NCT00638690

Brief Summary

This is a phase 3 study to compare the clinical benefit of abiraterone acetate plus prednisone with placebo plus prednisone in patients with metastatic castration-resistant prostate cancer (CRPC) who have failed one or two chemotherapy regimens. At least one of the previous chemotherapies must have contained docetaxel.

Trial Health

98
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Strong global presence with extensive site network
Enrollment
1,195

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started May 2008

Typical duration for phase_3

Geographic Reach
11 countries

110 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

First Submitted

Initial submission to the registry

March 13, 2008

Completed
6 days until next milestone

First Posted

Study publicly available on registry

March 19, 2008

Completed
1 month until next milestone

Study Start

First participant enrolled

May 1, 2008

Completed
2.3 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2010

Completed
2.2 years until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2012

Completed
8 months until next milestone

Results Posted

Study results publicly available

May 16, 2013

Completed
Last Updated

April 30, 2014

Status Verified

April 1, 2014

Enrollment Period

2.3 years

First QC Date

March 13, 2008

Results QC Date

August 23, 2011

Last Update Submit

April 10, 2014

Conditions

Keywords

Metastatic Castration-Resistant Prostate CancerCRPCAbiraterone AcetateCB7630

Outcome Measures

Primary Outcomes (1)

  • Overall Survival

    Overall survival is defined as the time interval from the date of randomization to the date of death from any cause.

    Up to 60 months

Secondary Outcomes (3)

  • Time to Prostate-Specific Antigen Progression According to Prostate Specific Antigen Working Group Criteria

    Up to 12 months

  • Number of Patients Achieving a Prostate-Specific Antigen Decline >=50%

    Up to 12 months

  • Radiographic Progression-free Survival

    Up to 11 months

Study Arms (2)

Abiraterone acetate plus prednisone/prednisolone

EXPERIMENTAL
Drug: Abiraterone acetateDrug: Prednisone/prednisolone

Placebo plus prednisone/prednisolone

PLACEBO COMPARATOR
Drug: PlaceboDrug: Prednisone/prednisolone

Interventions

Four tablets once daily until disease progression

Placebo plus prednisone/prednisolone

Four 250-mg tablets once daily until disease progression

Abiraterone acetate plus prednisone/prednisolone

5 mg twice daily until disease progression

Abiraterone acetate plus prednisone/prednisolonePlacebo plus prednisone/prednisolone

Eligibility Criteria

Age18 Years+
Sexmale
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Metastatic Castration-Resistant Prostate Cancer Progression after one or two prior cytotoxic chemotherapies
  • At least one chemotherapy must have contained docetaxel
  • Eastern Cooperative Oncology Group (ECOG) Performance Status \<= 2
  • Medical or surgical castration with testosterone \< 50 ng/dL
  • Adequate bone marrow, hepatic and renal function
  • Potassium \>= 3.5 mmol/L
  • Able to swallow the study drug whole as a tablet
  • Informed Consent

You may not qualify if:

  • More than two prior cytotoxic chemotherapy regimens
  • Prior Ketoconazole for prostate cancer
  • Prior abiraterone acetate or other CYP17 inhibitor or investigational agents targeting the androgen receptor for prostate cancer
  • Uncontrolled hypertension
  • Active or symptomatic viral hepatitis or chronic liver disease
  • History of pituitary or adrenal dysfunction
  • Clinically significant heart disease
  • Other malignancy
  • Known brain metastasis
  • GI disorder affecting absorption
  • Not willing to use contraception

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (127)

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Birmingham, Alabama, United States

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Tucson, Arizona, United States

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Beverly Hills, California, United States

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Duarte, California, United States

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Los Angeles, California, United States

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Marina del Rey, California, United States

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Sacramento, California, United States

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San Diego, California, United States

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San Francisco, California, United States

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Aurora, Colorado, United States

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Bristol, Connecticut, United States

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New Haven, Connecticut, United States

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Stamford, Connecticut, United States

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Boca Raton, Florida, United States

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Fort Lauderdale, Florida, United States

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Fort Myers, Florida, United States

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West Palm Beach, Florida, United States

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Atlanta, Georgia, United States

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Honolulu, Hawaii, United States

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Chicago, Illinois, United States

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Galesburg, Illinois, United States

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Indianapolis, Indiana, United States

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Westwood, Kansas, United States

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Wichita, Kansas, United States

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Marrero, Louisiana, United States

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New Orleans, Louisiana, United States

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Baltimore, Maryland, United States

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Boston, Massachusetts, United States

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Detroit, Michigan, United States

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Robbinsdale, Minnesota, United States

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St Louis, Missouri, United States

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Billings, Montana, United States

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Omaha, Nebraska, United States

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Las Vegas, Nevada, United States

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Box 302, New York, United States

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East Setauket, New York, United States

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New Hyde Park, New York, United States

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New York, New York, United States

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Stony Brook, New York, United States

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Durham, North Carolina, United States

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Raleigh, North Carolina, United States

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Canton, Ohio, United States

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Cincinnati, Ohio, United States

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Portland, Oregon, United States

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Philadelphia, Pennsylvania, United States

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Pittsburgh, Pennsylvania, United States

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Myrtle Beach, South Carolina, United States

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Chattanooga, Tennessee, United States

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Nashville, Tennessee, United States

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Dallas, Texas, United States

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Houston, Texas, United States

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San Antonio, Texas, United States

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Virgiania Beach, Virginia, United States

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Seattle, Washington, United States

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Adelaide, Australia

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Camperdown, Australia

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Footscray, Australia

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Geelong, Australia

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Heidelberg, Australia

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Herston, Australia

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Hobart, Australia

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Hornsby, Australia

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Kogarah, Australia

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Kurralta Park, Australia

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Liverpool, Australia

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Milton, Australia

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Parkville, Australia

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Perth, Australia

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Subiaco, Australia

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Wodonga, Australia

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Wollongong, Australia

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Linz, Austria

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Salzburg, Austria

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Vienna, Austria

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Antwerp, Belgium

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Bonheiden, Belgium

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Brussels, Belgium

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Ghent, Belgium

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Hasselt, Belgium

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Kortrijk, Belgium

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Leuven, Belgium

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Liège, Belgium

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Roeselare, Belgium

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Edmonton, Alberta, Canada

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Kelowna, British Columbia, Canada

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Vancouver, British Columbia, Canada

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Victoria, British Columbia, Canada

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Halifax, Nova Scotia, Canada

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Hamilton, Ontario, Canada

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Toronto, Ontario, Canada

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Montreal, Quebec, Canada

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Regina, Saskatchewan, Canada

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Calgary Ab, Canada

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London, Canada

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Angers, France

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Caen, France

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Cannes, France

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Dijon, France

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Lyon, France

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Paris, France

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Saint-Herblain, France

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Vandœuvre-lès-Nancy, France

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Villejuif, France

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Aachen, Germany

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Berlin, Germany

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Dresden, Germany

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Hamburg, Germany

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Homburg/Saar, Germany

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Pécs, Hungary

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Szombathely, Hungary

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Cork, Ireland

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Dublin, Ireland

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Nijmegen, Netherlands

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Badalona, Spain

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Barcelona, Spain

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Madrid, Spain

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Belfast, United Kingdom

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Birmingham, United Kingdom

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Cambridge, United Kingdom

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Glasgow, United Kingdom

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London, United Kingdom

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Manchester, United Kingdom

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Newcastle upon Tyne, United Kingdom

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Northwood, United Kingdom

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Oxford, United Kingdom

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Sutton, United Kingdom

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Whitchurch, United Kingdom

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Related Publications (12)

  • Heller G, McCormack R, Kheoh T, Molina A, Smith MR, Dreicer R, Saad F, de Wit R, Aftab DT, Hirmand M, Limon A, Fizazi K, Fleisher M, de Bono JS, Scher HI. Circulating Tumor Cell Number as a Response Measure of Prolonged Survival for Metastatic Castration-Resistant Prostate Cancer: A Comparison With Prostate-Specific Antigen Across Five Randomized Phase III Clinical Trials. J Clin Oncol. 2018 Feb 20;36(6):572-580. doi: 10.1200/JCO.2017.75.2998. Epub 2017 Dec 22.

  • Chi KN, Kheoh T, Ryan CJ, Molina A, Bellmunt J, Vogelzang NJ, Rathkopf DE, Fizazi K, Kantoff PW, Li J, Azad AA, Eigl BJ, Heng DY, Joshua AM, de Bono JS, Scher HI. A prognostic index model for predicting overall survival in patients with metastatic castration-resistant prostate cancer treated with abiraterone acetate after docetaxel. Ann Oncol. 2016 Mar;27(3):454-60. doi: 10.1093/annonc/mdv594. Epub 2015 Dec 18.

  • Fizazi K, Flaig TW, Stockle M, Scher HI, de Bono JS, Rathkopf DE, Ryan CJ, Kheoh T, Li J, Todd MB, Griffin TW, Molina A, Ohlmann CH. Does Gleason score at initial diagnosis predict efficacy of abiraterone acetate therapy in patients with metastatic castration-resistant prostate cancer? An analysis of abiraterone acetate phase III trials. Ann Oncol. 2016 Apr;27(4):699-705. doi: 10.1093/annonc/mdv545. Epub 2015 Nov 25.

  • Antoun S, Bayar A, Ileana E, Laplanche A, Fizazi K, di Palma M, Escudier B, Albiges L, Massard C, Loriot Y. High subcutaneous adipose tissue predicts the prognosis in metastatic castration-resistant prostate cancer patients in post chemotherapy setting. Eur J Cancer. 2015 Nov;51(17):2570-7. doi: 10.1016/j.ejca.2015.07.042. Epub 2015 Aug 13.

  • Xu XS, Ryan CJ, Stuyckens K, Smith MR, Saad F, Griffin TW, Park YC, Yu MK, Vermeulen A, Poggesi I, Nandy P. Correlation between Prostate-Specific Antigen Kinetics and Overall Survival in Abiraterone Acetate-Treated Castration-Resistant Prostate Cancer Patients. Clin Cancer Res. 2015 Jul 15;21(14):3170-7. doi: 10.1158/1078-0432.CCR-14-1549. Epub 2015 Mar 31.

  • Scher HI, Heller G, Molina A, Attard G, Danila DC, Jia X, Peng W, Sandhu SK, Olmos D, Riisnaes R, McCormack R, Burzykowski T, Kheoh T, Fleisher M, Buyse M, de Bono JS. Circulating tumor cell biomarker panel as an individual-level surrogate for survival in metastatic castration-resistant prostate cancer. J Clin Oncol. 2015 Apr 20;33(12):1348-55. doi: 10.1200/JCO.2014.55.3487. Epub 2015 Mar 23.

  • Mulders PF, Molina A, Marberger M, Saad F, Higano CS, Chi KN, Li J, Kheoh T, Haqq CM, Fizazi K. Efficacy and safety of abiraterone acetate in an elderly patient subgroup (aged 75 and older) with metastatic castration-resistant prostate cancer after docetaxel-based chemotherapy. Eur Urol. 2014 May;65(5):875-83. doi: 10.1016/j.eururo.2013.09.005. Epub 2013 Sep 20.

  • Harland S, Staffurth J, Molina A, Hao Y, Gagnon DD, Sternberg CN, Cella D, Fizazi K, Logothetis CJ, Kheoh T, Haqq CM, de Bono JS, Scher HI; COU-AA-301 Investigators. Effect of abiraterone acetate treatment on the quality of life of patients with metastatic castration-resistant prostate cancer after failure of docetaxel chemotherapy. Eur J Cancer. 2013 Nov;49(17):3648-57. doi: 10.1016/j.ejca.2013.07.144. Epub 2013 Aug 22.

  • Ryan CJ, Molina A, Li J, Kheoh T, Small EJ, Haqq CM, Grant RP, de Bono JS, Scher HI. Serum androgens as prognostic biomarkers in castration-resistant prostate cancer: results from an analysis of a randomized phase III trial. J Clin Oncol. 2013 Aug 1;31(22):2791-8. doi: 10.1200/JCO.2012.45.4595. Epub 2013 Jul 1.

  • Logothetis CJ, Basch E, Molina A, Fizazi K, North SA, Chi KN, Jones RJ, Goodman OB, Mainwaring PN, Sternberg CN, Efstathiou E, Gagnon DD, Rothman M, Hao Y, Liu CS, Kheoh TS, Haqq CM, Scher HI, de Bono JS. Effect of abiraterone acetate and prednisone compared with placebo and prednisone on pain control and skeletal-related events in patients with metastatic castration-resistant prostate cancer: exploratory analysis of data from the COU-AA-301 randomised trial. Lancet Oncol. 2012 Dec;13(12):1210-7. doi: 10.1016/S1470-2045(12)70473-4. Epub 2012 Nov 9.

  • Fizazi K, Scher HI, Molina A, Logothetis CJ, Chi KN, Jones RJ, Staffurth JN, North S, Vogelzang NJ, Saad F, Mainwaring P, Harland S, Goodman OB Jr, Sternberg CN, Li JH, Kheoh T, Haqq CM, de Bono JS; COU-AA-301 Investigators. Abiraterone acetate for treatment of metastatic castration-resistant prostate cancer: final overall survival analysis of the COU-AA-301 randomised, double-blind, placebo-controlled phase 3 study. Lancet Oncol. 2012 Oct;13(10):983-92. doi: 10.1016/S1470-2045(12)70379-0. Epub 2012 Sep 18.

  • de Bono JS, Logothetis CJ, Molina A, Fizazi K, North S, Chu L, Chi KN, Jones RJ, Goodman OB Jr, Saad F, Staffurth JN, Mainwaring P, Harland S, Flaig TW, Hutson TE, Cheng T, Patterson H, Hainsworth JD, Ryan CJ, Sternberg CN, Ellard SL, Flechon A, Saleh M, Scholz M, Efstathiou E, Zivi A, Bianchini D, Loriot Y, Chieffo N, Kheoh T, Haqq CM, Scher HI; COU-AA-301 Investigators. Abiraterone and increased survival in metastatic prostate cancer. N Engl J Med. 2011 May 26;364(21):1995-2005. doi: 10.1056/NEJMoa1014618.

MeSH Terms

Conditions

Prostatic Neoplasms

Interventions

Abiraterone AcetatePrednisonePrednisolone

Condition Hierarchy (Ancestors)

Genital Neoplasms, MaleUrogenital NeoplasmsNeoplasms by SiteNeoplasmsGenital Diseases, MaleGenital DiseasesUrogenital DiseasesProstatic DiseasesMale Urogenital Diseases

Intervention Hierarchy (Ancestors)

AndrostenesAndrostanesSteroidsFused-Ring CompoundsPolycyclic CompoundsPregnadienediolsPregnadienesPregnanesPregnadienetriols

Results Point of Contact

Title
Senior Director, Clinical Research
Organization
Johnson & Johnson Pharmaceutical Research & Development

Study Officials

  • Cougar Biotechnology, Inc Clinical Trial

    Cougar Biotechnology, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 13, 2008

First Posted

March 19, 2008

Study Start

May 1, 2008

Primary Completion

August 1, 2010

Study Completion

October 1, 2012

Last Updated

April 30, 2014

Results First Posted

May 16, 2013

Record last verified: 2014-04

Locations