NCT00597584

Brief Summary

The purpose of this study was to evaluate the safety and efficacy of peginesatide in the maintenance treatment of anemia in participants on dialysis.

Trial Health

93
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
823

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Oct 2007

Geographic Reach
9 countries

84 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

October 1, 2007

Completed
3 months until next milestone

First Submitted

Initial submission to the registry

January 10, 2008

Completed
8 days until next milestone

First Posted

Study publicly available on registry

January 18, 2008

Completed
1.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

July 1, 2009

Completed
6 months until next milestone

Study Completion

Last participant's last visit for all outcomes

January 1, 2010

Completed
2.6 years until next milestone

Results Posted

Study results publicly available

July 30, 2012

Completed
Last Updated

March 8, 2013

Status Verified

March 1, 2013

Enrollment Period

1.8 years

First QC Date

January 10, 2008

Results QC Date

April 26, 2012

Last Update Submit

March 6, 2013

Conditions

Keywords

anemiachronic kidney diseaseCKDchronic renal failureCRFdialysiserythropoietinEPOerythropoiesis stimulating agentESAHematide™hemodialysishemoglobinHbHgbOmontyspeginesatidered blood cellred blood cell production

Outcome Measures

Primary Outcomes (1)

  • Mean Change in Hemoglobin Between Baseline and the Evaluation Period

    The baseline hemoglobin value is defined as the mean of five hemoglobin values: the four most recent hemoglobin values taken prior to the day of randomization and the value obtained on the day of randomization. The mean hemoglobin during the Evaluation Period for each participant is calculated as the mean of the available hemoglobin values during study Weeks 29 through 36.

    Baseline to Weeks 29-36

Secondary Outcomes (2)

  • Proportion of Participants Who Receive Red Blood Cell (RBC) Transfusions During the Titration and Evaluation Periods

    Weeks 0 to 36

  • Proportion of Participants Whose Mean Hemoglobin Level During the Evaluation Period is Within the Target Range of 10.0 - 12.0 Grams Per Deciliter (g/dL)

    Weeks 29 to 36

Study Arms (2)

Peginesatide

EXPERIMENTAL
Drug: peginesatide

Epoetin

ACTIVE COMPARATOR
Drug: Epoetin alfa or Epoetin beta

Interventions

Participants received peginesatide by intravenous (IV) or subcutaneous (SC) injection once every 4 weeks. The starting dose was based on the participant's total weekly epoetin alfa or beta dose during the last week of the Screening Period; the first dose was administered one week after the last epoetin alfa or beta dose. Participants who received epoetin alfa or beta IV at the time of screening received peginesatide IV during the study, and participants who received epoetin alfa or beta SC at the time of screening received peginesatide SC during the study. The dose was adjusted to maintain hemoglobin levels in a target range of 10.0-12.0 g/dL and ± 1.5 g/dL from baseline during the Titration and Evaluation Periods, and 10.0-12.0 g/dL during the Long-Term Safety and Efficacy Period.

Also known as: Omontys, Hematide, AF37702 Injection
Peginesatide

Participants continued to receive commercially available epoetin alfa or beta by intravenous or subcutaneous injection, at the same starting dose, frequency and route of administration as received during the last week of the Screening Period, with the first study dose of epoetin alfa or beta administered after randomization at Week 0. The dose was adjusted to maintain hemoglobin levels in a target range of 10.0-12.0 g/dL and ± 1.5 g/dL from baseline during the Titration and Evaluation Periods, and 10.0-12.0 g/dL during the Long-Term Safety and Efficacy Period.

Also known as: Epogen, Neorecormon
Epoetin

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Participants with chronic renal failure on hemodialysis for ≥ 3 months prior to randomization.
  • On IV epoetin alfa or beta maintenance therapy continuously prescribed for a minimum of 8 weeks prior to randomization.
  • Four consecutive hemoglobin values with a mean ≥ 10.0 and ≤ 12.0 g/dL during the Screening Period.

You may not qualify if:

  • Females who are pregnant or breast-feeding.
  • Known intolerance to any erythropoiesis stimulating agent or pegylated molecule or to all parenteral iron supplementation products.
  • Known bleeding or coagulation disorder.
  • Known hematologic disease or cause of anemia other than renal disease
  • Poorly controlled hypertension.
  • Evidence of active malignancy within one year prior to randomization.
  • Temporary (untunneled) dialysis access catheter.
  • A scheduled kidney transplant.
  • A scheduled surgery that may be expected to lead to significant blood loss.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (84)

Research Facility

Phoenix, Arizona, 85012, United States

Location

Research Facility

Hot Springs, Arkansas, 71901, United States

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Research Facility

McGehee, Arkansas, 71654, United States

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Research Facility

Pine Bluff, Arkansas, 71603, United States

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Research Facility

Bakersfield, California, 93309, United States

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Research Facility

Glendale, California, 91205, United States

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Research Facility

Los Angeles, California, 90033, United States

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Research Facility

Los Angeles, California, 90048, United States

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Research Facility

Los Angeles, California, 90073, United States

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Research Facility

Riverside, California, 92505, United States

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Simi Valley, California, 93065, United States

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Whittier, California, 90602, United States

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Research Facility

Yuba City, California, 95991, United States

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Westminster, Colorado, 80031, United States

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Lauderdale Lakes, Florida, 33313, United States

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Miami, Florida, 33173, United States

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Research Facility

Pinecrest, Florida, 33156, United States

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Flossmoor, Illinois, 60422, United States

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Hines, Illinois, 60141, United States

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Louisville, Kentucky, 40202, United States

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Rockville, Maryland, 20850, United States

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Springfield, Massachusetts, 01107, United States

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Detroit, Michigan, 48202, United States

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Detroit, Michigan, 48236, United States

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Brookhaven, Mississippi, 39601, United States

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Brooklyn, New York, 11238, United States

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Flushing, New York, 11355, United States

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The Bronx, New York, 10461, United States

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Asheville, North Carolina, 28801, United States

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Toledo, Ohio, 43606, United States

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Oklahoma City, Oklahoma, 73116, United States

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Erie, Pennsylvania, 16507, United States

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Philadelphia, Pennsylvania, 19141, United States

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Providence, Rhode Island, 02904, United States

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Orangeburg, South Carolina, 29118, United States

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Arlington, Texas, 76015, United States

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Houston, Texas, 77099, United States

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San Antonio, Texas, 78215, United States

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Fairfax, Virginia, 22033, United States

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Burgas, 8000, Bulgaria

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Research Facility

Pazardzhik, 4400, Bulgaria

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Pleven, 5800, Bulgaria

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Plovdiv, 4000, Bulgaria

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Research Facility

Plovdiv, 4003, Bulgaria

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Rousse, 7002, Bulgaria

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Research Facility

Sofia, 1309, Bulgaria

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Research Facilities (2)

Sofia, 1431, Bulgaria

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Research Facility

Sofia, 1527, Bulgaria

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Research Facility

Sofia, 1606, Bulgaria

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Research Facility

Varna, 9010, Bulgaria

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Research Facility

Veliko Tarnovo, 5000, Bulgaria

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Research Facility

Amiens, 80054, France

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Research Facility

Bordeaux, 33000, France

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Research Facility

Montpellier, 34295, France

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Research Facility

Vannes, 56017, France

Location

Research Facilities (2)

Bremen, 28359, Germany

Location

Research Facility

Franfurt, 60528, Germany

Location

Research Facility

Hamburg, 22297, Germany

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Research Facility

Kaiserslautern, 67655, Germany

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Research Facility

Como, 22100, Italy

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Research Facility

Cremona, 26100, Italy

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Research Facility

Lecco, 23900, Italy

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Research Facility

Modena, 41100, Italy

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Prato, 59100, Italy

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Research Facility

Ciechanów, 06-400, Poland

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Katowice, 40-027, Poland

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Pabianice, 95-200, Poland

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Włocławek, 87-800, Poland

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Bucharest, 014461, Romania

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Research Facility

Bucharest, 050098, Romania

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Research Facility

Iași, 700503, Romania

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Research Facility

Alicante, 03010, Spain

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Research Facility

Barcelona, 08025, Spain

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Research Facility

Barcelona, 08902, Spain

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Barcelona, 08907, Spain

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Research Facility

Ciudad Real, 13005, Spain

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Research Facility

Madrid, 28041, Spain

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Research Facility

Madrid, 28922, Spain

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Santander, 39008, Spain

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Carshalton, SM5 1AA, United Kingdom

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London, E1 1BB, United Kingdom

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Research Facility

London, SE5 9RS, United Kingdom

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Research Facility

London, SW17 0QT, United Kingdom

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Research Facility

Swansea, SA6 6NL, United Kingdom

Location

Related Publications (2)

  • Fishbane S, Schiller B, Locatelli F, Covic AC, Provenzano R, Wiecek A, Levin NW, Kaplan M, Macdougall IC, Francisco C, Mayo MR, Polu KR, Duliege AM, Besarab A; EMERALD Study Groups. Peginesatide in patients with anemia undergoing hemodialysis. N Engl J Med. 2013 Jan 24;368(4):307-19. doi: 10.1056/NEJMoa1203165.

  • Macdougall IC, Provenzano R, Sharma A, Spinowitz BS, Schmidt RJ, Pergola PE, Zabaneh RI, Tong-Starksen S, Mayo MR, Tang H, Polu KR, Duliege AM, Fishbane S; PEARL Study Groups. Peginesatide for anemia in patients with chronic kidney disease not receiving dialysis. N Engl J Med. 2013 Jan 24;368(4):320-32. doi: 10.1056/NEJMoa1203166.

MeSH Terms

Conditions

Kidney Failure, ChronicRenal Insufficiency, ChronicAnemia

Interventions

peginesatidehematideEpoetin Alfaepoetin beta

Condition Hierarchy (Ancestors)

Renal InsufficiencyKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesChronic DiseaseDisease AttributesPathologic ProcessesPathological Conditions, Signs and SymptomsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

ErythropoietinColony-Stimulating FactorsGlycoproteinsGlycoconjugatesCarbohydratesHematopoietic Cell Growth FactorsCytokinesIntercellular Signaling Peptides and ProteinsPeptidesAmino Acids, Peptides, and ProteinsProteinsBiological Factors

Results Point of Contact

Title
Vice President, Clinical Development
Organization
Affymax

Study Officials

  • Vice President, Clinical Development

    Affymax

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 10, 2008

First Posted

January 18, 2008

Study Start

October 1, 2007

Primary Completion

July 1, 2009

Study Completion

January 1, 2010

Last Updated

March 8, 2013

Results First Posted

July 30, 2012

Record last verified: 2013-03

Locations