NCT00389428

Brief Summary

The primary objective of this study is to determine the recommended dose of CPX-351 for use in a phase 2 efficacy study in patients with leukemia. Secondarily, the study will assess the safety, serious adverse effects and how the body handles CPX-351. Preliminary evidence of antitumor activity will also be determined.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
48

participants targeted

Target at P50-P75 for phase_1

Timeline
Completed

Started Sep 2006

Typical duration for phase_1

Geographic Reach
1 country

4 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

September 1, 2006

Completed
2 months until next milestone

First Submitted

Initial submission to the registry

October 16, 2006

Completed
2 days until next milestone

First Posted

Study publicly available on registry

October 18, 2006

Completed
2.1 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

December 1, 2008

Completed
1 year until next milestone

Study Completion

Last participant's last visit for all outcomes

December 1, 2009

Completed
Last Updated

May 17, 2012

Status Verified

May 1, 2012

Enrollment Period

2.3 years

First QC Date

October 16, 2006

Last Update Submit

May 16, 2012

Conditions

Keywords

Hematologic malignanciesMalignancies, hematologicHematopoietic malignancies

Outcome Measures

Primary Outcomes (1)

  • To determine the maximum tolerated dose (MTD) for use in phase 2

Secondary Outcomes (3)

  • To evaluate the safety and dose-limiting toxicities (DLT) of CPX-351.

  • To determine the pharmacokinetic parameters of CPX-351 administered in this schedule.

  • To assess preliminary efficacy information of CPX-351 administered in this schedule in patients with advanced leukemias.

Interventions

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Ability to understand and voluntarily sign an informed consent form
  • Age \> 18 years at the time of signing the informed consent form
  • Pathological confirmation of leukemia or myelodysplastic syndrome.
  • AML according to WHO criteria; except for core-binding factor AMLs (t(8;21), inv(16) or t(16;16)) and APL
  • ALL
  • MDS
  • Patients with AML include the following:
  • Patients in 2nd or greater relapse
  • Patients in first relapse with initial CR duration lasting \<6 months
  • Patients in first relapse refractory to induction therapy
  • Patients with primary refractory AML
  • Patients with ALL include the following
  • Patients with T-cell ALL refractory or in relapse following nelarabine
  • Patients with other ALL that is refractory or in relapse.
  • Patients with MDS include the following:
  • +11 more criteria

You may not qualify if:

  • Any serious medical condition, laboratory abnormality or psychiatric illness that would prevent the patient from signing the informed consent form
  • Chemotherapy or other investigational anticancer therapeutic drugs in the two weeks prior to study entry; in the event of rapidly proliferative disease, however, the use of hydroxyurea is permitted up to 24 hours before study entry
  • Clinical evidence of active CNS leukemic involvement
  • Pregnant or lactating women
  • Clinically significant cardiac disease (New York Heart Association Class III or IV)
  • Severe debilitating pulmonary disease
  • Active and uncontrolled infection. Patients with an infection under active treatment with antibiotics and whose infection is controlled may be entered into the study
  • Current evidence of invasive fungal infection (blood or tissue culture); HIV or hepatitis C infection
  • Hypersensitivity to cytarabine, daunorubicin or liposomal products
  • History of Wilson's disease or other copper-related disorder

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (4)

Georgetown University Medical Center

Washington D.C., District of Columbia, 20007, United States

Location

H. Lee Moffit Cancer Center & Research Institute at the University of S. Florida

Tampa, Florida, 33612-9497, United States

Location

North Shore University Hospital

Manhasset, New York, 11030, United States

Location

New York Presbyterian Hospital Weill Medical College of Cornell University

New York, New York, 10021, United States

Location

Related Publications (1)

  • Feldman EJ, Kolitz JE, Trang JM, Liboiron BD, Swenson CE, Chiarella MT, Mayer LD, Louie AC, Lancet JE. Pharmacokinetics of CPX-351; a nano-scale liposomal fixed molar ratio formulation of cytarabine:daunorubicin, in patients with advanced leukemia. Leuk Res. 2012 Oct;36(10):1283-9. doi: 10.1016/j.leukres.2012.07.006. Epub 2012 Jul 26.

MeSH Terms

Conditions

Hematologic Neoplasms

Interventions

CPX-351Liposomes

Condition Hierarchy (Ancestors)

Neoplasms by SiteNeoplasmsHematologic DiseasesHemic and Lymphatic Diseases

Intervention Hierarchy (Ancestors)

Membranes, ArtificialBiomedical and Dental MaterialsDrug CarriersDosage FormsPharmaceutical PreparationsManufactured MaterialsTechnology, Industry, and AgricultureBiomimetic Materials

Study Officials

  • Arthur Louie, M.D.

    Jazz Pharmaceuticals

    STUDY DIRECTOR
  • Jonathan Kolitz, M.D.

    New York School of Medicine at North Shore University Hospital

    PRINCIPAL INVESTIGATOR

Study Design

Study Type
interventional
Phase
phase 1
Allocation
NON RANDOMIZED
Masking
NONE
Purpose
TREATMENT
Intervention Model
SINGLE GROUP
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

October 16, 2006

First Posted

October 18, 2006

Study Start

September 1, 2006

Primary Completion

December 1, 2008

Study Completion

December 1, 2009

Last Updated

May 17, 2012

Record last verified: 2012-05

Locations