NCT00658905

Brief Summary

The purpose of this study is to evaluate the efficacy in preterm infants following treatment with BSSL when administered in infant formula.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
33

participants targeted

Target at P25-P50 for phase_2

Timeline
Completed

Started Apr 2008

Shorter than P25 for phase_2

Geographic Reach
1 country

6 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

April 1, 2008

Completed
13 days until next milestone

First Submitted

Initial submission to the registry

April 14, 2008

Completed
2 days until next milestone

First Posted

Study publicly available on registry

April 16, 2008

Completed
1 year until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2009

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2009

Completed
Last Updated

November 3, 2014

Status Verified

October 1, 2014

Enrollment Period

1.1 years

First QC Date

April 14, 2008

Last Update Submit

October 31, 2014

Conditions

Keywords

Preterm infantsReplacement therapyInfant formulaBSSLBSSL is present in fresh mother's milk but not in infant formula.

Outcome Measures

Primary Outcomes (1)

  • Coefficient of Fat Absorption in stool

    Stool collected for a 72-hour period during the final 3 days of each treatment period

Secondary Outcomes (1)

  • Change in length and body weight between the start and end of each treatment period

    Baseline and after one week of treatment

Study Arms (2)

rhBSSL

ACTIVE COMPARATOR
Drug: rhBSSL

Placebo

PLACEBO COMPARATOR
Drug: Placebo

Interventions

rhBSSLDRUG

0.15 g/L rhBSSL added to infant formula; one week treatment

Also known as: bucelipase alfa (INN)
rhBSSL

One week treatment

Placebo

Eligibility Criteria

AgeUp to 32 Weeks
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17)

You may qualify if:

  • Preterm infants
  • less than or equal to 32 weeks of gestational age
  • appropriate for gestational age
  • enterally fed with infant formula

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (6)

Presidio Ospedaliero di Alta Specializzazione G.Salesi Azienda Ospedaliero Universitaria Ospedali Riuniti "Umberto I-G.M.Lancisi -G.Salesi

Ancona, Italy

Location

Azienda Ospedaliera "Ospedale Policlinico Consorziale",U.O Neonatologia e Terapia Intensiva Neonatale

Bari, Italy

Location

3) U.O. di Neonatologia e Terapia Intensiva Neonatale Università degli Studi di Milano, Ospedale Maggiore Policlinico,Mangiagalli e Regina Elena-Fondazione IRCCS

Milan, Italy

Location

4) Policlinico Universitario-Azienda Ospedaliera di Padova, Dipartimento di Pediatria

Padua, Italy

Location

Clinical Pediatrica-Neonatologia, Policlinico Gemelli, Universita Cattolica

Rome, Italy

Location

U.O. Neonatologia, Patologia Neonatale e Terapia Intensiva

Rome, Italy

Location

Related Publications (1)

  • Casper C, Carnielli VP, Hascoet JM, Lapillonne A, Maggio L, Timdahl K, Olsson B, Vagero M, Hernell O. rhBSSL improves growth and LCPUFA absorption in preterm infants fed formula or pasteurized breast milk. J Pediatr Gastroenterol Nutr. 2014 Jul;59(1):61-9. doi: 10.1097/MPG.0000000000000365.

Study Officials

  • Kristina Timdahl, MD

    Biovitrum AB

    STUDY DIRECTOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
CROSSOVER
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

April 14, 2008

First Posted

April 16, 2008

Study Start

April 1, 2008

Primary Completion

May 1, 2009

Study Completion

May 1, 2009

Last Updated

November 3, 2014

Record last verified: 2014-10

Locations