NCT00528801

Brief Summary

Sickle cell disease (SCD), also known as sickle cell anemia, is an inherited blood disease that can cause intense pain episodes and may lead to organ failure. Preliminary studies have shown that adults with SCD may have brain abnormalities that contribute to problems with cognitive functioning, including attention and memory difficulties. This study will use brain magnetic resonance imaging (MRI) and neuropsychological testing to examine the differences in cognitive functioning in adults with SCD and adults without SCD. 212 subjects participated in this cross-sectional study consisting of screening questionnaires, a neuropsychological testing battery, and MRI testing. Enrollment into this study ended in May 2008.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
212

participants targeted

Target at P75+ for all trials

Timeline
Completed

Started Dec 2004

Typical duration for all trials

Geographic Reach
1 country

12 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

December 1, 2004

Completed
2.8 years until next milestone

First Submitted

Initial submission to the registry

September 10, 2007

Completed
2 days until next milestone

First Posted

Study publicly available on registry

September 12, 2007

Completed
8 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

May 1, 2008

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2008

Completed
1.6 years until next milestone

Results Posted

Study results publicly available

November 26, 2009

Completed
Last Updated

March 21, 2017

Status Verified

February 1, 2017

Enrollment Period

3.4 years

First QC Date

September 10, 2007

Results QC Date

August 28, 2009

Last Update Submit

February 14, 2017

Conditions

Keywords

Sickle Cell DiseaseSickle Cell AnemiaHemoglobin SSHemoglobin SB0

Outcome Measures

Primary Outcomes (1)

  • Wechsler Adult Intelligence Scale (WAIS)-III Performance IQ

    Extent of neurocognitive dysfunction in neurologically asymptomatic adult patients with sickle cell disease as measured by WAIS-III performance IQ. This quotient is based on an average of 100, with a standard deviation of 15. The Wechsler intelligence scales are not considered adequate measures of extremely high and low intelligence (IQ scores above 160 and below 40, respectively). The performance IQ is derived from scores on seven subtests: picture completion, picture arrangement, block design, object assembly, digit symbol, matrix reasoning, and symbol search.

    Within 2 months of signing informed consent.

Secondary Outcomes (2)

  • Participants With Brain Lacunae as Measured by Clinical MRI

    Within 2 months of informed consent

  • Volume of Total Cortical Gray Matter as Measured by Volumetric MRI.

    Within 2 months of informed consent

Study Arms (2)

Cases (CLOSED)

These are patients diagnosed with sickle cell disease (confirmed by hemoglobin electrophoresis).

Behavioral: NP BatteryProcedure: MRI

Controls (CLOSED)

These are persons that do not have sickle cell disease (confirmed by hemoglobin electrophoresis); matched to cases by age, gender, and education level

Behavioral: NP BatteryProcedure: MRI

Interventions

NP BatteryBEHAVIORAL

Neuropsych Battery with 7 different tests that evaluate the patients neurological functioning.

Also known as: The Weschler Adult Intelligence Scale - Third Edition, The Woodcock Johnson Revised - Test of Achievement, The Delis-Kaplan Function System, The Wisconsin Card Sorting test, The Test of Everday Attention, The California Verbal Learning Test, The Weschler Memory Scales - Third Edition
Cases (CLOSED)Controls (CLOSED)
MRIPROCEDURE

The MRI is a standard procedure involving 30 minutes under the machine in order to obtain various images of the patients brain.

Cases (CLOSED)Controls (CLOSED)

Eligibility Criteria

Age21 Years - 55 Years
Sexall
Healthy VolunteersYes
Age GroupsAdult (18-64)
Sampling MethodNon-Probability Sample
Study Population

212 participants, 160 will have sickle cell anemia, 52 will be matched controls based on gender, age, and education level

You may qualify if:

  • Individuals who meet all of the following criteria are eligible for enrollment as cases into the study:
  • Adult between the ages of 21 and 55
  • African descent
  • Proficient/fluent in English
  • Hemoglobin electrophoresis confirming hemoglobin SS or SB0 (%A \<= 15)
  • Hemoglobin \<= 10 g/dL
  • Capable of giving informed consent for the protocol
  • Individuals who meet all of the following criteria are eligible for enrollment as community controls into the study:
  • Adult between the ages of 21 and 55
  • African descent
  • Proficient/fluent in English
  • Capable of giving informed consent for the protocol

You may not qualify if:

  • Individuals who meet any of the following criteria are disqualified from enrollment in the case group of the study:
  • Overt stroke
  • Previous evidence of an abnormal MRI or CT other than small peri-ventricular or watershed lesions
  • History of head injury that resulted in neurological symptoms or medical visit
  • Abnormal neurologic exam with focal findings
  • Mini-Mental Status Examination (MMSE) score of \< 20
  • Profile of Mood States (POMS) score on the Depression-Dejection Subscale suggestive of a clinical depression (score \> 40)
  • Alcohol consumption exceeding 14 drinks/week if female, 21 drinks/week if male
  • Drug abuse, defined as using non-prescribed medication
  • History of claustrophobia and/or presence of metallic implants such as pacemakers, surgical aneurysm clips, or known metal fragments embedded in the body
  • Pregnancy
  • Baseline blood pressure \> 140/90 on two repeated measurements. A second measurement is needed only if the first is \> 140/90
  • History of uncontrolled hypertension
  • Any chronic disorder that may result in neurocognitive or brain dysfunction that is not secondary to SCD including:
  • Inflammatory arterial disorders (lupus, polyarteritis)
  • +49 more criteria

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (12)

University of Southern California

Los Angeles, California, 90033, United States

Location

Children's Hospital & Research Center at Oakland

Oakland, California, 94609, United States

Location

Memorial Cancer Institute

Hollywood, Florida, 33021, United States

Location

University of Miami Miller School of Medicine

Miami, Florida, 33136, United States

Location

Medical College of Georgia

Augusta, Georgia, 30912, United States

Location

Boston Medical Center

Boston, Massachusetts, 02118, United States

Location

University of North Carolina at Chapel Hill

Chapel Hill, North Carolina, 27599, United States

Location

Duke University Medical Center

Durham, North Carolina, 27705, United States

Location

Cincinnati Children's Hospital

Cincinnati, Ohio, 45229, United States

Location

University of Cincinnati Medical Center

Cincinnati, Ohio, 45267, United States

Location

Children's Medical Center at Dallas

Dallas, Texas, 75390, United States

Location

University of Texas Medical Branch

Galveston, Texas, 77555, United States

Location

MeSH Terms

Conditions

Anemia, Sickle Cell

Condition Hierarchy (Ancestors)

Anemia, Hemolytic, CongenitalAnemia, HemolyticAnemiaHematologic DiseasesHemic and Lymphatic DiseasesHemoglobinopathiesGenetic Diseases, InbornCongenital, Hereditary, and Neonatal Diseases and Abnormalities

Limitations and Caveats

As a cross-sectional study, follow-up of patients not included. Age range of cases and controls not weighted enough to include elder population. Functional or perfusion brain measures not included. Biologic and genetic risk factors not included.

Results Point of Contact

Title
Elliott Vichinsky, MD
Organization
Children's Hospital of Oakland and Research Institute

Study Officials

  • Elliott Vichinsky, MD

    Northern California CSCC (Children's Hospital Oakland)

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
observational
Observational Model
CASE CONTROL
Time Perspective
CROSS SECTIONAL
Sponsor Type
OTHER

Study Record Dates

First Submitted

September 10, 2007

First Posted

September 12, 2007

Study Start

December 1, 2004

Primary Completion

May 1, 2008

Study Completion

May 1, 2008

Last Updated

March 21, 2017

Results First Posted

November 26, 2009

Record last verified: 2017-02

Locations