NCT00741819

Brief Summary

This is a 24-month, multi-center, prospective, open-label, safety evaluation in PAH subjects following transition from a stable dose of inhaled iloprost (Ventavis). Subjects are to be evaluated for safety throughout the course of the study while secondary assessments will be conducted at Baseline, Week 6, Week 12, and Months 6, 12, 18 and 24 following initiation of treprostinil sodium.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
73

participants targeted

Target at P25-P50 for phase_4

Timeline
Completed

Started Sep 2008

Typical duration for phase_4

Geographic Reach
1 country

15 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

August 23, 2008

Completed
3 days until next milestone

First Posted

Study publicly available on registry

August 26, 2008

Completed
6 days until next milestone

Study Start

First participant enrolled

September 1, 2008

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

March 1, 2010

Completed
9 months until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2010

Completed
2.2 years until next milestone

Results Posted

Study results publicly available

February 20, 2013

Completed
Last Updated

February 20, 2013

Status Verified

January 1, 2013

Enrollment Period

1.5 years

First QC Date

August 23, 2008

Results QC Date

May 17, 2012

Last Update Submit

January 16, 2013

Conditions

Keywords

pulmonary arterial hypertensionPAHtreprostinil sodiuminhalationventavisiloprost

Outcome Measures

Primary Outcomes (1)

  • Number of Adverse Events

    Overall safety of transitioning from inhaled iloprost to inhaled treprostinil was assessed by type and frequency of adverse events.

    up to 24 months

Secondary Outcomes (7)

  • Six-minute Walk Distance (6MWD)

    Baseline and 12 weeks

  • Quality of Life (QoL) Assessment: Cambridge Pulmonary Hypertension Outcome Review (CAMPHOR)

    Baseline and 12 weeks

  • Treatment Satisfaction Questionnaire of Medication (TSQM)

    Baseline and 12 weeks

  • Patient Impression of Change

    Baseline and 12 weeks

  • N-terminal Prohormone of Brain Natriuretic Peptide (NT-proBNP)

    Baseline and Week 12

  • +2 more secondary outcomes

Study Arms (1)

Inhaled treprostinil

EXPERIMENTAL

Solution for oral inhalation treprostinil (0.6 mg/mL). Inhaled via an ultrasonic nebulizer which provides a dose of 6mcg of treprostinil per breath. Doses are titrated up to 12 breaths four times daily.

Drug: Inhaled treprostinil

Interventions

Also known as: Tyvaso
Inhaled treprostinil

Eligibility Criteria

Age18 Years - 75 Years
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Between 18 and 75 years of age
  • PAH diagnosis defined by following WHO Group I categories: idiopathic/familial, associated with unrepaired or repaired congenital systemic-to-pulmonary shunts (repaired \>/= 5 years), associated with collagen vascular disease, associated with HIV, associated with appetite suppressant/toxin use
  • Baseline six-minute walk distance (6MWD) \>/= 250 meters
  • Currently receiving Ventavis and be stable at current dose for 30 days prior to Baseline
  • If currently receiving other approved background therapy (i.e. endothelin receptor antagonist or phosphodiesterase-5-inhibitor or both) must be on stable dose for 30 days prior to Baseline
  • Previous testing (e.g. right heart catheterization, echocardiography) consistent with diagnosis of PAH

You may not qualify if:

  • Nursing or pregnant
  • History of uncontrolled sleep apnea, left-sided heart disease, or parenchymal lung disease
  • Use of investigational drug within 30 days of Baseline

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (15)

University of Alabama Birmingham

Birmingham, Alabama, 35294, United States

Location

UCSD Medical Center

La Jolla, California, 82037, United States

Location

Ronald Reagan UCLA Medical Center

Los Angeles, California, 90095, United States

Location

Kansas University Medical Center

Kansas City, Kansas, 66160, United States

Location

Long Island Jewish Medical Center - North Shore

New Hyde Park, New York, 11040, United States

Location

Beth Israel Medical Center

New York, New York, 10003-3314, United States

Location

Cornell University Medical Center

New York, New York, 10021, United States

Location

Columbia Presbyterian Medical Center

New York, New York, 10032, United States

Location

Mary M. Parkes Center for Asthma, Allergy and Pulmonary Care

Rochester, New York, 14623, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Ohio State University Medical Center

Columbus, Ohio, 43210, United States

Location

Allegheny General Hospital

Pittsburgh, Pennsylvania, 15212, United States

Location

University of Pittsburg Medical Center

Pittsburgh, Pennsylvania, 15213, United States

Location

Vanderbilt University Medical Center

Nashville, Tennessee, 37232, United States

Location

Baylor College of Medicine

Houston, Texas, 77030, United States

Location

MeSH Terms

Conditions

Pulmonary Arterial HypertensionRespiratory Aspiration

Interventions

treprostinil

Condition Hierarchy (Ancestors)

Hypertension, PulmonaryLung DiseasesRespiratory Tract DiseasesRespiration DisordersPathologic ProcessesPathological Conditions, Signs and Symptoms

Limitations and Caveats

Small, open-label study without comparison arm.

Results Point of Contact

Title
Inhaled Treprostinil Program Head
Organization
United Therpaeutics Corporation

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 4
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

August 23, 2008

First Posted

August 26, 2008

Study Start

September 1, 2008

Primary Completion

March 1, 2010

Study Completion

December 1, 2010

Last Updated

February 20, 2013

Results First Posted

February 20, 2013

Record last verified: 2013-01

Locations