NCT00471211

Brief Summary

The purpose of the study is to determine the safety, tolerability and efficacy of 2 doses of PBT2 administered for 12 weeks compared to placebo in patients with early Alzheimer's disease treated with an acetylcholinesterase inhibitor.

Trial Health

90
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
80

participants targeted

Target at P50-P75 for phase_2

Timeline
Completed

Started Dec 2006

Shorter than P25 for phase_2

Geographic Reach
2 countries

15 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

December 1, 2006

Completed
5 months until next milestone

First Submitted

Initial submission to the registry

May 8, 2007

Completed
1 day until next milestone

First Posted

Study publicly available on registry

May 9, 2007

Completed
7 months until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2007

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2007

Completed
Last Updated

January 16, 2008

Status Verified

January 1, 2008

Enrollment Period

1 year

First QC Date

May 8, 2007

Last Update Submit

January 13, 2008

Conditions

Outcome Measures

Primary Outcomes (1)

  • Safety

    Study duration

Secondary Outcomes (1)

  • Change from baseline in biomarkers; Change from baseline in cognitive and global function scales

    Study duration

Interventions

PBT2DRUG

Eligibility Criteria

Age56 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • diagnosis of probable early Alzheimer's disease
  • stable dose of acetylcholinesterase inhibitor
  • community dwelling
  • stable medical condition

You may not qualify if:

  • unstable and significant medical conditions
  • recurrent major psychiatric disorder
  • treatment with memantine

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (15)

Unknown Facility

Sydney, New South Wales, 2031, Australia

Location

Unknown Facility

Sydney, New South Wales, 2077, Australia

Location

Unknown Facility

Adelaide, South Australia, 5011, Australia

Location

Unknown Facility

Melbourne, Victoria, 3081, Australia

Location

Unknown Facility

Melbourne, Victoria, 3101, Australia

Location

Unknown Facility

Melbourne, Victoria, 3146, Australia

Location

Unknown Facility

Melbourne, Victoria, 3199, Australia

Location

Unknown Facility

Falköping, 521 85, Sweden

Location

Unknown Facility

Kalix, 952 81, Sweden

Location

Unknown Facility

Kalmar, 391 85, Sweden

Location

Unknown Facility

Lund, 85, Sweden

Location

Unknown Facility

Malmo, 205 20, Sweden

Location

Unknown Facility

Stockholm, 112 98, Sweden

Location

Unknown Facility

Umeå, 901 85, Sweden

Location

Unknown Facility

Uppsala, 751 85, Sweden

Location

Related Publications (1)

  • Lannfelt L, Blennow K, Zetterberg H, Batsman S, Ames D, Harrison J, Masters CL, Targum S, Bush AI, Murdoch R, Wilson J, Ritchie CW; PBT2-201-EURO study group. Safety, efficacy, and biomarker findings of PBT2 in targeting Abeta as a modifying therapy for Alzheimer's disease: a phase IIa, double-blind, randomised, placebo-controlled trial. Lancet Neurol. 2008 Sep;7(9):779-86. doi: 10.1016/S1474-4422(08)70167-4. Epub 2008 Jul 30.

MeSH Terms

Conditions

Alzheimer Disease

Condition Hierarchy (Ancestors)

DementiaBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesTauopathiesNeurodegenerative DiseasesNeurocognitive DisordersMental Disorders

Study Officials

  • Lars Lannfelt, Professor

    Uppsala University Hospital, Sweden

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
DOUBLE
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY

Study Record Dates

First Submitted

May 8, 2007

First Posted

May 9, 2007

Study Start

December 1, 2006

Primary Completion

December 1, 2007

Study Completion

December 1, 2007

Last Updated

January 16, 2008

Record last verified: 2008-01

Locations