NCT00456365

Brief Summary

The purpose of this study is to determine whether the medication pravastatin will ameliorate renal and cardiovascular disease over a 3-year period in children and young adults with autosomal dominant polycystic kidney disease (ADPKD).

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
110

participants targeted

Target at P25-P50 for phase_3

Timeline
Completed

Started Nov 2006

Longer than P75 for phase_3

Geographic Reach
1 country

1 active site

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

November 1, 2006

Completed
4 months until next milestone

First Submitted

Initial submission to the registry

March 12, 2007

Completed
23 days until next milestone

First Posted

Study publicly available on registry

April 4, 2007

Completed
5.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2012

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

October 1, 2012

Completed
5.4 years until next milestone

Results Posted

Study results publicly available

March 9, 2018

Completed
Last Updated

March 9, 2018

Status Verified

February 1, 2018

Enrollment Period

5.9 years

First QC Date

March 12, 2007

Results QC Date

May 27, 2014

Last Update Submit

February 8, 2018

Conditions

Keywords

Autosomal dominant polycystic kidney diseaseCystic kidney diseaseHigh blood pressureStatin

Outcome Measures

Primary Outcomes (1)

  • Percent of Participants Demonstrating 20% or More Increase in Total Kidney Volume

    Percent of participants demonstrating 20% or more increase in total kidney volume corrected for height, left ventricular mass index, or urinary albumin excretion over the three year study period

    3 years

Secondary Outcomes (3)

  • Percentage Change in Total Kidney Volume Corrected for Height

    3 years

  • Left Ventricular Mass Index

    3 years

  • Urinary Albumin Excretion

    3 years

Study Arms (2)

Pravastatin

EXPERIMENTAL

Pravastatin

Drug: pravastatin

Placebo

PLACEBO COMPARATOR

Placebo

Drug: Placebo

Interventions

Pravastatin 20 mg daily (subject age 8-12 years) or 40 mg daily (subject age 13-21 years)

Pravastatin

Placebo daily

Placebo

Eligibility Criteria

Age8 Years - 22 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • Age 8-22 years
  • Autosomal dominant polycystic kidney disease
  • Normal kidney function

You may not qualify if:

  • Abnormal kidney function
  • Past allergic history to medications used in study
  • Liver disease
  • Muscle disease/dystrophy
  • Pregnancy, planned pregnancy, or lactation within study period
  • Inability to cooperate with or clinical contraindication for magnetic resonance imaging

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

University of Colorado at Denver and Health Sciences Center

Denver, Colorado, 80262, United States

Location

Related Publications (7)

  • Schrier RW. Optimal care of autosomal dominant polycystic kidney disease patients. Nephrology (Carlton). 2006 Apr;11(2):124-30. doi: 10.1111/j.1440-1797.2006.00535.x.

    PMID: 16669974BACKGROUND
  • Shamshirsaz AA, Reza Bekheirnia M, Kamgar M, Johnson AM, McFann K, Cadnapaphornchai M, Nobakhthaghighi N, Schrier RW. Autosomal-dominant polycystic kidney disease in infancy and childhood: progression and outcome. Kidney Int. 2005 Nov;68(5):2218-24. doi: 10.1111/j.1523-1755.2005.00678.x.

    PMID: 16221221BACKGROUND
  • Taylor M, Johnson AM, Tison M, Fain P, Schrier RW. Earlier diagnosis of autosomal dominant polycystic kidney disease: importance of family history and implications for cardiovascular and renal complications. Am J Kidney Dis. 2005 Sep;46(3):415-23. doi: 10.1053/j.ajkd.2005.05.029.

    PMID: 16129202BACKGROUND
  • Cadnapaphornchai MA, Fick-Brosnahan GM, Duley I, Johnson AM, Strain JD, DeGroff CG, Schrier RW. Design and baseline characteristics of participants in the study of antihypertensive therapy in children and adolescents with autosomal dominant polycystic kidney disease (ADPKD). Contemp Clin Trials. 2005 Apr;26(2):211-22. doi: 10.1016/j.cct.2005.01.001.

    PMID: 15837441BACKGROUND
  • Fick-Brosnahan GM, Belz MM, McFann KK, Johnson AM, Schrier RW. Relationship between renal volume growth and renal function in autosomal dominant polycystic kidney disease: a longitudinal study. Am J Kidney Dis. 2002 Jun;39(6):1127-34. doi: 10.1053/ajkd.2002.33379.

    PMID: 12046022BACKGROUND
  • Kelleher CL, McFann KK, Johnson AM, Schrier RW. Characteristics of hypertension in young adults with autosomal dominant polycystic kidney disease compared with the general U.S. population. Am J Hypertens. 2004 Nov;17(11 Pt 1):1029-34. doi: 10.1016/j.amjhyper.2004.06.020.

    PMID: 15533729BACKGROUND
  • St Pierre K, Cashmore BA, Bolignano D, Zoccali C, Ruospo M, Craig JC, Strippoli GF, Mallett AJ, Green SC, Tunnicliffe DJ. Interventions for preventing the progression of autosomal dominant polycystic kidney disease. Cochrane Database Syst Rev. 2024 Oct 2;10(10):CD010294. doi: 10.1002/14651858.CD010294.pub3.

Related Links

MeSH Terms

Conditions

Polycystic Kidney, Autosomal DominantKidney Diseases, CysticHypertension

Interventions

Pravastatin

Condition Hierarchy (Ancestors)

Polycystic Kidney DiseasesKidney DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesAbnormalities, MultipleCongenital AbnormalitiesCongenital, Hereditary, and Neonatal Diseases and AbnormalitiesCiliopathiesGenetic Diseases, InbornVascular DiseasesCardiovascular Diseases

Intervention Hierarchy (Ancestors)

NaphthalenesPolycyclic Aromatic HydrocarbonsHydrocarbons, AromaticHydrocarbons, CyclicHydrocarbonsOrganic ChemicalsPolycyclic Compounds

Results Point of Contact

Title
Melissa Cadnapaphornchai, MD
Organization
PKD Research Group, University of Colorado Anschutz Medical Campus

Study Officials

  • Melissa A Cadnapaphornchai, MD

    University of Colorado, Denver

    PRINCIPAL INVESTIGATOR
  • Robert W Schrier, MD

    University of Colorado, Denver

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
SPONSOR

Study Record Dates

First Submitted

March 12, 2007

First Posted

April 4, 2007

Study Start

November 1, 2006

Primary Completion

October 1, 2012

Study Completion

October 1, 2012

Last Updated

March 9, 2018

Results First Posted

March 9, 2018

Record last verified: 2018-02

Data Sharing

IPD Sharing
Will not share

Locations