NCT00323518

Brief Summary

CG53135-05 (velafermin), a recombinant human fibroblast growth factor-20 (rhFGF-20) protein, is under investigation for the prevention of oral mucositis. Oral mucositis is a commonly occurring side effect of high-dose chemotherapy in patients undergoing autologous hematopoietic stem cell transplant. The objective of this Phase II trial is to confirm the safety and efficacy of CG53135-05 (velafermin) when administered as a single dose to patients at risk for developing oral mucositis.

Trial Health

87
On Track

Trial Health Score

Automated assessment based on enrollment pace, timeline, and geographic reach

Enrollment
390

participants targeted

Target at P75+ for phase_2

Timeline
Completed

Started May 2006

Geographic Reach
1 country

33 active sites

Status
completed

Health score is calculated from publicly available data and should be used for screening purposes only.

Trial Relationships

Click on a node to explore related trials.

Study Timeline

Key milestones and dates

Study Start

First participant enrolled

May 1, 2006

Completed
7 days until next milestone

First Submitted

Initial submission to the registry

May 8, 2006

Completed
1 day until next milestone

First Posted

Study publicly available on registry

May 9, 2006

Completed
2.2 years until next milestone

Primary Completion

Last participant's last visit for primary outcome

August 1, 2008

Completed
Same day until next milestone

Study Completion

Last participant's last visit for all outcomes

August 1, 2008

Completed
Last Updated

April 13, 2016

Status Verified

March 1, 2016

Enrollment Period

2.3 years

First QC Date

May 8, 2006

Last Update Submit

March 14, 2016

Conditions

Keywords

oral mucositishematologicautologous stem cell transplantvelaferminstomatitisoncology - supportive caremouth diseases

Outcome Measures

Primary Outcomes (1)

  • the incidence of grade 3/4 oral mucositis using WHO grading system

    evaluated throughout the study

Study Arms (4)

1

PLACEBO COMPARATOR

placebo

Drug: placebo

2

EXPERIMENTAL

30 mcg/kg velafermin

Drug: velafermin

3

EXPERIMENTAL

10 mcg/kg velafermin

Drug: velafermin

4

EXPERIMENTAL

60 mcg/kg velafermin

Drug: velafermin

Interventions

administered intravenously as 100mL single dose over 15 minutes on day 1

Also known as: CG53135-05
234

administered intravenously as 100mL single dose over 15 minutes on day 1

1

Eligibility Criteria

Age18 Years+
Sexall
Healthy VolunteersNo
Age GroupsAdult (18-64), Older Adult (65+)

You may qualify if:

  • Age 18 years or older
  • Patients with multiple myeloma or lymphoma receiving myeloablative CT with or without TBI that require autologous stem cell support. The CT regimens are limited to high dose melphalan (200 mg/m2) as a single agent, BEAM, or TBI with cyclophosphamide or VP-16.
  • Adequate organ function that meets institutional requirements for autologous stem cell transplant. A minimum CD34+ cell dose of 2X106 /kg based on ideal body weight (IBW) has been or will be infused.
  • ECOG Performance Score of 2 or less
  • Signed Informed Consent Form (ICF)

You may not qualify if:

  • Premenopausal female patients who are pregnant, lactating or are likely to become pregnant
  • Patients diagnosed with active sero-positive acquired immunodeficiency syndrome (AIDS) or Hepatitis B/ C
  • Patients with known hypersensitivity to recombinant protein therapeutics
  • Patients who have taken velafermin (CG53135-05) previously
  • Patients who have taken palifermin in the past 90 days
  • Patients who have taken other investigational drugs in the past 30 days
  • Patients who have untreated symptomatic dental infection
  • Patients with a history of sensitivity or allergy to E. coli-derived products
  • Patients with WHO Grade 3 or 4 OM at the time of randomization
  • Patients who are sensitive or allergic to G-CSF, Fluconazole or acyclovir or equivalent
  • Patients with altered mental status precluding understanding of the informed consent process and/or completion of the necessary assessments
  • Patients with baseline creatinine level greater than or equal to 3 or any patient with renal insufficiency requiring dialysis.

Contact the study team to confirm eligibility.

Sponsors & Collaborators

Study Sites (33)

University of Arkansas for Medical Sciences

Little Rock, Arkansas, 72205, United States

Location

Alta Bates Comprehensive Cancer Center

Berkley, California, 94704, United States

Location

Research Facility

La Jolla, California, 92037, United States

Location

Scripps Green Medical Center

La Jolla, California, 92037, United States

Location

University of Colorado Health Sciences Center

Aurora, Colorado, 80045, United States

Location

Rocky Mountain Blood and Marrow Transplant Program

Denver, Colorado, 80218, United States

Location

Emory University

Atlanta, Georgia, 30322, United States

Location

Northwestern University

Chicago, Illinois, 60611, United States

Location

Rush University Medical Center

Chicago, Illinois, 60612, United States

Location

St. Francis Hospital and Health Centers

Beech Grove, Indiana, 46107, United States

Location

Indiana University Cancer Center

Indianapolis, Indiana, 46202, United States

Location

University of Iowa Hospitals and Clinics

Iowa City, Iowa, 52242, United States

Location

University of Kansas Medical Center

Kansas City, Kansas, 66160, United States

Location

Louisiana State University Health Science Center

Shreveport, Louisiana, 71130, United States

Location

Wayne State University

Detroit, Michigan, 48201, United States

Location

MAYO Clinic

Rochester, Minnesota, 55905, United States

Location

Cancer Center at Hackensack University Medical Center

Hackensack, New Jersey, 07601, United States

Location

Cornell Medical Center

New York, New York, 10021, United States

Location

Biomedical Research Alliance of New York

New York, New York, 10029, United States

Location

Biomedical Research Alliance of New York

The Bronx, New York, 10467, United States

Location

University of North Carolina

Chapel Hill, North Carolina, 27599, United States

Location

Duke University Medical Center

Durham, North Carolina, 27710, United States

Location

Wake Forest University Health Sciences

Winston-Salem, North Carolina, 27157, United States

Location

University Hospitals of Cleveland

Cleveland, Ohio, 44106, United States

Location

University of Oklahoma

Oklahoma City, Oklahoma, 73104, United States

Location

Legacy Good Samaritan Hospital and Cancer Center

Portland, Oregon, 97227, United States

Location

Oregon Health and Science University

Portland, Oregon, 97239, United States

Location

Fox Chase-Temple Bone Marrow Transplant Program

Philadelphia, Pennsylvania, 19111, United States

Location

Roger Williams Medical Center

Providence, Rhode Island, 02908, United States

Location

Medical University of South Carolina Hollings Cancer Center

Charleston, South Carolina, 29425, United States

Location

Baylor University Medical Center

Dallas, Texas, 75246, United States

Location

University of Texas Health Science Center

San Antonio, Texas, 78229-3900, United States

Location

Medical College of Wisonsin

Milwaukee, Wisconsin, 53226, United States

Location

MeSH Terms

Conditions

StomatitisMouth Diseases

Interventions

FGF20 protein, human

Condition Hierarchy (Ancestors)

Stomatognathic Diseases

Study Design

Study Type
interventional
Phase
phase 2
Allocation
RANDOMIZED
Masking
QUADRUPLE
Who Masked
PARTICIPANT, CARE PROVIDER, INVESTIGATOR, OUTCOMES ASSESSOR
Purpose
PREVENTION
Intervention Model
PARALLEL
Sponsor Type
INDUSTRY
Responsible Party
SPONSOR

Study Record Dates

First Submitted

May 8, 2006

First Posted

May 9, 2006

Study Start

May 1, 2006

Primary Completion

August 1, 2008

Study Completion

August 1, 2008

Last Updated

April 13, 2016

Record last verified: 2016-03

Locations