NCT00783718

Brief Summary

The primary purpose of this study was to determine the effect of vedolizumab induction treatment on clinical response at 6 weeks and to determine the effect of vedolizumab maintenance treatment on clinical remission at 52 weeks.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
895

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Jan 2009

Typical duration for phase_3

Geographic Reach
3 countries

105 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

October 31, 2008

Completed
3 days until next milestone

First Posted

Study publicly available on registry

November 3, 2008

Completed
2 months until next milestone

Study Start

First participant enrolled

January 1, 2009

Completed
2.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2011

Completed
3 months until next milestone

Study Completion

Last participant's last visit for all outcomes

March 1, 2012

Completed
2.4 years until next milestone

Results Posted

Study results publicly available

July 18, 2014

Completed
Last Updated

July 18, 2014

Status Verified

June 1, 2014

Enrollment Period

2.9 years

First QC Date

October 31, 2008

Results QC Date

June 19, 2014

Last Update Submit

June 19, 2014

Conditions

Outcome Measures

Primary Outcomes (2)

  • Induction Phase: Percentage of Participants With a Clinical Response at Week 6

    Clinical response is defined as a reduction in complete Mayo score of ≥ 3 points and ≥ 30% from Baseline with an accompanying decrease in rectal bleeding subscore of ≥ 1 point or absolute rectal bleeding subscore of ≤ 1 point. The Mayo Score is a standard assessment tool to measure ulcerative colitis disease activity in clinical trials. The index consists of 4 components: two that are patient reported (rectal bleeding and stool frequency), a global assessment by the physician, and an endoscopic subscore. Each component is scored on a scale from 0 to 3 and the complete score ranges from 1 to 12 (higher scores indicate greater disease activity). All participants who prematurely discontinued for any reason were considered as not achieving clinical response.

    Baseline and Week 6

  • Maintenance Phase: Percentage of Participants in Clinical Remission at Week 52

    Clinical Remission is defined as a complete Mayo score of ≤ 2 points and no individual subscore \> 1 point. The Mayo Score is a standard assessment tool to measure ulcerative colitis disease activity in clinical trials. The index consists of 4 components: two that are patient reported (rectal bleeding and stool frequency), a global assessment by the physician, and an endoscopic subscore. Each component is scored on a scale from 0 to 3 and the complete score ranges from 1 to 12 (higher scores indicate greater disease activity). All participants who prematurely discontinued for any reason were considered as not achieving clinical remission.

    Week 52

Secondary Outcomes (6)

  • Induction Phase: Percentage of Participants in Clinical Remission at Week 6

    Week 6

  • Induction Phase: Percentage of Participants With Mucosal Healing at Week 6

    Week 6

  • Maintenance Phase: Percentage of Participants With Durable Clinical Response

    Baseline, Week 6 and Week 52

  • Maintenance Phase: Percentage of Participants With Mucosal Healing at Week 52

    Week 52

  • Maintenance Phase: Percentage of Participants With Durable Clinical Remission

    Week 6 and Week 52

  • +1 more secondary outcomes

Study Arms (2)

Vedolizumab

EXPERIMENTAL

In the Induction Phase participants received vedolizumab 300 mg, administered by intravenous infusion at Week 0 and Week 2 (Days 1 and 15). In the Maintenance Phase, participants who demonstrated a clinical response at Week 6 according to protocol-specified criteria were randomized in a 1:1:1 ratio to double-blind treatment with vedolizumab administered every 4 weeks, vedolizumab administered every 8 weeks, or placebo for up to Week 50. Participants who did not demonstrate response at Week 6 of the Induction Phase continued treatment with vedolizumab, administered every 4 weeks during the Maintenance Phase.

Drug: vedolizumab

Placebo

PLACEBO COMPARATOR

In the Induction Phase participants received placebo intravenous infusion at Week 0 and Week 2 (Days 1 and 15). Participants continued to receive placebo during the Maintenance Phase, regardless of treatment response during Induction.

Other: Placebo

Interventions

Vedolizumab for intravenous infusion

Also known as: Entyvio, MLN0002, MLN02, LDP-02
Vedolizumab
PlaceboOTHER

Placebo intravenous infusion

Placebo

Eligibility Criteria

Age18 Years - 80 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Diagnosis of moderately to severely active ulcerative colitis
  • Demonstrated, over the previous 5 year period, an inadequate response to, loss of response to, or intolerance at least 1 of the following agents:
  • Immunomodulators
  • Tumor necrosis factor-alpha (TNFα) antagonists
  • Corticosteroids
  • May be receiving a therapeutic dose of conventional therapies for inflammatory bowel disease (IBD) as defined by the protocol

You may not qualify if:

  • Evidence of abdominal abscess at the initial screening visit
  • Extensive colonic resection, subtotal or total colectomy
  • Ileostomy, colostomy, or known fixed symptomatic stenosis of the intestine
  • Have received non permitted IBD therapies within either 30 or 60 days, depending on the medication, as stated in the protocol
  • Chronic hepatitis B or C infection
  • Active or latent tuberculosis

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (105)

University of Alabama at Birmingham

Birmingham, Alabama, 35233, United States

Location

Apex Clinical Trials

Birmingham, Alabama, 35234, United States

Location

Cedars-Sinai Medical Center

Los Angeles, California, 90048, United States

Location

Gastrointestinal Bioscience

Los Angeles, California, 90067, United States

Location

Paramount Medical Specialty

Montebello, California, 90640, United States

Location

Capital Gastroenterology Consultants Medical Group

Sacramento, California, 95815, United States

Location

Clinical Applications Laboratories Inc.

San Diego, California, 92103, United States

Location

Desta Digestive Disease Medical Center

San Diego, California, 92114, United States

Location

University of Colorado Health Sciences Center

Aurora, Colorado, 80045, United States

Location

Gastroenterology of the Rockies

Lafayette, Colorado, 80026, United States

Location

Rocky Mountain Gastroenterology Associates P.L.L.C.

Lakewood, Colorado, 80215, United States

Location

Arapahoe Gastroenterology Associates P.C

Littleton, Colorado, 80120, United States

Location

South Denver Gastroenterology

Lone Tree, Colorado, 80124, United States

Location

Lynn Institute of Pueblo

Pueblo, Colorado, 81007, United States

Location

Gastroenterology Center of Connecticut, P.C.

Hamden, Connecticut, 06518, United States

Location

University of Florida

Gainesville, Florida, 32608, United States

Location

University of Florida, Jacksonville

Jacksonville, Florida, 32209, United States

Location

East Coast Institute for Research

Jacksonville, Florida, 32223, United States

Location

Borland-Groover Clinic

Jacksonville, Florida, 32256, United States

Location

Osler Clinical Research

Melbourne, Florida, 32901, United States

Location

University of Miami Miller School of Medicine

Miami, Florida, 33136, United States

Location

United Medical Research Institute

New Smyrna Beach, Florida, 32168, United States

Location

Compass Research LLC

Orlando, Florida, 32806, United States

Location

Internal Medicine Specialists

Orlando, Florida, 32806, United States

Location

University of South Florida

Tampa, Florida, 33606, United States

Location

West Wind'r Research & Development, LLC

Tampa, Florida, 33607, United States

Location

Shafran Gastroenterology Center

Winter Park, Florida, 32789, United States

Location

Atlanta Gastroenterology Associates

Atlanta, Georgia, 30342, United States

Location

Southeast Regional Research Group

Columbus, Georgia, 31904, United States

Location

Atlanta Center for Gastroenterology, P.C.

Decatur, Georgia, 30033, United States

Location

Gastroenterology Associates of Central Georgia

Macon, Georgia, 31201, United States

Location

Digestive Research Associates

Newnan, Georgia, 30263, United States

Location

St. Joseph's/Candler Health System

Savannah, Georgia, 31405, United States

Location

DLW Research System

Snellville, Georgia, 30039, United States

Location

Carle Clinic Association P.C.

Urbana, Illinois, 61801, United States

Location

Digestive & Liver Consultants

Clive, Iowa, 50325, United States

Location

Iowa Digestive Disease Center

Clive, Iowa, 50325, United States

Location

University Of Kansas

Kansas City, Kansas, 66160, United States

Location

Cotton O'Neil Digestive Health Center

Topeka, Kansas, 66606, United States

Location

University of Kentucky Medical Center

Lexington, Kentucky, 40536, United States

Location

University Of Louisville

Louisville, Kentucky, 40202, United States

Location

Gastroenterology Associates

Baton Rouge, Louisiana, 70809, United States

Location

University of Maryland Medical Group

Baltimore, Maryland, 21201, United States

Location

Metropolitan Gastroenterology Group, P.C.

Chevy Chase, Maryland, 20815, United States

Location

Shah Associates

Prince Frederick, Maryland, 20678, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

Boston Medical Center

Boston, Massachusetts, 02118, United States

Location

The Center for Clinical Studies

Dearborn, Michigan, 48124, United States

Location

Center for Digestive Health

Troy, Michigan, 48098, United States

Location

Gastroenterology Associates of Western Michigan, P.L.C.

Wyoming, Michigan, 49519, United States

Location

Minnesota Gastroenterology, P.A.

Plymouth, Minnesota, 55486, United States

Location

Mayo Clinic

Rochester, Minnesota, 55905, United States

Location

Truman Medical Center

Kansas City, Missouri, 64108, United States

Location

Center for Digestive and Liver Diseases, Inc.

Mexico, Missouri, 65265, United States

Location

Washington University

St Louis, Missouri, 63110, United States

Location

St. Louis Center for Clinical Research

St Louis, Missouri, 63128, United States

Location

Dartmouth-Hitchcock Medical Center

Lebanon, New Hampshire, 03756, United States

Location

Affiliates in Gastroenterology PA

Morristown, New Jersey, 07960, United States

Location

University of Medicine and Dentistry of New Jersey-NJMS

New Brunswick, New Jersey, 08903, United States

Location

The Gastroenterology Group of South Jersey

Vineland, New Jersey, 08360, United States

Location

Hepatobiliary Associates of New York

Bayside, New York, 11358, United States

Location

Digestive Health Physician

Cheektowaga, New York, 14225, United States

Location

Long Island Clinical Research Associates

Great Neck, New York, 11021, United States

Location

Long Island Gastroenterology Group, P.C.

Merrick, New York, 11566, United States

Location

New York Presbyterian Hospital

New York, New York, 10021, United States

Location

Present Chapman Marion Steinlauf MD PC

New York, New York, 10028, United States

Location

Kim, Chung MD (Private Practice)

Pittsford, New York, 14534, United States

Location

University of Rochester

Rochester, New York, 14642, United States

Location

Long Island Digestive Disease Consultants

Setauket, New York, 11733, United States

Location

SUNY Stony Brook University Medical Center

Stony Brook, New York, 11794, United States

Location

Syracuse Gastroenterological Associates

Syracuse, New York, 13210, United States

Location

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, 27599, United States

Location

Charlotte Gastroentology and Hepatology, P.L.L.C

Charlotte, North Carolina, 28207, United States

Location

Northwest Piedmont Clinical Research, Inc.

Elkin, North Carolina, 28621, United States

Location

Burke Research Associates

Morganton, North Carolina, 28655, United States

Location

Consultants for Clinical Research Inc.

Cincinnati, Ohio, 45219, United States

Location

Dayton Science Institute

Dayton, Ohio, 45415, United States

Location

Options Health Research

Tulsa, Oklahoma, 74104, United States

Location

The Oregon Clinic-West Hills Gastroenterology

Portland, Oregon, 97225, United States

Location

University of Pittsburgh Medical Center - Cancer Centers

Pittsburgh, Pennsylvania, 15213, United States

Location

Medical University Of SC CAR

Charleston, South Carolina, 29425, United States

Location

Gastroenterology Center of the MidSouth, PC

Germantown, Tennessee, 38138, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232, United States

Location

Austin Gastroenterology, PA

Austin, Texas, 78705, United States

Location

Bayou City Research, Ltd.

Houston, Texas, 77024, United States

Location

Baylor College Of Medicine

Houston, Texas, 77030, United States

Location

Gastroenterology Consultants

Houston, Texas, 77034, United States

Location

Jacon Medical Research Associates

Houston, Texas, 77090, United States

Location

Digestive Health Center

Pasadena, Texas, 77504, United States

Location

Alamo Medical Research

San Antonio, Texas, 78215, United States

Location

Gastroenterology Clinic of San Antonio

San Antonio, Texas, 78229, United States

Location

Stone Oak Research Foundation

San Antonio, Texas, 78258, United States

Location

Digestive Health Specialists of Tyler

Tyler, Texas, 75701, United States

Location

Granite Peaks Gastroenterology

Sandy City, Utah, 84094, United States

Location

University of Virginia Health System

Charlottesville, Virginia, 22908, United States

Location

Gastroenterology Associates of Northern Virginia

Fairfax, Virginia, 22031, United States

Location

Digestive and Liver Disease Specialist Ltd

Norfolk, Virginia, 23502, United States

Location

Hunter Holmes McGuire VA Medical Center

Richmond, Virginia, 23249, United States

Location

Puget Sound Medical Research

Edmonds, Washington, 98026, United States

Location

Pharmaseek, LLC

Madison, Wisconsin, 53717, United States

Location

Wisconsin Center for Advanced Research

Milwaukee, Wisconsin, 53215, United States

Location

Medical College Of Wisconsin

Milwaukee, Wisconsin, 53226, United States

Location

Zeidler Ledcor Center-Univerisity of Alberta

Edmonton, Alberta, T6G2X8, Canada

Location

Royal University Hospital

Saskatoon, Saskatchewan, S7N 0W8, Canada

Location

Pharmaseek, LLC

Ponce, 716, Puerto Rico

Location

Related Publications (14)

  • Feagan BG, Rutgeerts P, Sands BE, Hanauer S, Colombel JF, Sandborn WJ, Van Assche G, Axler J, Kim HJ, Danese S, Fox I, Milch C, Sankoh S, Wyant T, Xu J, Parikh A; GEMINI 1 Study Group. Vedolizumab as induction and maintenance therapy for ulcerative colitis. N Engl J Med. 2013 Aug 22;369(8):699-710. doi: 10.1056/NEJMoa1215734.

  • Dulai PS, Feagan BG, Sands BE, Chen J, Lasch K, Lirio RA. Prognostic Value of Fecal Calprotectin to Inform Treat-to-Target Monitoring in Ulcerative Colitis. Clin Gastroenterol Hepatol. 2023 Feb;21(2):456-466.e7. doi: 10.1016/j.cgh.2022.07.027. Epub 2022 Aug 4.

  • Wyant T, Yang L, Rosario M. Comparison of the ELISA and ECL Assay for Vedolizumab Anti-drug Antibodies: Assessing the Impact on Pharmacokinetics and Safety Outcomes of the Phase 3 GEMINI Trials. AAPS J. 2020 Nov 16;23(1):3. doi: 10.1208/s12248-020-00518-0.

  • Okamoto H, Dirks NL, Rosario M, Hori T, Hibi T. Population pharmacokinetics of vedolizumab in Asian and non-Asian patients with ulcerative colitis and Crohn's disease. Intest Res. 2021 Jan;19(1):95-105. doi: 10.5217/ir.2019.09167. Epub 2020 Jul 10.

  • Loftus EV Jr, Sands BE, Colombel JF, Dotan I, Khalid JM, Tudor D, Geransar P. Sustained Corticosteroid-Free Clinical Remission During Vedolizumab Maintenance Therapy in Patients with Ulcerative Colitis on Stable Concomitant Corticosteroids During Induction Therapy: A Post Hoc Analysis of GEMINI 1. Clin Exp Gastroenterol. 2020 Jun 11;13:211-220. doi: 10.2147/CEG.S248597. eCollection 2020.

  • Dulai PS, Singh S, Vande Casteele N, Meserve J, Winters A, Chablaney S, Aniwan S, Shashi P, Kochhar G, Weiss A, Koliani-Pace JL, Gao Y, Boland BS, Chang JT, Faleck D, Hirten R, Ungaro R, Lukin D, Sultan K, Hudesman D, Chang S, Bohm M, Varma S, Fischer M, Shmidt E, Swaminath A, Gupta N, Rosario M, Jairath V, Guizzetti L, Feagan BG, Siegel CA, Shen B, Kane S, Loftus EV Jr, Sandborn WJ, Sands BE, Colombel JF, Lasch K, Cao C. Development and Validation of Clinical Scoring Tool to Predict Outcomes of Treatment With Vedolizumab in Patients With Ulcerative Colitis. Clin Gastroenterol Hepatol. 2020 Dec;18(13):2952-2961.e8. doi: 10.1016/j.cgh.2020.02.010. Epub 2020 Feb 13.

  • Feagan BG, Schreiber S, Wolf DC, Axler JL, Kaviya A, James A, Curtis RI, Geransar P, Stallmach A, Ehehalt R, Bokemeyer B, Khalid JM, O'Byrne S. Sustained Clinical Remission With Vedolizumab in Patients With Moderate-to-Severe Ulcerative Colitis. Inflamm Bowel Dis. 2019 May 4;25(6):1028-1035. doi: 10.1093/ibd/izy323.

  • Sandborn WJ, Colombel JF, Panaccione R, Dulai PS, Rosario M, Cao C, Barocas M, Lasch K. Deep Remission With Vedolizumab in Patients With Moderately to Severely Active Ulcerative Colitis: A GEMINI 1 post hoc Analysis. J Crohns Colitis. 2019 Feb 1;13(2):172-181. doi: 10.1093/ecco-jcc/jjy149.

  • Feagan BG, Sandborn WJ, Colombel JF, Byrne SO, Khalid JM, Kempf C, Geransar P, Bhayat F, Rubin DT. Incidence of Arthritis/Arthralgia in Inflammatory Bowel Disease with Long-term Vedolizumab Treatment: Post Hoc Analyses of the GEMINI Trials. J Crohns Colitis. 2019 Jan 1;13(1):50-57. doi: 10.1093/ecco-jcc/jjy125.

  • Feagan BG, Lasch K, Lissoos T, Cao C, Wojtowicz AM, Khalid JM, Colombel JF. Rapid Response to Vedolizumab Therapy in Biologic-Naive Patients With Inflammatory Bowel Diseases. Clin Gastroenterol Hepatol. 2019 Jan;17(1):130-138.e7. doi: 10.1016/j.cgh.2018.05.026. Epub 2018 May 29.

  • Arijs I, De Hertogh G, Lemmens B, Van Lommel L, de Bruyn M, Vanhove W, Cleynen I, Machiels K, Ferrante M, Schuit F, Van Assche G, Rutgeerts P, Vermeire S. Effect of vedolizumab (anti-alpha4beta7-integrin) therapy on histological healing and mucosal gene expression in patients with UC. Gut. 2018 Jan;67(1):43-52. doi: 10.1136/gutjnl-2016-312293. Epub 2016 Oct 7.

  • Feagan BG, Rubin DT, Danese S, Vermeire S, Abhyankar B, Sankoh S, James A, Smyth M. Efficacy of Vedolizumab Induction and Maintenance Therapy in Patients With Ulcerative Colitis, Regardless of Prior Exposure to Tumor Necrosis Factor Antagonists. Clin Gastroenterol Hepatol. 2017 Feb;15(2):229-239.e5. doi: 10.1016/j.cgh.2016.08.044. Epub 2016 Sep 14.

  • Colombel JF, Sands BE, Rutgeerts P, Sandborn W, Danese S, D'Haens G, Panaccione R, Loftus EV Jr, Sankoh S, Fox I, Parikh A, Milch C, Abhyankar B, Feagan BG. The safety of vedolizumab for ulcerative colitis and Crohn's disease. Gut. 2017 May;66(5):839-851. doi: 10.1136/gutjnl-2015-311079. Epub 2016 Feb 18.

  • Rosario M, Dirks NL, Gastonguay MR, Fasanmade AA, Wyant T, Parikh A, Sandborn WJ, Feagan BG, Reinisch W, Fox I. Population pharmacokinetics-pharmacodynamics of vedolizumab in patients with ulcerative colitis and Crohn's disease. Aliment Pharmacol Ther. 2015 Jul;42(2):188-202. doi: 10.1111/apt.13243. Epub 2015 May 20.

MeSH Terms

Conditions

Colitis, Ulcerative

Interventions

vedolizumabLDP-02

Condition Hierarchy (Ancestors)

ColitisGastroenteritisGastrointestinal DiseasesDigestive System DiseasesInflammatory Bowel DiseasesColonic DiseasesIntestinal Diseases

Results Point of Contact

Title
Medical Director
Organization
Millennium Pharmaceuticals Inc

Study Officials

  • Medical Monitor

    Millennium Pharmaceuticals, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
TRIPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 31, 2008

First Posted

November 3, 2008

Study Start

January 1, 2009

Primary Completion

December 1, 2011

Study Completion

March 1, 2012

Last Updated

July 18, 2014

Results First Posted

July 18, 2014

Record last verified: 2014-06

Locations