NCT00626028

Brief Summary

The primary purpose of this study is to compare the number of participants with reversible pulmonary hypertension (vasoreactivity) due to nitric oxide for inhalation and oxygen as compared to 100% oxygen.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
136

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Sep 2004

Longer than P75 for phase_3

Geographic Reach
5 countries

18 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2004

Completed
3.5 years until next milestone

First Submitted

Initial submission to the registry

February 20, 2008

Completed
9 days until next milestone

First Posted

Study publicly available on registry

February 29, 2008

Completed
1.9 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

February 1, 2010

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

February 1, 2010

Completed
8 months until next milestone

Results Posted

Study results publicly available

September 16, 2010

Completed
Last Updated

December 20, 2019

Status Verified

September 1, 2016

Enrollment Period

5.4 years

First QC Date

February 20, 2008

Results QC Date

September 21, 2009

Last Update Submit

December 6, 2019

Conditions

Keywords

Pulmonary VasculatureNitric OxideINOmax®Acute Lung InjuryPulmonary Vasodilator TestingIdiopathic Pulmonary Arterial HypertensionCongenital Heart Diseasereversible pulmonary hypertensionvasoreactivityCongenital Heart Disease with Pulmonary Hypertension

Outcome Measures

Primary Outcomes (1)

  • Number of Participants With Reversible Pulmonary Hypertension (Vasoreactivity)

    A composite of hemodynamic measurements were used to identify reversible pulmonary hypertension (vasoreactivity)

    on Day 1

Secondary Outcomes (4)

  • Number of Participants With Related Surgical Procedures Within 1 Year

    within 1 year

  • Number of Participants With Adverse Events (AEs)

    on Day 1

  • Number of Participants With Serious Adverse Events (SAEs)

    within 12 hours

  • Number of Participants With Related Surgical Procedures Within 3 Years

    within 3 years

Study Arms (2)

Nitric Oxide First, Oxygen Last

EXPERIMENTAL

10 minute dose of Nitric Oxide (NO) at 80 ppm, then 10 minute dose of NO plus Oxygen, then 10 minute washout, then 10 minute dose of 100% Oxygen on Day 1.

Drug: Nitric Oxide for inhalationDrug: OxygenDrug: Nitric Oxide plus Oxygen

Oxygen First, Nitric Oxide Last

EXPERIMENTAL

10 minute dose of 100% Oxygen, then 10 minute dose of NO plus Oxygen, then 10 minute washout, then 10 minute dose of NO at 80 ppm on Day 1.

Drug: Nitric Oxide for inhalationDrug: OxygenDrug: Nitric Oxide plus Oxygen

Interventions

Nitric Oxide (NO) for inhalation, given at 80ppm over 10 minutes using an INOvent® delivery system

Also known as: INOmax®
Nitric Oxide First, Oxygen LastOxygen First, Nitric Oxide Last
OxygenDRUG

100% oxygen (O2) for inhalation, given at 80ppm over 10 minutes using an INOvent® delivery system

Nitric Oxide First, Oxygen LastOxygen First, Nitric Oxide Last

Nitric Oxide (NO) for inhalation plus oxygen, given at 80ppm over 10 minutes using an INOvent® delivery system

Also known as: Inhaled Nitric Oxide, Oxygen
Nitric Oxide First, Oxygen LastOxygen First, Nitric Oxide Last

Eligibility Criteria

Age4 Weeks - 18 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Must have any one of these three disease categories:
  • Idiopathic Pulmonary Arterial Hypertension
  • Mean pulmonary arterial pressure (PAPm) \> 25 millimeters of mercury (mmHg) at rest, pulmonary capillary wedge pressure (PCWP) ≤ 15 mmHg, and PVRI\> 3 u•m\^2 or diagnosed clinically with no previous catheterization
  • Congenital heart disease (CHD) with pulmonary hypertension repaired and unrepaired
  • PAPm \> 25 mmHg at rest and PVRI\> 3 u•m\^2 or diagnosed clinically with no previous catheterization
  • Cardiomyopathy
  • PAPm \> 25 mmHg at rest and Pulmonary vascular resistance index (PVRI)\> 3 u•m\^2 or diagnosed clinically with no previous catheterization
  • Scheduled to undergo right heart catheterization to assess pulmonary vasoreactivity by acute pulmonary vasodilation testing.
  • Male or female, ages 4 weeks to 18 years, inclusive
  • Signed informed consent/assent

You may not qualify if:

  • Focal pulmonary infiltrates on chest radiograph.
  • Diagnosed with severe obstructive or restrictive pulmonary disease that is significantly contributing to the patient's pulmonary hypertension.
  • Received treatment with nitric oxide for inhalation within 30 days prior to study initiation, are on other investigational medications, nitroglycerin, sodium nitroprusside, sildenafil, other Phosphodiesterase type 5 (PDE-5) inhibitors, or prostacyclin
  • Pregnant \[urine human chorionic gonadotropin positive (HCG +)\]
  • Baseline Pulmonary capillary wedge pressure (PCWP) \> 20 mmHg

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (18)

Lucile Salter Packard Children's Hospital at Stanford

Stanford, California, 94304, United States

Location

The Children's Hospital

Denver, Colorado, 80218, United States

Location

Children's Hospital Boston

Boston, Massachusetts, 02115, United States

Location

St. Louis Children's Hospital

St Louis, Missouri, 63110, United States

Location

New York Presbyterian Hospital

New York, New York, 10032, United States

Location

Cincinnati Children's Hospital

Cincinnati, Ohio, 45229, United States

Location

Columbus Children's Hospital

Columbus, Ohio, 43205, United States

Location

The Medical University of South Carolina

Charleston, South Carolina, 29425, United States

Location

CHU Timone - Département de cardiologie

Marseille, France

Location

Hôpital d'Enfants

Nancy, France

Location

Hôpital NECKER - Enfants Malades

Paris, France

Location

Beatrix Children's Hospital / University Hospital Groningen

Groningen, Netherlands

Location

Hospital Sant Joan de Déu de Barcelona

Barcelona, Spain

Location

Unidad de Cardiologia Infantil - Hospital Vall d'Hebrón

Barcelona, Spain

Location

Hospital Gregorio Maranon

Madrid, Spain

Location

Instituto Pediátrico del Corazón - Hospital Materno Infatil Doce de Octubre

Madrid, Spain

Location

Royal Brompton Hospital

London, United Kingdom

Location

Southampton University Hospitals Trust - Wessex Cardiothoracic Centre

Southampton, United Kingdom

Location

Related Publications (1)

  • Barst RJ, Agnoletti G, Fraisse A, Baldassarre J, Wessel DL; NO Diagnostic Study Group. Vasodilator testing with nitric oxide and/or oxygen in pediatric pulmonary hypertension. Pediatr Cardiol. 2010 Jul;31(5):598-606. doi: 10.1007/s00246-010-9645-5. Epub 2010 Apr 20.

MeSH Terms

Conditions

Familial Primary Pulmonary HypertensionCardiomyopathiesAcute Lung InjuryHeart Defects, Congenital

Interventions

Nitric OxideInhalationEndothelium-Dependent Relaxing FactorsOxygen

Condition Hierarchy (Ancestors)

Hypertension, PulmonaryLung DiseasesRespiratory Tract DiseasesHeart DiseasesCardiovascular DiseasesLung InjuryCardiovascular AbnormalitiesCongenital AbnormalitiesCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Intervention Hierarchy (Ancestors)

Reactive Nitrogen SpeciesFree RadicalsInorganic ChemicalsNitrogen OxidesNitrogen CompoundsOxidesOxygen CompoundsOrganic ChemicalsRespiratory MechanicsRespirationRespiratory Physiological PhenomenaCirculatory and Respiratory Physiological PhenomenaVasodilator AgentsCardiovascular AgentsTherapeutic UsesPharmacologic ActionsChemical Actions and UsesChalcogensElementsGases

Limitations and Caveats

Although the first and last treatments were randomly assigned, the second treatment was always the same. Therefore, a time/treatment interaction cannot be ruled out.

Results Point of Contact

Title
Medical Information Call Center
Organization
Mallinckrodt Pharmaceuticals

Study Officials

  • Global Clinical Leader, MD

    Mallinckrodt

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
DIAGNOSTIC
Intervention Model
CROSSOVER
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

February 20, 2008

First Posted

February 29, 2008

Study Start

September 1, 2004

Primary Completion

February 1, 2010

Study Completion

February 1, 2010

Last Updated

December 20, 2019

Results First Posted

September 16, 2010

Record last verified: 2016-09

Data Sharing

IPD Sharing
Will not share

Locations