NCT00449865

Brief Summary

The purpose of this trial is to determine if the nutritional supplement creatine slows the progression of Parkinson's disease over time.

Trial Health

60
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
1,741

participants targeted

Target at P75+ for phase_3

Timeline
Completed

Started Mar 2007

Longer than P75 for phase_3

Geographic Reach
2 countries

50 active sites

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

March 1, 2007

Completed
19 days until next milestone

First Submitted

Initial submission to the registry

March 20, 2007

Completed
1 day until next milestone

First Posted

Study publicly available on registry

March 21, 2007

Completed
6.5 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

September 1, 2013

Completed
8 months until next milestone

Study Completion

Last participant's last visit for all outcomes

May 1, 2014

Completed
11 months until next milestone

Results Posted

Study results publicly available

April 2, 2015

Completed
Last Updated

April 2, 2015

Status Verified

March 1, 2015

Enrollment Period

6.5 years

First QC Date

March 20, 2007

Results QC Date

February 19, 2015

Last Update Submit

March 23, 2015

Conditions

Keywords

Parkinson's diseasecreatineNET-PDneuroprotectionPD

Outcome Measures

Primary Outcomes (1)

  • The Global Outcome Combined Information on Change From Baseline in Schwab England Activities of Daily Living, 39-Item Parkinson's Disease Questionnaire, Ambulatory Capacity, Symbol Digit Modalities, and Modified Rankin at 5 Years.

    All outcomes were coded such that higher scores indicated worse outcomes. Patients were ranked on each outcome and their ranks were summed (summed-ranks). Higher summed ranks (range, 5-4775) indicate worse outcomes. The mean summed ranks were compared by treatment group by a global statistical test (GST).

    Change from baseline to 5 YEARS

Study Arms (2)

Placebo

PLACEBO COMPARATOR
Other: placebo

creatine

ACTIVE COMPARATOR
Drug: creatine

Interventions

Creatine, a widely used dietary supplement is thought to improve exercise performance. In animal models and human studies, creatine has been shown to be well tolerated and may have some ability to protect brain cells. The study is comparing creatine 5 grams twice daily with placebo.

creatine
placeboOTHER

an inactive substance

Placebo

Eligibility Criteria

Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64), Older Adult (65+)

You may qualify if:

  • Willing and able to give informed consent and willing to commit to long-term follow-up
  • PD (asymmetric features including slowness (bradykinesia) plus resting tremor and/or rigidity) within 5 years of diagnosis
  • Treated/responsive to dopaminergic therapy (dopamine agonists or levodopa) for at least 90 days, but not more than 2 years.

You may not qualify if:

  • Use of creatine 14 days prior to baseline or during the study
  • History of known hypersensitivity or intolerability to creatine
  • Any unstable or clinically significant condition that would impair the subject's ability to comply with long term study follow-up
  • Other know or suspected causes of parkinsonism (e.g. metabolic, drug induced, etc.), or any significant features suggestive of a diagnosis of atypical parkinsonism.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (50)

University Of Alabama, Birmingham, 350 Sparks Center, 1720 7th Avenue South

Birmingham, Alabama, 35233, United States

Location

Barrow Neurological Clinics At, St Joseph's Hospital & Medical Center, 500 West Thomas Road Suite 720,

Phoenix, Arizona, 85013, United States

Location

Parkinson's & Movement Disorder Institute, 9940 Talbert Avenue, Suite 204,

Fountain Valley, California, 92708, United States

Location

University Of Southern California, Healthcare Consultation Building II, 1520 San Pablo Street Suite 3000

Los Angeles, California, 90033, United States

Location

University Of California San Francisco, Parkinson's Disease Clinic And Research Cen, 505 Parnassus Avenue M-798

San Francisco, California, 94143-0114, United States

Location

The Parkinson's Institute, 675 Almanor Avenue

Sunnyvale, California, 94085, United States

Location

University Of Colorado Health Sciences Ctr, 4200 East 9th Avenue Campus Box C238, Department Of Clinical Pharmacy

Denver, Colorado, 80262, United States

Location

Neurodegenerative Disorders, 60 Temple Street Suite 8b

New Haven, Connecticut, 06510, United States

Location

VA Medical Center, 1601 Southwest Archer Road, Neurology Service (151)

Gainesville, Florida, 32608, United States

Location

University Of Florida, Mcknight Brain Institute, 100 South Newell Drive Room L3-100

Gainesville, Florida, 32610, United States

Location

University Of Florida Jacksonville, 580 West 8th Street, Tower 1 8th Floor,

Jacksonville, Florida, 32209, United States

Location

University Of Miami, 1501 North West 9th Avenue Second Floor, Department Of Neurology D4-5

Miami, Florida, 33136, United States

Location

University Of South Florida, Movement Disorders Center, 5 Tampa General Circle Suite 410

Tampa, Florida, 33606, United States

Location

Emory University, Wesley Woods Health Center, 1841 Clifton Road NE Room 328

Atlanta, Georgia, 30329, United States

Location

Medical College Of Georgia, Movement Disorders Clinic, 1429 Harper Street HF 1121

Augusta, Georgia, 30912, United States

Location

Pacific Health Research Institute, 405 North Kuakini Street, Suite 1011,

Honolulu, Hawaii, 96817, United States

Location

Northwestern University, 710 North Lake Shore Drive

Chicago, Illinois, 60611, United States

Location

Rush University Medical Center, Department Of Neurological Sciences, 1725 West Harrison Suite 755,

Chicago, Illinois, 60612, United States

Location

Evanston Northwestern Healthcare, Department Of Neurology, 2100 Pfingsten Road Suite B110

Glenview, Illinois, 60026, United States

Location

Southern Illinois University School Of Medicine, PO Box 19645

Springfield, Illinois, 62794-9645, United States

Location

Indiana University School Of Medicine, Outpatient Clinical Research Facility, 535 Barnhill Drive Room #150

Indianapolis, Indiana, 46202, United States

Location

University Of Kansas Medical Center, 3599 Rainbow Blvd, Department Of Neurology Mail Stop # 2012

Kansas City, Kansas, 66160-7314, United States

Location

University Of Kentucky Clinical Research, C201 Kentucky Clinic, 740 South Limestone Street

Lexington, Kentucky, 40536-0284, United States

Location

Ochsner Clinic Foundation, 1514 Jefferson Highway, Dept. Of Neurology 7th Floor

New Orleans, Louisiana, 70121, United States

Location

LSU Health Science Center Shreveport, 1501 Kings Highway, Room 3-436

Shreveport, Louisiana, 71130, United States

Location

University Of Maryland School Of Medicine, Department Of Neurology, 22 South Greene Street N4W46

Baltimore, Maryland, 21201, United States

Location

Johns Hopkins University, 601 North Caroline Street, Suite 5064

Baltimore, Maryland, 21287-0875, United States

Location

Brigham & Women's Hospital, Neurology Department ASB2, 75 Francis Street

Boston, Massachusetts, 02115, United States

Location

Beth Israel Deaconess Medical Center, 330 Brookline Avenue Shapiro 809D

Boston, Massachusetts, 02215, United States

Location

University Of Michigan, 1500 E Medical Center Drive, B1 H202 Nuclear Medicine,

Ann Arbor, Michigan, 48109-0028, United States

Location

Michigan State University, Department Of Neurology A217 Clinical Center, 138 Service Road

East Lansing, Michigan, 48824, United States

Location

Struthers Parkinson's Center, 6701 Country Club Drive,

Golden Valley, Minnesota, 55427, United States

Location

Washington University School Of Medicine, 660 South Euclid Avenue, Campus 8111,

St Louis, Missouri, 63110, United States

Location

Dartmouth Hitchcock Medical Center, One Medical Center Drive, 2 Buck Road

Lebanon, New Hampshire, 03756, United States

Location

UMDNJ Robert Wood Johnson Medical School, Dept Of Neurology Suite 6100, 125 Paterson Street

New Brunswick, New Jersey, 08901, United States

Location

SUNY Downstate Medical Center, 450 Clarkson Avenue, Department Of Neurology Box 1213

Brooklyn, New York, 11203-2098, United States

Location

Northshore-LIJ Health System, The Feinstein Institute FPR Medical Research, 350 Community Drive Room,

Manhasset, New York, 11030, United States

Location

Duke University Medical Center, Duke Health Center At Morreene Road, 932 Morreene Road Room 213,

Durham, North Carolina, 27705, United States

Location

OHSU Oregon Health &Science University, Department Of Neurology, 3181 South West Sam Jackson Park Road

Portland, Oregon, 97239, United States

Location

Thomas Jefferson University, 1015 Chestnut Street Suite 520

Philadelphia, Pennsylvania, 19107, United States

Location

University of Pennsylvania; Pennsylvania Hospital, Penn Neurological Institute, 330 South Ninth Street

Philadelphia, Pennsylvania, 19107, United States

Location

Thomas Jefferson University/Lankenau Hospital, Lankenau Medical Building Suite 161 East, 100 Lancaster Avenue

Wynnewood, Pennsylvania, 19096, United States

Location

Medical University Of South Carolina, Charleston Memorial Hospital, 326 Calhoun Street Suite 308

Charleston, South Carolina, 29401, United States

Location

Vanderbilt University Medical Center, 2311 Pierce Avenue, Room 2217,

Nashville, Tennessee, 37212, United States

Location

University Of Texas Southwestern Med Ctr. At Dallas, 5323 Harry Hines Boulevard H1-108

Dallas, Texas, 75390-9016, United States

Location

Baylor College Of Medicine, 6550 Fannin Suite 1801

Houston, Texas, 77030, United States

Location

University Of Vermont, Department Of Neurology , Given Building C-219, 89 Beaumont Avenue

Burlington, Vermont, 05405, United States

Location

University Of Virginia Neurology Fontaine, Department Of Neurology, 500 Ray C Hunt Drive

Charlottesville, Virginia, 22903, United States

Location

University Of Calgary Movement Disorders Program, Dept Of Clin Neurosciences Area 3 Neurology, 3350 Hospital DR NW Health Sciences Centre

Calgary, Alberta, T2N4NI, Canada

Location

University Of Alberta, 10230-111 Avenue Room 0601, Movement Disorders Clinic Glenrose Rehab Hospital

Edmonton, Alberta, T5G 0B7, Canada

Location

Related Publications (5)

  • Leehey M, Luo S, Sharma S, Wills AA, Bainbridge JL, Wong PS, Simon DK, Schneider J, Zhang Y, Perez A, Dhall R, Christine CW, Singer C, Cambi F, Boyd JT. Association of metabolic syndrome and change in Unified Parkinson's Disease Rating Scale scores. Neurology. 2017 Oct 24;89(17):1789-1794. doi: 10.1212/WNL.0000000000004572. Epub 2017 Sep 29.

  • Wills AM, Li R, Perez A, Ren X, Boyd J; NINDS NET-PD Investigators. Predictors of weight loss in early treated Parkinson's disease from the NET-PD LS-1 cohort. J Neurol. 2017 Aug;264(8):1746-1753. doi: 10.1007/s00415-017-8562-4. Epub 2017 Jul 15.

  • Augustine EF, Dorsey ER, Hauser RA, Elm JJ, Tilley BC, Kieburtz KK. Communicating with participants during the conduct of multi-center clinical trials. Clin Trials. 2016 Dec;13(6):592-596. doi: 10.1177/1740774516665596. Epub 2016 Aug 29.

  • Wills AM, Perez A, Wang J, Su X, Morgan J, Rajan SS, Leehey MA, Pontone GM, Chou KL, Umeh C, Mari Z, Boyd J; NINDS Exploratory Trials in Parkinson Disease (NET-PD) Investigators. Association Between Change in Body Mass Index, Unified Parkinson's Disease Rating Scale Scores, and Survival Among Persons With Parkinson Disease: Secondary Analysis of Longitudinal Data From NINDS Exploratory Trials in Parkinson Disease Long-term Study 1. JAMA Neurol. 2016 Mar;73(3):321-8. doi: 10.1001/jamaneurol.2015.4265.

  • Writing Group for the NINDS Exploratory Trials in Parkinson Disease (NET-PD) Investigators; Kieburtz K, Tilley BC, Elm JJ, Babcock D, Hauser R, Ross GW, Augustine AH, Augustine EU, Aminoff MJ, Bodis-Wollner IG, Boyd J, Cambi F, Chou K, Christine CW, Cines M, Dahodwala N, Derwent L, Dewey RB Jr, Hawthorne K, Houghton DJ, Kamp C, Leehey M, Lew MF, Liang GS, Luo ST, Mari Z, Morgan JC, Parashos S, Perez A, Petrovitch H, Rajan S, Reichwein S, Roth JT, Schneider JS, Shannon KM, Simon DK, Simuni T, Singer C, Sudarsky L, Tanner CM, Umeh CC, Williams K, Wills AM. Effect of creatine monohydrate on clinical progression in patients with Parkinson disease: a randomized clinical trial. JAMA. 2015 Feb 10;313(6):584-93. doi: 10.1001/jama.2015.120.

Related Links

MeSH Terms

Conditions

Parkinson Disease

Interventions

Creatine

Condition Hierarchy (Ancestors)

Parkinsonian DisordersBasal Ganglia DiseasesBrain DiseasesCentral Nervous System DiseasesNervous System DiseasesMovement DisordersSynucleinopathiesNeurodegenerative Diseases

Intervention Hierarchy (Ancestors)

GuanidinesAmidinesOrganic ChemicalsAmino AcidsAmino Acids, Peptides, and Proteins

Results Point of Contact

Title
Karl Kieburtz, Director of CTSI
Organization
University of Rochester

Study Officials

  • Karl Kieburtz, MD

    Coordination Center

    PRINCIPAL INVESTIGATOR
  • Barbara Tilley, PhD

    Statistics Center

    PRINCIPAL INVESTIGATOR

Publication Agreements

PI is Sponsor Employee
No
Restrictive Agreement
No

Study Design

Study Type
interventional
Phase
phase 3
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
TREATMENT
Intervention Model
PARALLEL
Sponsor Type
OTHER
Responsible Party
PRINCIPAL INVESTIGATOR
PI Title
Principal Investigator

Study Record Dates

First Submitted

March 20, 2007

First Posted

March 21, 2007

Study Start

March 1, 2007

Primary Completion

September 1, 2013

Study Completion

May 1, 2014

Last Updated

April 2, 2015

Results First Posted

April 2, 2015

Record last verified: 2015-03

Locations