NCT00569582

Brief Summary

Patients will receive Corlux (mifepristone) daily for up to 24 weeks. Assessments of the signs and symptoms of Cushing's syndrome will be obtained.

Trial Health

80
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
50

participants targeted

Target at below P25 for phase_3

Geographic Reach
1 country

17 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

December 1, 2007

Completed
4 days until next milestone

First Submitted

Initial submission to the registry

December 5, 2007

Completed
2 days until next milestone

First Posted

Study publicly available on registry

December 7, 2007

Completed
3.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

January 1, 2011

Completed
1.4 years until next milestone

Results Posted

Study results publicly available

May 28, 2012

Completed
Last Updated

August 22, 2013

Status Verified

August 1, 2013

Enrollment Period

3.1 years

First QC Date

December 5, 2007

Results QC Date

April 4, 2012

Last Update Submit

August 12, 2013

Conditions

Keywords

Cushing's DiseaseCushing's SyndromeCushingsPituitaryACTHAdrenocorticotropic hormoneEctopicAdrenal adenomaAdrenal carcinomaAdrenal autonomyCortisolHypercortisolemiaCushingoidMoon faciesDorsocervical fatPlethoraHirsutismViolaceous striaeHormoneContraceptiveEndocrineCushing SyndromeEctopic ACTH Secretion

Outcome Measures

Primary Outcomes (2)

  • Improvement in Diabetes and/or Glucose Intolerance.

    Responder is defined as subject with a decrease greater than or equal to 25% in area under the curve for glucose on 2-hour oral glucose test from baseline to week 24 or last visit, for Cushing's patients with type-2 diabetes mellitus/impaired glucose tolerance.

    Baseline to Week 24

  • Decrease in Diastolic Blood Pressure.

    Responder is defined as subject with a decrease greater than or equal to 5mm Hg in diastolic blood pressure from baseline to week 24 or last visit.

    Baseline to Week 24

Study Arms (1)

1

EXPERIMENTAL
Drug: mifepristone

Interventions

Patients take mifepristone by mouth once a day. The dose is increased during scheduled timepoints during the study or until symptoms improve or the highest dosage allowed is reached. Dose escalation will be based upon weight. During clinic visits, blood pressure, glucose tolerance and blood chemistries are measured and EKG and urinalysis will be performed.

Also known as: CORLUX
1

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Individuals eligible for enrollment into this study are adult male and non-pregnant female adult patients who:
  • Are at least 18 years of age
  • Have a confirmed diagnosis of endogenous hypercortisolemia caused by ACTH dependent or ACTH independent etiologies, including
  • Cushing's Disease (that has recurred after primary pituitary surgery, or has failed pituitary surgery, or has been treated with radiation therapy to the pituitary, or is not treatable with surgery, or exists in patients who are not candidates for surgery, and is confirmed by documentation of ACTH immuno-reactivity on a pathological evaluation of pituitary tissue from a previous surgical specimen or IPSS with a central-to-peripheral gradient (ratio) of \>2 before or \>3 after CRH administration).
  • Ectopic ACTH
  • Ectopic CRF secretion
  • Adrenal adenoma
  • Adrenal carcinoma
  • Adrenal autonomy
  • Require medical treatment of hypercortisolemia

You may not qualify if:

  • Individuals not eligible to be enrolled into the study are those who:
  • Have de novo Cushing's disease and are surgical candidates for pituitary surgery.
  • Have an acute or unstable medical problem, which could be aggravated by mifepristone treatment.
  • Taking medications within 14 days of the baseline visit (Day 1) that a) have a large first pass metabolism largely mediated by CYP3A4 and a narrow therapeutic margin and/or b) are strong CYP3A4 inhibitors.
  • Female patients of reproductive potential, who are pregnant or who are unable or unwilling to use medically acceptable, non-hormonal methods of contraception during the study.
  • Have received investigational treatment (drug, biological agent or device) within 30 days of Screening
  • Have a history of an allergic reaction or intolerance to CORLUX (mifepristone)
  • Have a non-endogenous source of hypercortisolemia such as factious hypercortisolemia (exogenous source of glucocorticoid, iatrogenic Cushing's syndrome), factious or therapeutic use of ACTH
  • Have Pseudo-Cushing's syndrome.
  • Receive PPARgamma agonist drugs (e.g. pioglitazone, rosiglitazone) within 4 months of Baseline (Day 1).
  • Postmenopausal women with an intact uterus who have experienced unexplained vaginal bleeding within 12 months of Screening are excluded.
  • Have renal failure as defined by a serum creatinine of ≥2.2 mg/dL.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (17)

University of Alabama at Birmingham School of Medicine

Birmingham, Alabama, 35294, United States

Location

AMCR Institute Inc.

Escondido, California, 92026, United States

Location

Stanford University Medical Center

Stanford, California, 94305-5826, United States

Location

The Center for Diabetes and Endocrine Care

Hollywood, Florida, 33021, United States

Location

Northwestern University Feinberg Medical; Division of Endocrinology, Metabolism & Molecular Medicine

Chicago, Illinois, 60611, United States

Location

The University of Chicago

Chicago, Illinois, 60637, United States

Location

Sinai Hospital of Baltimore

Baltimore, Maryland, 21215, United States

Location

Massachusetts General Hospital

Boston, Massachusetts, 02114, United States

Location

University of Michigan Medical Center

Ann Arbor, Michigan, 48109, United States

Location

University of Mississippi Medical Center

Jackson, Mississippi, 39216, United States

Location

University of New Mexico HSC

Albuquerque, New Mexico, 87131, United States

Location

Cleveland Clinic Foundation; Dept of Endocrinology, Diabetes & Metabolism

Cleveland, Ohio, 44195, United States

Location

Oklahoma University Health Science Center

Oklahoma City, Oklahoma, 73104, United States

Location

Oregon Health Sciences University

Portland, Oregon, 97239, United States

Location

University of Texas Southwestern Medical Center

Dallas, Texas, 75390, United States

Location

Diabetes and Glandular Disease Clinic

San Antonio, Texas, 78229, United States

Location

Endocrinology Center at North Hills, Froedtert and Medical College of Wisconsin

Menomonee Falls, Wisconsin, 53051, United States

Location

Related Publications (11)

  • Sartor O, Cutler GB Jr. Mifepristone: treatment of Cushing's syndrome. Clin Obstet Gynecol. 1996 Jun;39(2):506-10. doi: 10.1097/00003081-199606000-00024.

    PMID: 8734015BACKGROUND
  • Johanssen S, Allolio B. Mifepristone (RU 486) in Cushing's syndrome. Eur J Endocrinol. 2007 Nov;157(5):561-9. doi: 10.1530/EJE-07-0458.

    PMID: 17984235BACKGROUND
  • Morris D, Grossman A. The medical management of Cushing's syndrome. Ann N Y Acad Sci. 2002 Sep;970:119-33. doi: 10.1111/j.1749-6632.2002.tb04418.x.

    PMID: 12381547BACKGROUND
  • Chu JW, Matthias DF, Belanoff J, Schatzberg A, Hoffman AR, Feldman D. Successful long-term treatment of refractory Cushing's disease with high-dose mifepristone (RU 486). J Clin Endocrinol Metab. 2001 Aug;86(8):3568-73. doi: 10.1210/jcem.86.8.7740.

    PMID: 11502780BACKGROUND
  • Agarwai MK. The antiglucocorticoid action of mifepristone. Pharmacol Ther. 1996;70(3):183-213. doi: 10.1016/0163-7258(96)00016-2.

    PMID: 8888066BACKGROUND
  • Miller JW, Crapo L. The medical treatment of Cushing's syndrome. Endocr Rev. 1993 Aug;14(4):443-58. doi: 10.1210/edrv-14-4-443. No abstract available.

    PMID: 7693447BACKGROUND
  • Nieman LK, Chrousos GP, Kellner C, Spitz IM, Nisula BC, Cutler GB, Merriam GR, Bardin CW, Loriaux DL. Successful treatment of Cushing's syndrome with the glucocorticoid antagonist RU 486. J Clin Endocrinol Metab. 1985 Sep;61(3):536-40. doi: 10.1210/jcem-61-3-536.

    PMID: 2991327BACKGROUND
  • Fleseriu M, Biller BM, Findling JW, Molitch ME, Schteingart DE, Gross C; SEISMIC Study Investigators. Mifepristone, a glucocorticoid receptor antagonist, produces clinical and metabolic benefits in patients with Cushing's syndrome. J Clin Endocrinol Metab. 2012 Jun;97(6):2039-49. doi: 10.1210/jc.2011-3350. Epub 2012 Mar 30.

  • Fein HG, Vaughan TB 3rd, Kushner H, Cram D, Nguyen D. Sustained weight loss in patients treated with mifepristone for Cushing's syndrome: a follow-up analysis of the SEISMIC study and long-term extension. BMC Endocr Disord. 2015 Oct 27;15:63. doi: 10.1186/s12902-015-0059-5.

  • Fleseriu M, Findling JW, Koch CA, Schlaffer SM, Buchfelder M, Gross C. Changes in plasma ACTH levels and corticotroph tumor size in patients with Cushing's disease during long-term treatment with the glucocorticoid receptor antagonist mifepristone. J Clin Endocrinol Metab. 2014 Oct;99(10):3718-27. doi: 10.1210/jc.2014-1843. Epub 2014 Jul 11.

  • Wallia A, Colleran K, Purnell JQ, Gross C, Molitch ME. Improvement in insulin sensitivity during mifepristone treatment of Cushing syndrome: early and late effects. Diabetes Care. 2013 Sep;36(9):e147-8. doi: 10.2337/dc13-0246. No abstract available.

Related Links

MeSH Terms

Conditions

Cushing SyndromePituitary ACTH HypersecretionPituitary DiseasesChoristomaACTH Syndrome, EctopicAdrenal Cortex NeoplasmsHirsutism

Interventions

MifepristoneCorlux

Condition Hierarchy (Ancestors)

Adrenocortical HyperfunctionAdrenal Gland DiseasesEndocrine System DiseasesHyperpituitarismHypothalamic DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesPathological Conditions, AnatomicalPathological Conditions, Signs and SymptomsParaneoplastic Endocrine SyndromesParaneoplastic SyndromesNeoplasmsAdrenal Gland NeoplasmsEndocrine Gland NeoplasmsNeoplasms by SiteAdrenal Cortex DiseasesHair DiseasesSkin DiseasesSkin and Connective Tissue DiseasesVirilismSigns and Symptoms

Intervention Hierarchy (Ancestors)

EstrenesEstranesSteroidsFused-Ring CompoundsPolycyclic Compounds

Results Point of Contact

Title
Medical Director
Organization
Corcept Therapeutics

Study Officials

  • Coleman Gross

    Corcept Therapeutics

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
GT60
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 3
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

December 5, 2007

First Posted

December 7, 2007

Study Start

December 1, 2007

Primary Completion

January 1, 2011

Last Updated

August 22, 2013

Results First Posted

May 28, 2012

Record last verified: 2013-08

Locations