NCT00419120

Brief Summary

Subjects with neurogenic bladder secondary to spina bifida refractory to medical treatment will be enrolled. The hypothesis is that augmentation cystoplasty using an autologous neo-bladder construct will significantly increase bladder compliance.

Trial Health

57
Monitor

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
10

participants targeted

Target at below P25 for phase_2

Timeline
Completed

Started Dec 2006

Typical duration for phase_2

Geographic Reach
1 country

1 active site

Status
terminated

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

December 1, 2006

Completed
1 month until next milestone

First Submitted

Initial submission to the registry

January 4, 2007

Completed
4 days until next milestone

First Posted

Study publicly available on registry

January 8, 2007

Completed
1.7 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

October 1, 2008

Completed
1.7 years until next milestone

Results Posted

Study results publicly available

June 7, 2010

Completed
10 months until next milestone

Study Completion

Last participant's last visit for all outcomes

April 1, 2011

Completed
Last Updated

November 30, 2015

Status Verified

November 1, 2015

Enrollment Period

1.8 years

First QC Date

January 4, 2007

Results QC Date

December 8, 2009

Last Update Submit

November 2, 2015

Conditions

Outcome Measures

Primary Outcomes (1)

  • Number of Responders as Assessed by Compliance

    Efficacy of the autologous neo-bladder construct as assessed by a responder analysis (comparing each patient's baseline with 12 month data). Improvement in compliance (i.e. improved bladder pressure/volume relationship) was measured by urodynamics at predetermined bladder pressure points. This was coupled with an assessment of clinical benefit and used to determine responders versus non-responders

    12 months

Secondary Outcomes (1)

  • Overall Safety Profile - Number of Participants Experiencing an Adverse Event

    periodically within first 12 months as well as during long term follow up out to 5 years

Study Arms (1)

Neo-bladder construction

EXPERIMENTAL

Surgical implantation of autologous neo-bladder construct

Biological: Autologous neo bladder construct

Interventions

augmentation cystoplasty with autologous neo-bladder construct

Neo-bladder construction

Eligibility Criteria

Age3 Years - 21 Years
Sexall
Healthy VolunteersNo
Age GroupsChild (0-17), Adult (18-64)

You may qualify if:

  • subjects with neurogenic bladders secondary to myleodysplasia

You may not qualify if:

  • prior augment procedures
  • recent urologic surgery
  • requires concomitant urologic intervention

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (1)

Boston Childrens Hospital

Boston, Massachusetts, 02115, United States

Location

MeSH Terms

Conditions

Urinary Bladder, Neurogenic

Condition Hierarchy (Ancestors)

Neurologic ManifestationsNervous System DiseasesUrinary Bladder DiseasesUrologic DiseasesFemale Urogenital DiseasesFemale Urogenital Diseases and Pregnancy ComplicationsUrogenital DiseasesMale Urogenital DiseasesSigns and SymptomsPathological Conditions, Signs and Symptoms

Results Point of Contact

Title
Sunita Sheth, MD - Chief Medical Officer
Organization
Tengion, Inc.

Study Officials

  • Sunita Sheth, MD

    Tengion, Inc.

    STUDY DIRECTOR

Publication Agreements

PI is Sponsor Employee
No
Restriction Type
OTHER
Restrictive Agreement
Yes

Study Design

Study Type
interventional
Phase
phase 2
Allocation
NA
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

January 4, 2007

First Posted

January 8, 2007

Study Start

December 1, 2006

Primary Completion

October 1, 2008

Study Completion

April 1, 2011

Last Updated

November 30, 2015

Results First Posted

June 7, 2010

Record last verified: 2015-11

Locations