NCT00751842

Brief Summary

The intended purpose of this study was to determine whether Diamyd (rhGAD65 formulated in alum) is effective in preserving the body's own insulin producing capacity in patients recently diagnosed with type 1 diabetes. Based on results from other clinical trials with the study drug it was judged unlikely this study would meet the intended primary or secondary efficacy endpoints. Therefore the primary focus of this study was changed to ensure that safety data was available for at least 6 months following the last dose of active study drug. Thereafter the study was terminated.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
331

participants targeted

Target at P50-P75 for phase_3

Timeline
Completed

Started Sep 2008

Typical duration for phase_3

Geographic Reach
1 country

43 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2008

Completed
10 days until next milestone

First Submitted

Initial submission to the registry

September 11, 2008

Completed
1 day until next milestone

First Posted

Study publicly available on registry

September 12, 2008

Completed
3.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2012

Completed
4 months until next milestone

Study Completion

Last participant's last visit for all outcomes

July 1, 2012

Completed
Last Updated

October 10, 2012

Status Verified

October 1, 2012

Enrollment Period

3.5 years

First QC Date

September 11, 2008

Last Update Submit

October 9, 2012

Conditions

Keywords

DiabetesJuvenile DiabetesDiabetes type 1Autoimmune DiabetesInsulin dependent DiabetesType 1 diabetesType 1 diabetes mellitusDiamydrhGAD65GADGAD-alum

Outcome Measures

Primary Outcomes (1)

  • Meal Stimulated C-peptide (area under the curve)

    15 months

Secondary Outcomes (2)

  • HbA1c

    15 months

  • Insulin Dose

    15 months

Study Arms (3)

A

ACTIVE COMPARATOR

This arm will receive 2 subcutaneous injections with 20 µg Diamyd on days 1 and 30, i.e., 1 prime and 1 booster dose, followed by 2 additional single doses with Diamyd 20 µg on days 90 and 270.

Drug: rhGAD65

B

ACTIVE COMPARATOR

This arm will receive 2 subcutaneous injections with 20 µg Diamyd on days 1 and 30, i.e., 1 prime and 1 booster dose, followed by 2 additional single doses with placebo on days 90 and 270.

Drug: rhGAD65

C

PLACEBO COMPARATOR

This arm will receive 4 injections of placebo, 1 each on days 1, 30, 90 and 270.

Drug: Placebo

Interventions

Diamyd (rhGAD65) 20 µg injected subcutaneously at days 1, 30, 90 and 270.

A

Placebo injected subcutaneously at days 1, 30, 90 and 270.

C

Eligibility Criteria

Age10 Years - 20 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Insulin dependent type 1 diabetes mellitus diagnosed within the previous 3 months at time of screening
  • Fasting C-peptide level at time of screening above 0.1 nmol/L
  • Elevated GAD65 antibodies (GADA) at time of screening
  • Male and female patients between 10 and 20 years of age

You may not qualify if:

  • Treatment with immunosuppressants or any anti-diabetic medications other than insulin
  • A history of certain diseases or conditions (e.g. anemia, HIV, hepatitis, epilepsy, head trauma, neurological diseases or cerebrovascular accident, alcohol or drug abuse etc)
  • Treatment with any vaccine within 1 month prior to planned first Diamyd dose or planned treatment with vaccine up to 2 months after the last injection with Diamyd, excluding the influenza vaccine
  • Participation in other clinical trials with a new chemical entity within the previous 3 months
  • Pregnancy or planned pregnancy within 1 year after the last Diamyd dose
  • Presence of associated serious disease or condition which in the opinion of the investigator makes the patient non-eligible for the study

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (43)

University of Arizona

Tucson, Arizona, 85724, United States

Location

Arkansas Children's Hospital Research Institute

Little Rock, Arkansas, 72202, United States

Location

Alex Endocrine Associates

Rogers, Arkansas, 72758, United States

Location

Children's Hospital Orange County

Orange, California, 92868, United States

Location

Rady Children's Hospital

San Diego, California, 92123, United States

Location

Stanford University Medical Center

Stanford, California, 94305, United States

Location

Barbara Davis Center for Childhood Diabetes

Aurora, Colorado, 80045, United States

Location

Christina Care Research institute

Newark, Delaware, 19713, United States

Location

University of Florida

Gainsville, Florida, 32610, United States

Location

Nemours Children's Clinic

Jacksonville, Florida, 32207, United States

Location

Miami Children's Hospital Research Institute

Miami, Florida, 33155, United States

Location

University of South Florida

Tampa, Florida, 33606, United States

Location

Atlanta Diabetes Associates

Atlanta, Georgia, 30309, United States

Location

Rocky Mountain Diabetes and Osteoporosis Center

Idaho Falls, Idaho, 83404, United States

Location

University of Iowa Hospitals and Clinicals

Iowa City, Iowa, 52242, United States

Location

Mid America Diabetes Associates

Wichita, Kansas, 67211, United States

Location

University of Kentucky College of Medicine

Lexington, Kentucky, 40536, United States

Location

University of Louisville Research Foundation

Louisville, Kentucky, 40202, United States

Location

Children's Hospital

New Orleans, Louisiana, 70118, United States

Location

University of Maryland Medical Center

Baltimore, Maryland, 21201, United States

Location

Tufts Medical Center

Boston, Massachusetts, 02111, United States

Location

UMass Memorial Medical Center

Worcester, Massachusetts, 01655, United States

Location

University of Michigan Health System

Ann Arbor, Michigan, 48109, United States

Location

Alzohaili Medical Consultants

Dearborn, Michigan, 48126, United States

Location

The Children's Mercy Hospital

Kansas City, Missouri, 64108, United States

Location

St. Louis Children's Hospital

St Louis, Missouri, 63110, United States

Location

Creighton Diabetes Center

Omaha, Nebraska, 68131, United States

Location

Kathryn Eckert

Reno, Nevada, 89502, United States

Location

Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

Morristown Memorial Hospital

Morristown, New Jersey, 07962, United States

Location

Winthrop University Hospital

Mineola, New York, 11501, United States

Location

Naomi Berrie Diabetes Center of Columbia University

New York, New York, 10032, United States

Location

University of Rochester

Rochester, New York, 14642, United States

Location

SUNY Institute for Human Performance

Syracuse, New York, 13210, United States

Location

Children's Hospital Medical Center of Akron

Akron, Ohio, 44308, United States

Location

University of Oklahoma, Schustermann Center Clinic

Tulsa, Oklahoma, 74135, United States

Location

Children's Hospital of Pittsburgh of UPMC

Pittsburgh, Pennsylvania, 15224, United States

Location

Regional Medical Clinic - Endocrinology

Rapid City, South Dakota, 57701, United States

Location

LeBonheur Children's Medical Center

Memphis, Tennessee, 38103, United States

Location

Cook Children's Medical Center

Fort Worth, Texas, 76104, United States

Location

CHRISTUS Santa Rosa Children's Hospital

San Antonio, Texas, 78207, United States

Location

Virginia Commonwealth University

Richmond, Virginia, 23219, United States

Location

Benaroya Research Institute

Seattle, Washington, 98101, United States

Location

Related Publications (3)

  • Ludvigsson J, Faresjo M, Hjorth M, Axelsson S, Cheramy M, Pihl M, Vaarala O, Forsander G, Ivarsson S, Johansson C, Lindh A, Nilsson NO, Aman J, Ortqvist E, Zerhouni P, Casas R. GAD treatment and insulin secretion in recent-onset type 1 diabetes. N Engl J Med. 2008 Oct 30;359(18):1909-20. doi: 10.1056/NEJMoa0804328. Epub 2008 Oct 8.

    PMID: 18843118BACKGROUND
  • Ludvigsson J, Krisky D, Casas R, Battelino T, Castano L, Greening J, Kordonouri O, Otonkoski T, Pozzilli P, Robert JJ, Veeze HJ, Palmer J, Samuelsson U, Elding Larsson H, Aman J, Kardell G, Neiderud Helsingborg J, Lundstrom G, Albinsson E, Carlsson A, Nordvall M, Fors H, Arvidsson CG, Edvardson S, Hanas R, Larsson K, Rathsman B, Forsgren H, Desaix H, Forsander G, Nilsson NO, Akesson CG, Keskinen P, Veijola R, Talvitie T, Raile K, Kapellen T, Burger W, Neu A, Engelsberger I, Heidtmann B, Bechtold S, Leslie D, Chiarelli F, Cicognani A, Chiumello G, Cerutti F, Zuccotti GV, Gomez Gila A, Rica I, Barrio R, Clemente M, Lopez Garcia MJ, Rodriguez M, Gonzalez I, Lopez JP, Oyarzabal M, Reeser HM, Nuboer R, Stouthart P, Bratina N, Bratanic N, de Kerdanet M, Weill J, Ser N, Barat P, Bertrand AM, Carel JC, Reynaud R, Coutant R, Baron S. GAD65 antigen therapy in recently diagnosed type 1 diabetes mellitus. N Engl J Med. 2012 Feb 2;366(5):433-42. doi: 10.1056/NEJMoa1107096.

    PMID: 22296077BACKGROUND
  • Wherrett DK, Bundy B, Becker DJ, DiMeglio LA, Gitelman SE, Goland R, Gottlieb PA, Greenbaum CJ, Herold KC, Marks JB, Monzavi R, Moran A, Orban T, Palmer JP, Raskin P, Rodriguez H, Schatz D, Wilson DM, Krischer JP, Skyler JS; Type 1 Diabetes TrialNet GAD Study Group. Antigen-based therapy with glutamic acid decarboxylase (GAD) vaccine in patients with recent-onset type 1 diabetes: a randomised double-blind trial. Lancet. 2011 Jul 23;378(9788):319-27. doi: 10.1016/S0140-6736(11)60895-7. Epub 2011 Jun 27.

    PMID: 21714999BACKGROUND

MeSH Terms

Conditions

Diabetes Mellitus, Type 1Diabetes Mellitus

Condition Hierarchy (Ancestors)

Glucose Metabolism DisordersMetabolic DiseasesNutritional and Metabolic DiseasesEndocrine System DiseasesAutoimmune DiseasesImmune System Diseases

Study Officials

  • Jerry Palmer, Professor

    University of Washington

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

September 11, 2008

First Posted

September 12, 2008

Study Start

September 1, 2008

Primary Completion

March 1, 2012

Study Completion

July 1, 2012

Last Updated

October 10, 2012

Record last verified: 2012-10

Locations