

    12 weeks

  • Amylase Level

    12 weeks

  • Serum Creatinine

    12 weeks

Study Arms (1)

Autologous CD34+ stem cells

EXPERIMENTAL

Up to 5 x 10 log 8 of autologous stem cells on a single occasion

Biological: Autologous CD34+ stem cells

Interventions

Up to 5 x 10 log 8 of autologous stem cells on a single occasion

Autologous CD34+ stem cells

Eligibility Criteria

Age16 Years - 65 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Male or female patients aged from 16 to 65 years of age
  • Patient with Type I or Type 2 diabetes mellitus plus:
  • Successful previous kidney transplant.
  • Good kidney allograft function /no episodes of rejection for at least one year post-transplant
  • Not taking steroids as part of standard immuno-suppression
  • Has a WHO performance score of less than 2
  • Has a life expectancy of at least 3 months
  • Ability to give written consent
  • Women of childbearing potential may be included, but must use a reliable and appropriate contraceptive method

You may not qualify if:

  • Patients below the age of 16 or above the age of 65 years
  • Patients with chronic pancreatitis and poor exocrine pancreatic function
  • Pregnant or lactating women
  • Patients with recent recurrent GI bleeding or spontaneous bacterial peritonitis
  • Patients with evidence of HIV or other life threatening infection
  • Patients unable to give written consent
  • Patients with a history of hypersensitivity to G-CSF
  • Patients who have been included in any other clinical trial within the previous month

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Imperial College NHS Healthcare Trust, Hammersmith Hospital

London, W12 0HS, United Kingdom

Location

MeSH Terms

Conditions

Diabetes Mellitus, Type 1Diabetes Mellitus, Type 2

Condition Hierarchy (Ancestors)

Diabetes MellitusGlucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System DiseasesAutoimmune DiseasesImmune System Diseases

Results Point of Contact

Title
Professor Charles Pusey
Organization
Imperial College London

Study Officials

  • Charles Pusey, MD

    Imperial College London

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
Yes

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Model Details: Autologous stem cells
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

November 10, 2008

First Posted

November 11, 2008

Study Start

November 1, 2008

Primary Completion

May 1, 2013

Study Completion

May 1, 2013

Last Updated

November 18, 2019

Results First Posted

November 18, 2019

Record last verified: 2019-10

Data Sharing

IPD Sharing
Will not share

Locations